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Search clinical trials for: Progressive Myoclonic Epilepsy
Total 4718 results
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University College, LondonUniversity of North Carolina, Chapel Hill; NYU Grossman School of MedicineRecruitingDentatorubral-Pallidoluysian AtrophyUnited States, United Kingdom
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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Autifony Therapeutics LimitedCompletedMyoclonus Epilepsies, ProgressiveUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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UCB PharmaCompletedUnverricht-Lundborg DiseaseUnited States, Canada, Finland, France, Israel, Russian Federation, Serbia, Tunisia
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Ionis Pharmaceuticals, Inc.CompletedLafora DiseaseUnited States, Italy, Spain
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Azienda Socio Sanitaria Territoriale di MantovaUnknownUnverricht-Lundborg Disease
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National Human Genome Research Institute (NHGRI)CompletedFamilial Dementia With Neuroserpin Inclusion Bodies | Nervous System Heredodegenerative DisorderUnited States
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UCB Pharma SACompletedUnverricht-Lundborg DiseaseFrance, Italy, Sweden, Finland, Netherlands, Tunisia, Réunion
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University of TurkuUnknownUnverricht-Lundborg SyndromeFinland
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National Institute of Neurological Disorders and...Completed
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Biohaven Therapeutics Ltd.Not yet recruiting
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TakedaRecruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)United Kingdom, Denmark
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TakedaNot yet recruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)
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TC Erciyes UniversityRecruitingEpilepsy in ChildrenTurkey
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Encoded TherapeuticsRecruiting
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UCB BIOSCIENCES, Inc.Recruiting
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Encoded TherapeuticsRecruiting
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TakedaRecruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)Spain
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Omeicos Therapeutics GmbHRecruitingPrimary Mitochondrial DiseaseGermany, Italy
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Cook Children's Health Care SystemEncoded TherapeuticsRecruiting
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Sanguine BiosciencesRecruitingHeart Diseases | Stroke | Lymphoma | Multiple Sclerosis | Kidney Diseases | Diabetes | Leukemia | Age-Related Macular Degeneration | Cancer | Arthritis | Schizophrenia | Thyroid Diseases | Parkinson Disease | Hepatitis | Vasculitis | Psoriasis | Asthma | Amyloidosis | Fibromyalgia | Graves Disease | Alzheimer Disease | Celiac Disease | Cirr... and other conditionsUnited States
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University Health Network, TorontoZogenix, Inc.Not yet recruiting
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BiocodexRecruitingDravet SyndromeUnited States
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Jazz PharmaceuticalsEvidilya S.r.l.Not yet recruitingDravet Syndrome | Lennox Gastaut SyndromeItaly
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Hospices Civils de LyonRecruitingEpilepsy | Dravet SyndromeBelgium, France, Germany
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Encoded TherapeuticsRecruiting
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TakedaRecruitingLennox Gastaut Syndrome (LGS) | Dravet Syndrome (DS)United States, China, Spain, France, Belgium, Australia, Brazil, Canada, Germany, Greece, Hungary, Italy, Japan, Latvia, Netherlands, Poland, Serbia, Mexico, Russian Federation, Ukraine
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Aga Khan UniversityNational Institute of Child Health, Karachi, PakistanNot yet recruiting
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Novartis PharmaceuticalsRecruitingRelapsing Multiple SclerosisChina, Spain, Switzerland, Taiwan, United States, Italy, Austria, Belgium, Saudi Arabia, United Arab Emirates, Latvia, Poland, Argentina, India, Croatia, Bulgaria, Malaysia, Slovakia, Israel, Lebanon, Guatemala, Netherlands, Colombia, Chil... and more
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Assistance Publique - Hôpitaux de ParisOrphelia PharmaNot yet recruitingEpilepsy | Dravet Syndrome | West SyndromeFrance
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Jazz PharmaceuticalsRecruitingTuberous Sclerosis Complex | Dravet Syndrome | Lennox Gastaut SyndromeUnited States
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Boston Children's HospitalEncoded TherapeuticsRecruitingDravet SyndromeUnited States
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Eisai Inc.RecruitingEpilepsies, MyoclonicUnited States, Canada
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Jazz PharmaceuticalsRecruitingSeizure in Participants With Tuberous Sclerosis Complex | Seizure in Participants With Dravet Syndrome | Seizure in Participants With Lennox-Gastaut SyndromeUnited States
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EpygenixForest Hills Lab; Liberyx TherapeuticsRecruitingDravet SyndromeUnited States, Canada, Spain, Georgia, Hungary
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Centre Hospitalier Universitaire, AmiensUniversity Hospital, Rouen; University Hospital, LilleRecruitingEpileptic Syndromes | Learning Disabilities | Doose SyndromeFrance
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King's College LondonKing's College Hospital NHS Trust; Charles University, Czech Republic; Hopital... and other collaboratorsRecruitingJuvenile Myoclonic EpilepsyUnited States, Canada, Czechia, Denmark, Estonia, France, Italy, Norway, United Kingdom
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Boston Children's HospitalRecruitingEpilepsy | Dravet Syndrome | Infantile Spasms | Epileptic Encephalopathy | Ohtahara Syndrome | Early Myoclonic Epileptic Encephalopathy | PCDH19-related Epilepsy and Related Conditions | KCNQ2-Related Epileptic Encephalopathy | Epilepsy of Infancy With Migrating Focal Seizures (Disorder)United States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Longboard PharmaceuticalsActive, not recruitingDravet Syndrome | Lennox-Gastaut Syndrome | Developmental and Epileptic EncephalopathyUnited States, Australia
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Zogenix, Inc.Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.Active, not recruitingDravet Syndrome | Epileptic Encephalopathy | Lennox Gastaut SyndromeUnited States, Australia, Belgium, Canada, Denmark, France, Germany, Italy, Mexico, Netherlands, Poland, Spain, Sweden, United Kingdom
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Stoke Therapeutics, IncEnrolling by invitationDravet SyndromeUnited States
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TakedaCompletedDravet Syndrome (DS)China, Canada, France, Hungary, Poland, United States, Spain, Greece, Australia, Brazil, Serbia, Germany, Italy, Japan, Latvia, Netherlands, Ukraine, Russian Federation
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Stoke Therapeutics, IncCompleted
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Fondazione Policlinico Universitario Agostino Gemelli...IRCCS San RaffaeleEnrolling by invitation
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Longboard PharmaceuticalsAvailableDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathiesUnited States