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Search clinical trials for: SMN protein depletion
Total 22359 results
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Malaysia, China, Japan, Italy, Singapore, United Kingdom, France, Australia, Thailand, Denmark, United States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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Istanbul Medipol University HospitalIstanbul UniversityRecruitingNeuromuscular Diseases | Spinal Muscular Atrophy Type 3Turkey
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University of BirminghamIMPACT (funded by NHS Blood & Transplant, Anthony Nolan and Leukaemia UK)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Multiple Myeloma | Hodgkin Lymphoma | Myelofibrosis | Chronic Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | Non Hodgkin Lymphoma | Chronic Myelogenous LeukemiaUnited Kingdom
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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M.D. Anderson Cancer CenterBristol-Myers Squibb; Pfizer; Janssen Scientific Affairs, LLCCompletedProstate CancerUnited States
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St. Jude Children's Research HospitalCompletedHodgkin Lymphoma | Myelodysplastic Syndrome (MDS) | Leukemia, Acute Lymphocytic (ALL) | Juvenile Myelomonocytic Leukemia (JMML) | Leukemia, Myeloid, Acute(AML) | Leukemia, Myeloid, Chronic(CML) | Hemoglobinuria, Paroxysmal Nocturnal (PNH) | Lymphoma, Non-Hodgkin (NHL)United States
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National Cancer Institute (NCI)TerminatedLeukemia | Multiple Myeloma | MDS | Non-Hodgkins Lymphoma | Hodgkins LymphomaUnited States
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Massachusetts General HospitalDana-Farber Cancer InstituteTerminatedLymphoma | Leukemia | Multiple Myeloma | Myelodysplastic SyndromeUnited States
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Charite University, Berlin, GermanyUniversity of SydneyCompleted
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The Cleveland ClinicNational Cancer Institute (NCI)TerminatedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Precancerous/Nonmalignant Condition | Secondary Myelofibrosis | Multiple Myeloma and Malignant Plasma Cell NeoplasmsUnited States
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National Cancer Institute (NCI)TerminatedStage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent... and other conditionsUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Completed
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Indiana University School of MedicineCompletedMultiple Myeloma | Non-Hodgkin's Lymphoma | Myelofibrosis | Chronic Lymphocytic Leukemia | Anemia, Aplastic | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Myelodysplasia | Hemoglobinuria, Paroxysmal | Hodgkin's DiseaseUnited States
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Indiana UniversityTerminatedMultiple Myeloma | Myelofibrosis | Chronic Lymphocytic Leukemia | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Mantle-Cell Lymphoma | Chronic Myelogenous Leukemia | Lymphoma, Non-Hodgkin's | Myelodysplasia | Hodgkin's DiseaseUnited States
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M.D. Anderson Cancer CenterWithdrawn
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Dana-Farber Cancer InstituteBrigham and Women's HospitalCompletedMultiple Myeloma | Hodgkin's Lymphoma | AML | Hematologic Malignancy | NHL | CML | ALLUnited States
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University of FloridaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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St. Jude Children's Research HospitalCompletedLymphoma, Non-Hodgkin | Hodgkin Disease | Chronic Myeloid Leukemia | Acute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Myelodysplastic Syndrome (MDS) | Secondary AML | Juvenile Myelomonocytic Leukemia (JMML) | Secondary MDSUnited States
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St. Jude Children's Research HospitalCompletedAcute Myeloid Leukemia | Leukemia | Hodgkin's Lymphoma | Juvenile Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | Non-Hodgkin Lymphoma | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Paroxysmal Nocturnal HemoglobinuriaUnited States
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Merck Sharp & Dohme LLCNot yet recruiting
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Novartis PharmaceuticalsNot yet recruitingLeukemia, Myelogenous, Chronic, BCR-ABL Positive
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Duke UniversityTemple UniversityNot yet recruitingAmyotrophic Lateral Sclerosis ALSUnited States
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Shenzhen Geno-Immune Medical InstituteThe No.2 Clinical Hospital of the Ministry of HealthRecruitingMultiple Myeloma | PlasmacytomaChina, Russian Federation
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Khyber Medical University PeshawarRecruitingInflammation | Obesity | Insulin Resistance | Dyslipidemias | Advance GlycationPakistan
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Janssen Research & Development, LLCNot yet recruitingRelapsed or Refractory Multiple Myeloma
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Masaryk UniversityBrno University Hospital; University Hospital Bratislava; University Hospital... and other collaboratorsRecruitingAmyotrophic Lateral SclerosisCzechia
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Henan Cancer HospitalNot yet recruitingLymphoma, Non-Hodgkin | Lymphoma, Mantle-Cell
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Lei-Miao YinXiangya Hospital of Central South University; Shanghai 6th People's Hospital; Yueyang Hospital of Integrated Traditional Chinese and Western Medicine and other collaboratorsNot yet recruiting
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Xie KangjieRecruitingDiabetes | Postoperative DeliriumChina
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Peking University Cancer Hospital & InstituteNot yet recruitingMelanoma | Metastatic Melanoma | Mucosal MelanomaChina
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Xie KangjieRecruitingPharmacokinetics | Hypoproteinemia | CiprofolChina
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Semmelweis UniversityRecruitingDental Implants, Single-Tooth | Dental Impression TechniqueHungary
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Ascentage Pharma Group Inc.Not yet recruitingChronic Myeloid Leukemia | CML | CML, Chronic PhaseUnited States
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Emory UniversityNational Cancer Institute (NCI)Not yet recruitingStage II Pancreatic Cancer AJCC v8 | Stage III Pancreatic Cancer AJCC v8 | Stage I Pancreatic Cancer AJCC v8 | Resectable Pancreatic Adenocarcinoma | Borderline Resectable Pancreatic Ductal AdenocarcinomaUnited States
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Radboud University Medical CenterNot yet recruitingInflammation | Diabetes Mellitus, Type 1
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Chen XiaopingNot yet recruiting
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University of Santiago de CompostelaHospital Clinico Universitario de SantiagoNot yet recruitingBacteremia | EndocarditisSpain
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Clinical Nutrition Research Centre, SingaporeRecruitingNutrition, HealthySingapore
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Ontario Clinical Oncology Group (OCOG)PfizerNot yet recruitingRefractory Multiple MyelomaCanada
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UGECAM Rhône-AlpesRecruiting
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National Healthcare Group PolyclinicsNational Healthcare Group, SingaporeRecruiting
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PfizerNot yet recruiting
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Beijing 302 HospitalNot yet recruitingHER2-negative Breast Cancer Brain MetastasesChina
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Technische Universität DresdenALS Association; German Society of Muscle DiseasesRecruitingAmyotrophic Lateral SclerosisGermany
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Nantes University HospitalNot yet recruiting
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Peking University People's HospitalRecruitingMonoclonal Gammopathy of Renal SignificanceChina
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Liangjing LuShanghai Ming Ju Biotechnology Co., Ltd.Not yet recruiting
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Zhiyong HuangNot yet recruitingIntrahepatic CholangiocarcinomaChina