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Search clinical trials for: alpha mannosidosis
Total 8737 results
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Chiesi Farmaceutici S.p.A.Not yet recruiting
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Greenwood Genetic CenterCompletedGalactosialidosis | Sialidosis | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Beta Mannosidosis | Mucolipidosis II | Mucolipidosis III | Schindler DiseaseUnited States
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Chiesi Farmaceutici S.p.A.Completed
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Chiesi Farmaceutici S.p.A.CompletedAlpha-MannosidosisFrance
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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CENTOGENE GmbH RostockWithdrawnAlpha-Mannosidase B Deficiency | Lysosomal Alpha B Mannosidosis | Alpha-Mannosidase DeficiencyIndia, Sri Lanka, Germany
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CENTOGENE GmbH RostockTerminatedDeafness | Immunodeficiency | Mental Retardation | Gingival Hypertrophy | Skeletal Abnormalities | Facial DysmorphismGermany, Switzerland
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Chiesi Farmaceutici S.p.A.CromsourceCompletedAlpha-MannosidosisFrance, Denmark, Austria, Germany, Italy
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Chiesi Farmaceutici S.p.A.Withdrawn
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Zymenex A/SCompleted
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Zymenex A/SEuropean CommissionCompletedA Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-MannosidosisAlpha-MannosidosisDenmark, United Kingdom, France, Germany, Poland
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Zymenex A/SEuropean CommissionCompletedAlpha MannosidosisCzechia, Germany, Norway, United Kingdom
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Zymenex A/SEuropean CommissionCompleted
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Eunice Kennedy Shriver National Institute of Child...Completed
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Mucopolysaccharidosis VI | Mannosidosis | Mucolipidosis Type II (I-cell Disease)United States
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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Zymenex A/SEuropean CommissionCompletedAlpha-MannosidosisBelgium, Denmark, Spain, United Kingdom
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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Zymenex A/SEuropean CommissionUnknown
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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Ain Shams UniversityRecruitingIntraoperative BleedingEgypt
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BeiGeneNot yet recruitingMetastatic Solid Tumor | Advanced Hepatocellular Carcinoma | Metastatic Hepatocellular Carcinoma | Alpha-fetoprotein (AFP)-Producing Gastric Cancer | Extragonadal Yolk Sac Tumors | Glypican-3 (GPC3)-Positive Squamous Non-small Cell Lung Cancer
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National Cancer Institute (NCI)Not yet recruitingPheochromocytoma | Somatostatin Receptor Positive | Paragangliomas | Gastrointestinal Neuroendocrine TumorsUnited States
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Radboud University Medical CenterNot yet recruitingInflammation | Diabetes Mellitus, Type 1
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Centre Hospitalier Universitaire de NiceNot yet recruitingIntensive Care Unit Syndrome | Cardiovascular Physiological PhenomenaFrance
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Benha UniversityRecruiting
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Icahn School of Medicine at Mount SinaiNot yet recruiting
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Ain Shams UniversityRecruitingPolycystic Ovary Syndrome | Infertility, FemaleEgypt
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Anqing Municipal HospitalRecruitingDexmedetomidine Plus Esketamine Affect Postoperative Sleep QualityChina
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Not yet recruiting
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Theodor Bilharz Research InstituteRecruiting
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Fujian Provincial HospitalFujian Maternity and Child Health Hospital; Fujian Children's HospitalNot yet recruiting
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Muhammad IlyasNot yet recruitingNausea and Vomiting, Postoperative
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Jules Bordet InstituteRayzeBio, Inc.Not yet recruitingMultiple Myeloma in Relapse | Multiple Myeloma, Refractory | Multiple Myeloma ProgressionBelgium
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Assiut UniversityNot yet recruiting
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Stanford UniversityNot yet recruiting
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Ain Shams UniversityDar EL Salam Cancer HospitalRecruitingBreast Cancer | Chemotherapy | Neurologic Disorder | Paclitaxel | Alpha Lipoic AcidEgypt
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AstraZenecaParexelRecruiting
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Beijing Tiantan HospitalNot yet recruitingPostoperative Pain | Analgesia | Supratentorial Brain Tumor
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Wave Life Sciences Ltd.Not yet recruiting
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Ottawa Heart Institute Research CorporationNot yet recruitingHypotension | Heart Failure With Reduced Ejection Fraction | LV Dysfunction
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University of IoanninaRecruitingPain, Postoperative | Breast Cancer | Anesthesia | Pain, Chronic | Cancer Recurrence | Opioid Free AnaesthesiaGreece
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Izmir Katip Celebi UniversityRecruiting