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Search clinical trials for: genetic disorders
Total 154527 results
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University of North Carolina, Chapel HillNorth Carolina Translational and Clinical Sciences InstituteNot yet recruitingColorectal Cancer | Rectal Cancer | Rectal Neoplasms | Colon Cancer | Colon Adenocarcinoma | Colon Rectal Cancer | Hereditary Nonpolyposis Colon CancerUnited States
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University of MonsRecruitingFacioscapulohumeral Muscular DystrophyBelgium
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Leiden University Medical CenterThe Dutch Brain Foundation (funding)Not yet recruitingCerebral Amyloid Angiopathy
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Regeneron PharmaceuticalsNot yet recruitingNon-transfusion Dependent Beta-thalassemia (NTDT)
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University of HaifaBnai Zion Medical Center; Clalit Health Services, Haifa and West GalileeNot yet recruitingCardiovascular Diseases | Infections | Autoimmune Diseases | Parkinson Disease | Dementia | Alzheimer Disease | Chronic Lymphocytic Leukemia | Monoclonal B-Cell Lymphocytosis | Cancers
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AstraZenecaRecruitingCarpal Tunnel Syndrome | Amyloidosis | Polyneuropathy | Hereditary Transthyretin AmyloidosisRussian Federation
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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Poitiers University HospitalRecruiting
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SpinogenixAvance Clinical Pty Ltd.Not yet recruiting
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Masonic Cancer Center, University of MinnesotaNot yet recruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic Thrombocytopenia
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Avidity Biosciences, Inc.Not yet recruitingMyotonic Dystrophy | Myotonic Disorders | Myotonia | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert Disease | Steinert
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QED Therapeutics, Inc.RecruitingHypochondroplasiaUnited States, Australia, Norway, Portugal, Singapore, Spain
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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Johns Hopkins UniversityNational Center for Complementary and Integrative Health (NCCIH); Bowdoin CollegeRecruitingTourette Syndrome | Tic Disorders | Tourette's Disorder | Persistent Tic Disorder | Chronic Motor Tic Disorder | Chronic Vocal Tic Disorder | Persistent Motor Tic Disorder | Persistent Vocal Tic DisorderUnited States
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Riphah International UniversityNot yet recruiting
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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M.D. Anderson Cancer CenterAscentage Pharma Group Inc.Not yet recruitingAdvanced Chronic Myeloid Leukemia | Philadelphia Chromosome-Positive Acute Myeloid LeukemiaUnited States
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Istanbul University - Cerrahpasa (IUC)Not yet recruitingCarpal Tunnel Syndrome | Entrapment Neuropathy | Median Nerve EntrapmentTurkey
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CSL BehringNot yet recruiting
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Vanderbilt University Medical CenterAminu Kano Teaching HospitalNot yet recruitingMalnutrition | Sickle Cell Disease
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Steminent US, Inc.Not yet recruitingSpinocerebellar Ataxias
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Alnylam PharmaceuticalsRecruitingCerebral Amyloid AngiopathyCanada
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Natural Resources Institute FinlandTampere UniversityRecruitingMicrobial Colonization | Atopic Dermatitis | Immune System and Related Disorders | Nature, HumanFinland
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Peking Union Medical College HospitalNot yet recruitingDuchenne Muscular Dystrophy (DMD)
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AbbVieNot yet recruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruitingLimb Girdle Muscular Dystrophy
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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University College, LondonLondon School of Hygiene and Tropical Medicine; King's College London; University... and other collaboratorsRecruitingTourette Syndrome | Deep Brain StimulationUnited Kingdom
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Laval UniversityRecruitingFamilial Hypercholesterolemia | Cholesterol, Elevated | Nutrition, HealthyCanada
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Gene SolutionsMedical Genetics Institute (MGI)Not yet recruitingPreterm Birth | Preeclampsia | Gestational Diabetes | Pregnant With Complication
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University of UtahRecruitingClinical Characteristics and Temporal Properties of Individual Tics in Persistent Tic Disorder (PTD)Tourette Syndrome | Tic Disorders | Tics | Tourette Syndrome in Children | Tourette Syndrome in Adolescence | Vocal Tic | Motor Tic | Tics/TremorUnited States
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Washington University School of MedicineAlzheimer's Association; Eisai Inc.Not yet recruitingDementia | Alzheimer's Disease | Alzheimer's Disease, FamilialUnited States, Australia, United Kingdom
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Shanghai Ninth People's Hospital Affiliated to...RecruitingNeurofibromatosis 1 | Plexiform NeurofibromaChina
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The First Affiliated Hospital of Zhejiang Chinese...RecruitingInflammatory Response | Tourette Syndrome in Children | Food IntoleranceChina
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Regeneron PharmaceuticalsIntellia TherapeuticsNot yet recruiting
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IRCCS Eugenio MedeaRecruiting
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University of PennsylvaniaNot yet recruitingParkinson Disease | Alzheimer Disease | ALS | Polyneuropathies | Frontotemporal Dementia | Pheochromocytoma | Thoracic Aortic Aneurysm | Paraganglioma | Genetic Predisposition | Cardiomyopathy Non-ischemic
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IRCCS Eugenio MedeaRecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Limb Girdle Muscular Dystrophy | Facio-Scapulo-Humeral DystrophyItaly
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Enzyre B.V.Indiana Hemophilia & Thrombosis CenterNot yet recruiting
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Chugai PharmaceuticalNot yet recruitingAntiphospholipid Syndrome (APS) | Immune Thrombocytopenia (ITP) | Dermatomyositis (DM) | Bullous Pemphigoid (BP) | Behçet's Syndrome (BS) | Immune-mediated Necrotizing Myopathy (IMNM)United States, Japan
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SensorionNot yet recruitingOtorhinolaryngologic Diseases | Ear Diseases | Hearing Disorders | Deafness | Hearing Loss, Sensorineural | Congenital Deafness | DFNB9 | OTOF Gene MutationFrance
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Hospices Civils de LyonNot yet recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Harmony Biosciences, LLCRecruiting
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Dan BingNot yet recruitingCongenital Hearing Loss | Congenital Deafness
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AstraZenecaRecruiting
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National Cancer Institute (NCI)Not yet recruitingLeukemia, Lymphocytic, Chronic, B-Cell | B-Cell Chronic Lymphocytic Leukemia | B-Lymphocytic Leukemia, ChronicUnited States