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Search clinical trials for: genetic disorders
Total 154050 results
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Johns Hopkins UniversityNational Center for Complementary and Integrative Health (NCCIH); Bowdoin CollegeRecruitingTourette Syndrome | Tic Disorders | Tourette's Disorder | Persistent Tic Disorder | Chronic Motor Tic Disorder | Chronic Vocal Tic Disorder | Persistent Motor Tic Disorder | Persistent Vocal Tic DisorderUnited States
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Riphah International UniversityNot yet recruiting
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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M.D. Anderson Cancer CenterAscentage Pharma Group Inc.Not yet recruitingAdvanced Chronic Myeloid Leukemia | Philadelphia Chromosome-Positive Acute Myeloid LeukemiaUnited States
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Istanbul University - Cerrahpasa (IUC)Not yet recruitingCarpal Tunnel Syndrome | Entrapment Neuropathy | Median Nerve EntrapmentTurkey
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CSL BehringNot yet recruiting
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Vanderbilt University Medical CenterAminu Kano Teaching HospitalNot yet recruitingMalnutrition | Sickle Cell Disease
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Steminent US, Inc.Not yet recruitingSpinocerebellar Ataxias
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Alnylam PharmaceuticalsRecruitingCerebral Amyloid AngiopathyCanada
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Natural Resources Institute FinlandTampere UniversityRecruitingMicrobial Colonization | Atopic Dermatitis | Immune System and Related Disorders | Nature, HumanFinland
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Peking Union Medical College HospitalNot yet recruitingDuchenne Muscular Dystrophy (DMD)
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AbbVieNot yet recruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruitingLimb Girdle Muscular Dystrophy
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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University College, LondonLondon School of Hygiene and Tropical Medicine; King's College London; University... and other collaboratorsRecruitingTourette Syndrome | Deep Brain StimulationUnited Kingdom
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Laval UniversityRecruitingFamilial Hypercholesterolemia | Cholesterol, Elevated | Nutrition, HealthyCanada
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Gene SolutionsMedical Genetics Institute (MGI)Not yet recruitingPreterm Birth | Preeclampsia | Gestational Diabetes | Pregnant With Complication
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University of UtahRecruitingClinical Characteristics and Temporal Properties of Individual Tics in Persistent Tic Disorder (PTD)Tourette Syndrome | Tic Disorders | Tics | Tourette Syndrome in Children | Tourette Syndrome in Adolescence | Vocal Tic | Motor Tic | Tics/TremorUnited States
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Washington University School of MedicineAlzheimer's Association; Eisai Inc.Not yet recruitingDementia | Alzheimer's Disease | Alzheimer's Disease, FamilialUnited States, Australia, United Kingdom
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Shanghai Ninth People's Hospital Affiliated to...RecruitingNeurofibromatosis 1 | Plexiform NeurofibromaChina
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The First Affiliated Hospital of Zhejiang Chinese...RecruitingInflammatory Response | Tourette Syndrome in Children | Food IntoleranceChina
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Regeneron PharmaceuticalsIntellia TherapeuticsNot yet recruiting
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IRCCS Eugenio MedeaRecruiting
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University of PennsylvaniaNot yet recruitingParkinson Disease | Alzheimer Disease | ALS | Polyneuropathies | Frontotemporal Dementia | Pheochromocytoma | Thoracic Aortic Aneurysm | Paraganglioma | Genetic Predisposition | Cardiomyopathy Non-ischemic
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IRCCS Eugenio MedeaRecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Limb Girdle Muscular Dystrophy | Facio-Scapulo-Humeral DystrophyItaly
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Enzyre B.V.Indiana Hemophilia & Thrombosis CenterNot yet recruiting
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Chugai PharmaceuticalNot yet recruitingAntiphospholipid Syndrome (APS) | Immune Thrombocytopenia (ITP) | Dermatomyositis (DM) | Bullous Pemphigoid (BP) | Behçet's Syndrome (BS) | Immune-mediated Necrotizing Myopathy (IMNM)United States, Japan
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SensorionNot yet recruitingOtorhinolaryngologic Diseases | Ear Diseases | Hearing Disorders | Deafness | Hearing Loss, Sensorineural | Congenital Deafness | DFNB9 | OTOF Gene MutationFrance
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Hospices Civils de LyonNot yet recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Harmony Biosciences, LLCRecruiting
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Dan BingNot yet recruitingCongenital Hearing Loss | Congenital Deafness
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AstraZenecaRecruiting
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National Cancer Institute (NCI)Not yet recruitingLeukemia, Lymphocytic, Chronic, B-Cell | B-Cell Chronic Lymphocytic Leukemia | B-Lymphocytic Leukemia, ChronicUnited States
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Chang Gung UniversityRecruiting
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University of MalagaNot yet recruitingMuscular Dystrophy | Duchenne Muscular Dystrophy | Becker Muscular DystrophySpain
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Fondazione SISA (Societa Italiana per lo Studio...RecruitingFamilial Hypercholesterolemia | Genetic DisorderItaly
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Seoul National University HospitalNot yet recruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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AstraZenecaNot yet recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform
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Xuanwu Hospital, BeijingNot yet recruiting
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Assistance Publique - Hôpitaux de ParisVaincre la MucoviscidoseNot yet recruiting
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IRCCS Eugenio MedeaRecruitingEpilepsy | Angelman Syndrome | Dup15q SyndromeItaly
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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CHU de ReimsRecruitingPrimary Immunodeficiency | Common Variable Immunodeficiency | Igg Subclass Deficiency | Selective IgM DeficiencyFrance
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SensorionNot yet recruitingSensorineural Hearing Loss, BilateralFrance
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Hasan Kalyoncu UniversityRecruitingDown SyndromeTurkey
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University Hospital, BonnSwedish Orphan BiovitrumRecruitingHaemophilia A | Synovitis | Hemophilia Arthropathy | SonographyGermany