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Search clinical trials for: glycosphingolipid storage disorder
Total 147706 results
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National Human Genome Research Institute (NHGRI)RecruitingMyoclonus | Neurological Regression | Cherry Red Spot | Brain AtrophyUnited States
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ShireNo longer available
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Genzyme, a Sanofi CompanyCompleted
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University of WashingtonNational Institute on Aging (NIA)Recruiting
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Hawra Al-DandanRecruitingOveractive Bladder SyndromeSaudi Arabia
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Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
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Caroline Michaela KistorpSanofiNot yet recruitingChronic Kidney Diseases | Fabry DiseaseDenmark
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Forge Biologics, IncNot yet recruitingKrabbe DiseaseUnited States
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Ondokuz Mayıs UniversityRecruitingQuality of Life | Urinary Incontinence | Menopause | Wolman Disease | Psychological Well-BeingTurkey
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRecruiting
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Chung-Hsing WangSanofiNot yet recruiting
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Stichting European Myeloma NetworkJanssen, LPRecruitingMultiple Myeloma | Smoldering Multiple Myeloma | Plasma Cell Leukemia | MGUS | Extramedullary MyelomaItaly, Austria, Czechia, Greece, Serbia
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University of CambridgeSanofiRecruiting
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Rocket Pharmaceuticals Inc.Recruiting
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Children's Hospital of Fudan UniversityNot yet recruiting
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States
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Qilu Hospital of Shandong UniversityRecruitingFabry Disease | Hypertrophic Cardiomyopathy | Left Ventricular HypertrophyChina
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Fondazione IRCCS San Gerardo dei TintoriFondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico; A.O. Ospedale Papa... and other collaboratorsRecruitingTraumatic Brain Injury With Loss of ConsciousnessItaly
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He HuangLingyi Biotech Co., Ltd.Recruiting
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McMaster UniversityNot yet recruitingObesity | Lysosomal Storage Diseases | Muscle Loss | Glycogen Storage Disease Type II | Pompe Disease | Nutrition Poor | Glycogen Storage Disease Type II, Adult | Glycogen Storage Disease Type II Late Onset
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States
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Lysosomal and Rare Disorders Research and Treatment...RecruitingBone Diseases | Gaucher DiseaseUnited States
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AceLink Therapeutics, Inc.Tigermed Consulting Co., LtdRecruiting
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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Westfälische Wilhelms-Universität MünsterChiesi GmbHRecruiting
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ISU Abxis Co., Ltd.RecruitingFabry DiseaseKorea, Republic of
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University of Milano BicoccaRecruitingAutoimmune Hepatitis | Liver DisorderItaly
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Lysosomal and Rare Disorders Research and Treatment...Recruiting
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SanofiRecruiting
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Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
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TakedaRecruitingHunter SyndromeCanada, France
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SanofiRecruitingFabry's DiseaseUnited States
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaRecruiting
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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Cystinose StiftungCystinosis Research Network; Leben eben! Cystinose-Selbsthilfe e.V.Recruiting
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... and other collaboratorsRecruitingGlycogen Storage Disease Type II | Pompe Disease (Late-onset)Italy
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Université de SherbrookeCentre de recherche du Centre hospitalier universitaire de Sherbrooke; Institut...RecruitingDiabetes Mellitus Type 2Canada
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Eline C. B. EskesRecruiting
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Neoped - Centru de PediatrieUniversity of Medicine and Pharmacy "Victor Babes" Timisoara; West University...Not yet recruitingAtherosclerosis | Metabolic Syndrome | Pediatric Obesity | Nonalcoholic Fatty Liver | Cardiometabolic Syndrome | PsychologyRomania
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Eline C. B. EskesRecruitingAsmd, Visceral TypeNetherlands
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Institut National de la Santé Et de la Recherche...Recruiting
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National Yang Ming UniversityCardinal Tien HospitalNot yet recruitingLower Urinary Tract Symptoms | Diabetes Mellitus | Sleep | Self-management | Sleep Health | Health-related Quality of Life | Conservative Management
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Bio Sidus SARecruiting
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University of MinnesotaRecruitingGaucher DiseaseUnited States