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Search clinical trials for: hereditary transthyretin amyloidosis
Total 3467 results
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AstraZenecaRecruitingCarpal Tunnel Syndrome | Amyloidosis | Polyneuropathy | Hereditary Transthyretin AmyloidosisRussian Federation
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AstraZenecaRecruiting
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Alnylam PharmaceuticalsRecruitingHereditary Amyloidosis, Transthyretin-Related | Asymptomatic Carrier StateFrance
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
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Rennes University HospitalRecruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryFrance
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
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University of Sao Paulo General HospitalRecruitingMicrobial Colonization | Amyloidosis, Hereditary, Transthyretin-RelatedBrazil
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Ionis Pharmaceuticals, Inc.RecruitingHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Italy, Portugal, Spain, Taiwan, Sweden, Canada, Brazil, France, New Zealand, Argentina, Cyprus, Australia, Turkey
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Alnylam PharmaceuticalsRecruitingPolyneuropathy | Hereditary Transthyretin-mediated (hATTR) AmyloidosisNetherlands, Spain, United States, Germany, France, Italy, Portugal
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
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Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated Amyloidosis | ATTR AmyloidosisIsrael, Italy, Netherlands, Spain, United States, France, Denmark, Germany, Portugal, Brazil, Taiwan
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Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
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Akcea TherapeuticsRecruitingPregnancy | Hereditary Transthyretin-mediated Amyloidosis With PolyneropathyUnited States
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
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Alnylam PharmaceuticalsApproved for marketingAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid Polyneuropathies
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PfizerCompletedPolyneuropathy | Hereditary Transthyretin Amyloidosis (ATTRv)Spain
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Alnylam PharmaceuticalsCompletedAmyloidosis, Familial | Transthyretin AmyloidosisFrance, Germany, Italy, Portugal, Spain, Sweden, United Kingdom
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The Cleveland ClinicActive, not recruitingAL Amyloidosis | Amyloidosis | Amyloid Neuropathies, Familial | Amyloid | Transthyretin Amyloidosis | Amyloid Cardiomyopathy | Amyloid - PrimaryUnited States
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Ionis Pharmaceuticals, Inc.CompletedHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Spain, Taiwan, Italy, Germany, Argentina, Australia, Brazil, Canada, Cyprus, France, Greece, New Zealand, Portugal, Sweden, Turkey
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University of PennsylvaniaAstraZeneca; Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary Amyloidosis, Transthyretin-RelatedUnited States
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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PfizerCompletedHereditary Transthyretin Amyloidosis (ATTRv) Cardiomyopathy (CM), Mixed PhenotypeUnited States
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Ionis Pharmaceuticals, Inc.CompletedHealthy Volunteers | hATTR AmyloidosisCanada
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Alnylam PharmaceuticalsCompletedPolyneuropathy | Hereditary Transthyretin-mediated (ATTRv) AmyloidosisUnited States
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Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
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Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid PolyneuropathyUnited States
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Alnylam PharmaceuticalsCompletedTransthyretin-mediated Amyloidosis (ATTR Amyloidosis)United Kingdom
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
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PfizerCompletedFamilial Amyloid Polyneuropathy | ATTR-PNSweden, Brazil, Germany, Argentina, France, Portugal
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PfizerCompletedFamilial Amyloid PolyneuropathyUnited Kingdom, Spain, United States, Argentina, Brazil, France, Germany, Portugal, Sweden
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PfizerRecruitingTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)United States
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Steen Hvitfeldt PoulsenRecruitingAortic Stenosis | Transthyretin Amyloid CardiomyopathyDenmark
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John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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Mahidol UniversityPfizerNot yet recruiting
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Algalarrondo VincentBichat Hospital; BioquantisRecruitingTransthyretin Cardiac Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Amyloid CardiomyopathyFrance
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Steen Hvitfeldt PoulsenRecruitingATTR Amyloidosis Wild TypeDenmark
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Steen Hvitfeldt PoulsenNovo Nordisk A/SRecruitingQuality of Life | Transthyretin Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Wild-Type Transthyretin-Related (ATTR)AmyloidosisDenmark
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Novo Nordisk A/SRecruitingTransthyretin Amyloid Cardiomyopathy (ATTR CM)United States, Netherlands, Germany, Canada, Czechia, France, Italy, Portugal, Spain
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Medical University of GrazMedical University InnsbruckRecruitingAmyloid Cardiomyopathy | Wild Type ATTR AmyloidosisAustria
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Paolo MilaniRecruitingAmyloidosis | Amyloidosis Cardiac | ATTR Amyloidosis Wild TypeItaly
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AstraZenecaRecruiting
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Alexion Pharmaceuticals, Inc.RecruitingTransthyretin Amyloid CardiomyopathyUnited States, Spain, United Kingdom, Norway, Israel, China, Korea, Republic of, Belgium, France, Germany, Italy, Japan, Australia, Argentina, Austria, Taiwan, Switzerland, Canada, Sweden, Poland, Denmark, Turkey, Brazil, Netherlands, G... and more
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Philippe DebonnaireNot yet recruitingTransthyretin Amyloid Cardiomyopathy
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PfizerRecruitingTransthyretin Amyloid CardiomyopathyIndia
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Zhejiang UniversityRecruitingTransthyroxin Amyloidosis CardiomyopathyChina
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom