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Search clinical trials for: inherited immune disorder
Total 182603 results
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Washington University School of MedicineNational Cancer Institute (NCI); The Foundation for Barnes-Jewish HospitalRecruitingMultiple Myeloma | Rectal Cancer | Cholangiocarcinoma | Colon CancerUnited States
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Kiminori Kimura, MDJapan Agency for Medical Research and DevelopmentRecruiting
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Institut National de la Santé Et de la Recherche...RecruitingNeurofibromatosis Type 1 | Ichthyosis | Ectodermal Dysplasia | Albinism | Pemphigus | Mucous Membrane Pemphigoid | Inherited Epidermolysis Bullosa | Palmoplantar Keratoderma | Incontinentia PigmentiFrance
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Dignity Health Medical FoundationDolly Roy MD PhD (author); J. Michael Menke (statistician); Sabeen Lulu MD (Principal...Not yet recruitingMultiple Sclerosis | Relapse
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Institute of Hematology & Blood Diseases Hospital...Sinocelltech Ltd.RecruitingHemophilia A With InhibitorChina
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Nantes University HospitalRecruiting
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Institute of Hematology & Blood Diseases HospitalRecruitingLymphoma | Acute Myeloid Leukemia | Leukemia | Hemophilia A | Hemophilia B | Hemophilia | Multiple Myeloma | Myelodysplastic Syndrome | Bone Marrow Transplantation | MDS | Aplastic Anemia | Bleeding Disorder | Myeloma, Multiple | Myelomas, Multiple | Leukemias, Acute Myeloid | Myeloid Leukemias, Acute | Hemophilia As | Hemophilia... and other conditionsChina
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Johns Hopkins All Children's HospitalRecruitingMetabolic Disease | Primary Immune Deficiency DisordersUnited States
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Federal Research Institute of Pediatric Hematology...RecruitingWiskott-Aldrich SyndromeRussian Federation
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Washington University School of MedicineRecruitingSevere Combined Immunodeficiency | Chronic Granulomatous Disease | DiGeorge Syndrome | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Syndrome | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | IPEX | Autoimmune Lymphoproliferative Syndrome | Common Variable... and other conditionsUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Masonic Cancer Center, University of MinnesotaRecruitingHemoglobinopathies | Immunodeficiencies | Hematologic DisordersUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingCommon Variable Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Disease | Langerhan's Cell Histiocytosis | Chediak-Higashi Syndrome | Griscelli Syndrome | Bare Lymphocyte Syndrome | SCID | Omenn's Syndrome | Reticular... and other conditionsUnited States
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Center for International Blood and Marrow Transplant...National Marrow Donor ProgramRecruitingAutoimmune Diseases | Hodgkin Lymphoma | Hematologic Malignancies | Acute Lymphoblastic Leukemia (ALL) | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Inherited Disorders of Metabolism | Inherited Abnormalities of Platelets | Histiocytic Disorders | Acute Myelogenous Leukemia (AML or ANLL) | Other Acute... and other conditionsUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Severe Combined Immune Deficiency (XSCID) | Leukocyte Adhesion Deficiency 1 (LAD) | Graft Versus Host Disease (cGvHD)United States
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Immunic AGActive, not recruitingRelapsing-Remitting Multiple Sclerosis (RRMS)Poland, Bulgaria, Romania, Ukraine
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Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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National Human Genome Research Institute (NHGRI)Active, not recruitingWiskott- Aldrich Syndrome | ADA Deficient SCIDUnited States
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Fondazione TelethonOspedale San RaffaeleCompleted
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Fondazione TelethonOspedale San RaffaeleActive, not recruitingWiskott-Aldrich SyndromeItaly, United States
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Fondazione TelethonEnrolling by invitationImmunologic Deficiency SyndromesItaly
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Rigel PharmaceuticalsCompletedImmune Thrombocytopenic PurpuraSpain, United States, Australia, Poland, United Kingdom, Canada, Czechia, Bulgaria, Romania, Austria, Denmark, Hungary, Italy, Netherlands, Norway
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Paul SzabolcsEnrolling by invitationChronic Granulomatous Disease (CGD) | Wiskott-Aldrich Syndrome | Severe Chronic Neutropenia | Severe Combined Immunodeficiency (SCID) | Immunodeficiency With Predominant T-cell Defect, Unspecified | Hyper IgE Syndromes | Hyper IgM Deficiencies | Mendelian Susceptibility to Mycobacterial Disease | Common...United States
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Children's Hospital Los AngelesGrifols Biologicals, LLCActive, not recruitingHemophilia A | Immune ToleranceUnited States
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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Weill Medical College of Cornell UniversityActive, not recruitingTargeting the IPA and Matching for the Non-Inherited Maternal Antigen for Haplo-Cord TransplantationHematologic MalignanciesUnited States
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Kiminori Kimura, MDJapan Agency for Medical Research and Development; Ohara Pharmaceutical Co....Completed
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David WilliamsActive, not recruitingWiskott-Aldrich SyndromeUnited States
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National Human Genome Research Institute (NHGRI)National Institute of Allergy and Infectious Diseases (NIAID); National Institute...CompletedCGD | Wiskott-Aldrich Syndrome | Primary Immunodeficiencies | APECED | SCIDUnited States
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XperiomeThe Touro College and University SystemWithdrawnHemophilia A | Hemophilia B | Idiopathic Pulmonary Fibrosis | Myasthenia Gravis | Cystic Fibrosis | Sickle Cell Disease
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Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia A With InhibitorsUnited States, Spain, Canada, Belgium, France, Bulgaria, Italy, United Kingdom, Japan, Germany
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Swedish Orphan BiovitrumBioverativ Therapeutics Inc.CompletedHemophilia AIreland, United Kingdom, Germany, United States, Canada, Slovenia, Sweden
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Grifols Therapeutics LLCGrifols Biologicals, LLCTerminatedHemophilia A, CongenitalUnited States, Spain, Italy, India, Canada, Russian Federation
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | Hemophilia AUnited States
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City of Hope Medical CenterCSL Behring; Grifols Therapeutics LLC; Grifols Biologicals, LLC; Charta Foundation and other collaboratorsCompletedSevere Hemophilia AUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedNon-Neoplastic Hematologic and Lymphocytic DisorderUnited States
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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OctapharmaTerminated
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...TerminatedGenetic Disorder | Severe Aplastic Anemia | Immunodeficiency SyndromeUnited States
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Federal Research Institute of Pediatric Hematology...CompletedWiskott-Aldrich SyndromeRussian Federation
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletedWiskott-Aldrich SyndromeUnited States, Canada
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Novo Nordisk A/STerminatedHaemophilia AAustria, Serbia, Bulgaria, United Kingdom, Germany, France, Turkey