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Search clinical trials for: serotype Rh10 AAV
Total 440 results
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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CSL BehringRecruiting
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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UniQure Biopharma B.V.RecruitingHuntington DiseasePoland, United Kingdom, Germany
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UniQure Biopharma B.V.RecruitingHuntington's DiseaseUnited States
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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Excision BioTherapeuticsEnrolling by invitationHIV-1-infectionUnited States
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IAUnited States, Brazil, Canada, Denmark, Germany, Italy, Netherlands, Spain
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Baxalta now part of ShireTakeda Development Center Americas, Inc.; Baxalta Innovations GmbH, now part...Active, not recruitingHemophilia AUnited States, Spain, Hungary, Italy, Germany, Austria, France
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Sangamo TherapeuticsCeregeneCompletedIdiopathic Parkinson's DiseaseUnited States
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Second Affiliated Hospital, School of Medicine,...Recruiting
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NGGT (Suzhou) Biotechnology Co., Ltd.Not yet recruitingPhenylketonurias
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Spark Therapeutics, Inc.Recruiting
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Zhongmou TherapeuticsNot yet recruitingRetinitis PigmentosaChina
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ViGeneron GmbHRecruiting
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Lantu BiopharmaNot yet recruitingSpinal Muscular Atrophy
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Asklepios Biopharmaceutical, Inc.BayerNot yet recruiting
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Encoded TherapeuticsRecruiting
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Tangerang District HospitalRecruiting
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Tenaya TherapeuticsJohns Hopkins University; Mayo ClinicRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States
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NovelMed TherapeuticsNot yet recruitingAnti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis
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Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
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Shanghai Vitalgen BioPharma Co., Ltd.RecruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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Leiden University Medical CenterRecruitingVaccine-Preventable DiseasesNetherlands
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Mitsubishi Tanabe Pharma CorporationRecruitingAntineutrophil Cytoplasmic Antibody (ANCA) -Associated Vasculitis (AAV)Japan
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Lori GawronPlanned Parenthood Association of UtahRecruitingEmergency ContraceptionUnited States
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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Encoded TherapeuticsRecruiting
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UniQure Biopharma B.V.Not yet recruitingAmyotrophic Lateral SclerosisUnited States
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Weill Medical College of Cornell UniversityMassachusetts General HospitalRecruitingPain, Postoperative | Sensation Disorders | Pain, Chronic | Sensory Disorder | Phantom Pain | Phantom Sensation | Sensation, Phantom | Sensory Defect | NumbnessUnited States
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AmgenRecruitingAntineutrophil Cytoplasmic Antibody-associated VasculitisUnited States
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Apurano Pharmaceuticals GmbHRecruitingStroke | Pain | Multiple Sclerosis | Chronic Pain | Traumatic Brain Injury | Neuropathic Pain | Pain, Chronic | Chronic Pain Syndrome | Paraplegia | Phantom Pain | Pain Syndrome | Central Neuropathic Pain | Phantom Limb Syndrome With PainGermany
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Apurano Pharmaceuticals GmbHRecruitingStroke | Pain | Multiple Sclerosis | Chronic Pain | Traumatic Brain Injury | Neuropathic Pain | Pain, Chronic | Chronic Pain Syndrome | Paraplegia | Phantom Pain | Pain Syndrome | Central Neuropathic Pain | Phantom Limb Syndrome With PainGermany
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Zhongmou TherapeuticsRecruitingX-linked RetinoschisisChina
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uniQure France SASRecruitingMesial Temporal Lobe EpilepsyUnited States
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AviadoBio LtdRecruitingFrontotemporal Dementia | FTD | FTD-GRN | Dementia, FrontotemporalNetherlands, Spain, Poland, United States
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Sardocor Corp.RecruitingHeart Failure, Diastolic | Heart Failure With Preserved Ejection FractionUnited States
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Zuyderland Medisch CentrumRecruitingBreast CancerNetherlands
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RenJi HospitalRecruitingHemodialysis Access FailureChina
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Shanghai General Hospital, Shanghai Jiao Tong University...Not yet recruitingTo Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
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Neuracle Genetics, IncORA, Inc.RecruitingAge-Related Macular DegenerationCanada
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St. Jude Children's Research HospitalNot yet recruiting
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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MeiraGTx, LLCRecruitingGrade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Parotid GlandsUnited States, Canada
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Shirley Ryan AbilityLabCoapt, LLCRecruitingLower Limb Amputation Below Knee (Injury) | Lower Limb Amputation Above Knee (Injury) | Amputation | Phantom Limb Pain | Phantom Pain | Phantom Sensation | Lower Limb Amputation Knee | Lower Limb Amputation at Ankle (Injury) | Upper Limb Amputation at the Hand | Upper Limb Amputation at the Wrist | Upper... and other conditionsUnited States
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Vifor Fresenius Medical Care Renal PharmaRecruiting
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VA Office of Research and DevelopmentRecruitingChronic Pain | Lower Limb Amputation | Phantom Pain | Upper Limb Amputation | Phantom Limb Pain After AmputationUnited States