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Search clinical trials for: stem cell deficiency
Total 66295 results
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IRCCS Ospedale San RaffaeleNot yet recruitingRare Diseases | Corneal Neovascularization | Limbal Stem Cell Deficiency | Aniridia | Neurotrophic Keratopathy | Ocular Cicatricial Pemphigoid | Ocular Graft-versus-host Disease | EEC Syndrome
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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University Hospital, MontpellierInstitute for Neuroscience MontpellierNot yet recruitingLimbal Stem Cell DeficiencyFrance
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Africa Health Research InstituteRecruitingHIV InfectionsSouth Africa
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University GhentInstitut de Recherche en Sciences de la Sante, Burkina Faso; Addis Ababa University and other collaboratorsRecruitingDepressive Symptoms | Vitamin B 12 Deficiency | Folate Deficiency | Cognitive Development | Anemia, MegaloblasticEthiopia
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University of MinnesotaRecruiting
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National Cancer Institute (NCI)RecruitingImmunodeficiency | GATA2United States
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Shandong Qilu Cell Therapy Engineering Technology...Shandong Public Health Clinical CenterRecruitingAIDS Virus | Disorder of Immune ReconstitutionChina
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Vastra Gotaland RegionRecruitingStem Cell Transplantation | Acute Myeloid Leukemia (AML) in RemissionBelgium, Denmark, Finland, Hong Kong, Israel, Lithuania, Netherlands, Norway, Spain, Sweden
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National Institute of Allergy and Infectious Diseases...Recruiting
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University of California, Los AngelesRecruitingAdenosine Deaminase Severe Combined Immune DeficiencyUnited States
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The University of Hong KongQueen Mary Hospital, Hong KongRecruiting
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Vinmec Research Institute of Stem Cell and Gene...RecruitingSexual Dysfunction MaleVietnam
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Vinmec Research Institute of Stem Cell and Gene...Not yet recruitingSexual Dysfunction FemaleVietnam
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Centre Leon BerardRecruitingMyelodysplastic Syndromes | Severe Combined Immunodeficiency | Acute Leukemia | Haematological Malignancy | Hemoglobinopathy in Children | Bone Marrow AplasiaFrance
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
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Assistance Publique - Hôpitaux de ParisRecruitingArtemis (DCLRE1C ) Deficient Severe Combined ImmunodeficiencyFrance
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The S.N. Fyodorov Eye Microsurgery State InstitutionRecruitingLimbal Stem-cell DeficiencyRussian Federation
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Leiden University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Horizon...RecruitingSevere Combined Immunodeficiency Due to RAG1 DeficiencySpain, Netherlands, Italy, Poland, Australia, Turkey, United Kingdom
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Porteus, Matthew, MDRecruiting
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Children's National Research InstituteRecruitingViral Infection | Hematopoietic Stem Cell Transplantation (HSCT) | Primary Immunodeficiency Disorders (PID)United States
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Atara BiotherapeuticsRecruitingLymphoproliferative Disorders | Leiomyosarcoma | Stem Cell Transplant Complications | Solid Organ Transplant Complications | Epstein-Barr Virus (EBV)-Associated Diseases | EBV+ Post-transplant Lymphoproliferative Disease (EBV+ PTLD) | Allogeneic Hematopoietic Cell Transplant | EBV+ Sarcomas | EBV+ Lymphoproliferative... and other conditionsUnited States, Austria, Belgium, France, Italy, Spain, United Kingdom
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National Cancer Institute (NCI)RecruitingImmune System Diseases | Lymphoproliferative Disorders | Common Variable Immunodeficiency | Primary T-cell Immunodeficiency Disorders | Autoimmune LymphoproliferativeUnited States
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National Taiwan University HospitalRecruiting
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National Taiwan University HospitalRecruiting
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University of California, Los AngelesNational Eye Institute (NEI); California Institute for Regenerative Medicine...Recruiting
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Hospices Civils de LyonRecruitingTotal Bilateral Limbal Cell DeficiencyFrance
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Chang Gung Memorial HospitalRecruiting
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous DiseaseUnited States
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Instituto Universitario de Oftalmobiología Aplicada...University of Valladolid; Red de Terapia Celular; CitospinNot yet recruitingLimbal Stem-cell DeficiencySpain
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Assistance Publique - Hôpitaux de ParisRecruitingPediatric Patients | Any Type of Severe Combined Immunodeficiency (SCID) | Partial HLA Incompatible Allogeneic Hematopoietic Stem Cell Transplantation (HSCT)France
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University College, LondonMedical Research CouncilRecruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Myeloma | Graft Vs Host Disease | Severe Aplastic Anemia | Primary Immune DeficiencyUnited Kingdom
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Children's Hospital of Fudan UniversityRecruitingImmunologic Deficiency Syndromes | Diabetes Mellitus, Type 1China
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University of California, San FranciscoRecruiting
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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IRCCS San RaffaeleFondazione TelethonRecruitingChronic Granulomatous Disease X-linked (X-CGD)Italy
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Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
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Novartis PharmaceuticalsRecruitingAdvanced Solid Tumors Which Are cMET-dependentGermany, Korea, Republic of, Belgium, Italy, Singapore, United States, Denmark, Spain, France, Canada
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Children's Hospital of PhiladelphiaUniversity of California, San FranciscoRecruitingImmunodeficiencies | Immune Dysregulation SyndromesUnited States
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Jasper Therapeutics, Inc.Recruiting
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Fondation Ophtalmologique Adolphe de RothschildRecruitingLimbus CorneaeFrance
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Taiga Biotechnologies, Inc.Not yet recruitingSevere Combined ImmunodeficiencyIsrael
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National Cancer Institute (NCI)RecruitingLynch Syndrome | Malignant Glioma | Recurrent Childhood Ependymoma | Recurrent Medulloblastoma | Refractory Ependymoma | Refractory Medulloblastoma | Recurrent Diffuse Intrinsic Pontine Glioma | Refractory Diffuse Intrinsic Pontine Glioma | Recurrent Brain Neoplasm | Refractory Brain Neoplasm | Constitutional...United States, Canada
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRecruitingFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Severe Marrow FailureUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingIdiopathic CD4-Positive | T-LymphocytopeniaUnited States
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Johns Hopkins UniversityNational Cancer Institute (NCI); National Institutes of Health (NIH); ChiRhoClin...RecruitingLynch Syndrome | Pancreas Cancer | Gene Mutation | Peutz-Jeghers Syndrome (PJS) | Germline Mutation CarrierUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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St. Anna KinderkrebsforschungAssistance Publique - Hôpitaux de Paris; Australian & New Zealand Children's... and other collaboratorsRecruitingAllogeneic Stem Cell Transplantation for Children and Adolescents With Acute Lymphoblastic LeukaemiaAcute Lymphoblastic LeukaemiaItaly, Israel, Spain, Argentina, Australia, Austria, Belarus, Belgium, Canada, Chile, Croatia, Czechia, Denmark, Finland, Greece, Malaysia, Mexico, Netherlands, Norway, Poland, Romania, Saudi Arabia, Slovakia, Sweden, Switzerland, Turkey, F... and more
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Wake Forest University Health SciencesRecruitingMyelodysplastic Syndromes | Multiple Myeloma | Non-Hodgkin's Lymphoma | Chronic Lymphocytic Leukemia | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Hodgkin's Disease | Germ Cell Neoplasms | Immunodeficiency DiseasesUnited States