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Search clinical trials for: thérapie génique
Total 25948 results
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)SuspendedMethylmalonic Acidemia (MMA)United States
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University of California, Los AngelesGreat Ormond Street Hospital for Children NHS Foundation TrustEnrolling by invitationAdenosine Deaminase Deficiency | Severe Combined Immunodeficiency (SCID)United States, United Kingdom
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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National Cancer Institute (NCI)CompletedT Cells Expressing a Fully-human AntiCD19 Chimeric Antigen Receptor for Treating B-cell MalignanciesLymphoma, B-Cell | Lymphoma, Non-hodgkinsUnited States
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseFrance
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseUnited Kingdom
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University Hospital, ToulouseBIOTHERAPY department of the clinical center of investigation- CIC 1436,... and other collaboratorsCompletedEffect of Intratumoral Injection of Gene Therapy for Locally Advanced Pancreatic Cancer (THERGAP-02)Pancreatic AdenocarcinomaFrance
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Wake Forest University Health SciencesNational Cancer Institute (NCI)CompletedPain | Breast Cancer | Fatigue | Skin Abnormalities | Radiation Toxicity | Cognitive Ability, General | Psychosocial DeprivationUnited States
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REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
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University of ReadingUnited States Department of DefenseCompletedStress, Psychological | Gut BacteriaUnited Kingdom
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HaemnetUniQure Biopharma B.V.Completed
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Adverum Biotechnologies, Inc.Active, not recruitingNeovascular Age-related Macular Degeneration | Wet Age-related Macular DegenerationUnited States
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
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Megan WaldropAlcyone TherapeuticsEnrolling by invitation
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Morphogenesis, Inc.CompletedBasal Cell Carcinoma | Cutaneous Squamous Cell CarcinomaUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited Kingdom
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Sangamo TherapeuticsTerminated
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Xalud Therapeutics, Inc.Terminated
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Brain Neurotherapy Bio, Inc.California Institute for Regenerative Medicine (CIRM); Asklepios Biopharmaceutical...Active, not recruiting
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Shenzhen Geno-Immune Medical InstituteEnrolling by invitationGlioblastoma Multiforme | Glioblastoma Multiforme of BrainChina
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Xalud Therapeutics, Inc.CompletedOsteoarthritis, KneeAustralia, United States
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
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American Gene Technologies International Inc.Enrolling by invitation
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American Gene Technologies International Inc.Enrolling by invitation
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Kunming Hope of Health HospitalTerminatedMenkes SyndromeChina
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IRCCS San RaffaeleTelethon Institute for Gene Therapy (OSR-TIGET)Active, not recruiting
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Ultragenyx Pharmaceutical IncCompletedGSD1Netherlands, United States, Canada, Spain
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Orchard TherapeuticsOspedale San RaffaeleActive, not recruitingLysosomal Storage Disease | Metachromatic LeukodystrophyItaly
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Adverum Biotechnologies, Inc.Enrolling by invitationDiabetic Retinopathy | Diabetic Macular EdemaUnited States, Puerto Rico
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Assistance Publique - Hôpitaux de ParisCSL BehringCompleted
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Sangamo TherapeuticsTerminatedMucopolysaccharidosis II | MPS IIUnited States
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Institute of Hematology & Blood Diseases HospitalEast China University of Science and TechnologyActive, not recruiting
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REGENXBIO Inc.Withdrawn
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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PACT Pharma, Inc.Suspended
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Novartis Gene TherapiesCompletedGene Therapy | SMA - Spinal Muscular AtrophyUnited States
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Morphogenesis, Inc.H. Lee Moffitt Cancer Center and Research InstituteCompletedCutaneous Melanoma, Stage III | Cutaneous Melanoma, Stage IVUnited States
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Mayo ClinicNational Cancer Institute (NCI)CompletedBreast Cancer | Cardiac ToxicityUnited States
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GenSight BiologicsActive, not recruitingLeber Hereditary Optic NeuropathyBelgium, Spain, United States, France, United Kingdom, Taiwan, Italy
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University of California, Los AngelesOrchard Therapeutics; California Institute for Regenerative Medicine (CIRM)CompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
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University of California, Los AngelesNational Institute of Allergy and Infectious Diseases (NIAID); National Heart... and other collaboratorsCompleted
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CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
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Janssen Research & Development, LLCCompleted
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
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Axovant Sciences Ltd.Oxford BioMedicaTerminatedParkinson's DiseaseFrance, United Kingdom
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Sio Gene TherapiesTerminatedParkinson DiseaseUnited Kingdom, France
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom