- ICH GCP
- US Clinical Trials Registry
- Klinisk utprøving NCT07711158
A Phase II Exploratory Study of SR604 Injection Evaluating the Safety and Efficacy in the Treatment of Congenital Coagulation Factor VII Deficiency
14. juli 2026 oppdatert av: Shanghai RAAS Blood Products Co., Ltd.
An Open-Label, Multicenter, Phase II Clinical Trial to Evaluate the Efficacy, Safety, and Pharmacokinetic Characteristics of SR604 Injection in Patients With Congenital Coagulation Factor VII Deficiency
This is an open-label, multicenter, exploratory Phase II clinical trial designed to evaluate the efficacy, safety, and pharmacokinetic characteristics of SR604 Injection in patients with congenital coagulation Factor VII deficiency.
Studieoversikt
Status
Har ikke rekruttert ennå
Forhold
Intervensjon / Behandling
Studietype
Intervensjonell
Registrering (Antatt)
12
Fase
- Fase 2
Kontakter og plasseringer
Denne delen inneholder kontaktinformasjon for de som utfører studien, og informasjon om hvor denne studien blir utført.
Studiekontakt
- Navn: Research and Development
- Telefonnummer: 862122130888
- E-post: hanyu@raas-corp.com
Studiesteder
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Tianjin, Kina
- Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences
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Deltakelseskriterier
Forskere ser etter personer som passer til en bestemt beskrivelse, kalt kvalifikasjonskriterier. Noen eksempler på disse kriteriene er en persons generelle helsetilstand eller tidligere behandlinger.
Kvalifikasjonskriterier
Alder som er kvalifisert for studier
- Voksen
- Eldre voksen
Tar imot friske frivillige
Nei
Beskrivelse
Inclusion Criteria:
- Age ≥12 years and ≤65 years at the time of signing the informed consent form; both genders eligible;
- Clinically diagnosed with congenital coagulation Factor VII deficiency, with historical or screening FVII activity <10%, and ≥2 treated new-onset bleeding events within 3 months prior to enrollment;
- No active bleeding symptoms prior to first administration of SR604 Injection;
- The subject and/or legal representative and impartial witness have signed the informed consent form, indicating voluntary agreement to participate in this trial, to provide biological samples for testing as required by the protocol, and to comply with the planned study visits;
- Female subjects (post-menarche) must have a negative serum pregnancy test (HCG) during the screening period; subjects with childbearing potential (females post-menarche or males post-spermarche) must agree to use highly effective contraceptive measures throughout the study period.
Exclusion Criteria:
- Known history of hypersensitivity to the study drug formulation or any of its components;
- Intolerance to subcutaneous injection or other local skin abnormalities or dermatoses that may affect drug administration or safety assessment;
Meeting any one of the following criteria during screening:
- Hemoglobin <60 g/L;
- Platelet count <100×10⁹/L;
- Abnormal hepatic or renal function: alanine aminotransferase (ALT) or aspartate aminotransferase (AST) ≥2.5× upper limit of normal (ULN), or total bilirubin ≥1.5× ULN; or serum creatinine (Cr) ≥1.5× ULN;
- Positive for anti-human immunodeficiency virus (HIV) antibodies.
- Any bleeding disorder other than congenital Factor VII deficiency, or other conditions causing significantly abnormal coagulation parameters (e.g., hemophilia A or B, von Willebrand disease, platelet disorders, vitamin K deficiency, etc.);
- Protein C deficiency or Protein S deficiency;
- History of thrombosis, family history of thrombosis, or history of thrombophilia;
- Intracranial hemorrhage within 2 years prior to signing the informed consent form;
- Severe cardiac disease, such as unstable angina, congestive heart failure (New York Heart Association class ≥III), serious arrhythmia (QTc interval >450 ms, corrected by Fridericia formula), uncontrolled hypertension (systolic blood pressure ≥160 mmHg or diastolic blood pressure ≥100 mmHg), etc.;
- Female patients with menstrual abnormalities caused by organic gynecological conditions (e.g., uterine fibroids, endometriosis, adenomyosis, etc.);
- Received Factor VII-containing products within 48 hours prior to first administration of SR604 Injection; received whole blood or plasma transfusion within 2 weeks prior to first administration of SR604 Injection;
- Used any anticoagulants, antifibrinolytics, or agents affecting platelet function (including chemical drugs, biological products, or traditional Chinese medicine), including aspirin, within 1 week prior to screening, or required use of such agents during the treatment period;
- Underwent major surgery (defined as Grade III or IV surgery) within 1 month prior to signing the informed consent form, or planned to undergo surgery during the study period;
- Enrolled in other clinical trials within 1 month prior to signing the informed consent form;
- Miscarriage or pregnancy termination within 3 months prior to signing the informed consent form; pregnant or breastfeeding women;
- Mental illness or significant psychiatric disorder, or incapacity or lack of cognitive ability due to other causes;
Other conditions deemed by the investigator to be unsuitable for enrollment, such as alcoholism, anticipated poor subject compliance preventing completion of dosing and study follow-up, poorly controlled comorbid chronic diseases, or serious systemic diseases.
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Studieplan
Denne delen gir detaljer om studieplanen, inkludert hvordan studien er utformet og hva studien måler.
Hvordan er studiet utformet?
Designdetaljer
- Primært formål: Behandling
- Tildeling: N/A
- Intervensjonsmodell: Parallell tildeling
- Masking: Ingen (Open Label)
Våpen og intervensjoner
Deltakergruppe / Arm |
Intervensjon / Behandling |
|---|---|
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Eksperimentell: SR604:Multiple-dose exploratory efficacy trial consists of 2 cohorts
Participants with FVII deficiency will receive SR604 dose 1/2 as multiple SC injections every 4-weeks
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SR604 vil bli administrert som SC-injeksjon.
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Hva måler studien?
Primære resultatmål
Resultatmål |
Tidsramme |
|---|---|
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Treated overall Annualized Bleeding Rate (ABR)
Tidsramme: Through 28 weeks of treatment.
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Through 28 weeks of treatment.
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Sekundære resultatmål
Resultatmål |
Tidsramme |
|---|---|
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Treated spontaneous annualized bleeding rate
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Treated overall annualized joint bleeding rate
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Overall annualized bleeding rate including treated and untreated bleeding events
Tidsramme: over 28 weeks of treatment,
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over 28 weeks of treatment,
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Annualized menorrhagia bleeding rate (menstruating females only)
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Change in PBAC score (menstruating females only);
Tidsramme: From baseline over 28 weeks of treatment
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From baseline over 28 weeks of treatment
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Change in EQ-5D-5L health index score
Tidsramme: From pre-treatment over 28 weeks of treatment
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From pre-treatment over 28 weeks of treatment
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Change in EQ-VAS score
Tidsramme: From baseline over 28 weeks of treatment;
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From baseline over 28 weeks of treatment;
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Subject overall satisfaction score with treatment efficacy
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Andre resultatmål
Resultatmål |
Tidsramme |
|---|---|
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Single-dose pharmacokinetic (PK) parameters:Time to Peak Plasma Concentration (Tmax)
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Single-dose pharmacokinetic (PK) parameters:Peak Plasma Concentration (Cmax)
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Single-dose pharmacokinetic (PK) parameters:Area Under the Concentration-Time Curve from Zero to Last Quantifiable Time Point (AUC0-t)
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Multiple-dose pharmacokinetic parameters-Time to Peak Plasma Concentration (Tmax)
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Multiple-dose pharmacokinetic parameters-Peak Plasma Concentration (Cmax)
Tidsramme: Over 28 weeks of treatment
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Over 28 weeks of treatment
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Safety and Immunogenicity:Incidence of AEs/SAEs/AESI,
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Incidence of drug-related AEs/SAEs/AESIs
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Safety and Immunogenicity: Anti-drug antibody (ADA) and neutralizing antibody (NAb) - number of subjects and incidence rate.
Tidsramme: over 28 weeks of treatment
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over 28 weeks of treatment
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Samarbeidspartnere og etterforskere
Det er her du vil finne personer og organisasjoner som er involvert i denne studien.
Studierekorddatoer
Disse datoene sporer fremdriften for innsending av studieposter og sammendragsresultater til ClinicalTrials.gov. Studieposter og rapporterte resultater gjennomgås av National Library of Medicine (NLM) for å sikre at de oppfyller spesifikke kvalitetskontrollstandarder før de legges ut på det offentlige nettstedet.
Studer hoveddatoer
Studiestart (Antatt)
1. juli 2026
Primær fullføring (Antatt)
1. februar 2027
Studiet fullført (Antatt)
1. desember 2027
Datoer for studieregistrering
Først innsendt
14. juli 2026
Først innsendt som oppfylte QC-kriteriene
14. juli 2026
Først lagt ut (Faktiske)
17. juli 2026
Oppdateringer av studieposter
Sist oppdatering lagt ut (Faktiske)
17. juli 2026
Siste oppdatering sendt inn som oppfylte QC-kriteriene
14. juli 2026
Sist bekreftet
1. mai 2026
Mer informasjon
Begreper knyttet til denne studien
Ytterligere relevante MeSH-vilkår
Andre studie-ID-numre
- LS-SR604-VII-II01
Plan for individuelle deltakerdata (IPD)
Planlegger du å dele individuelle deltakerdata (IPD)?
NEI
Legemiddel- og utstyrsinformasjon, studiedokumenter
Studerer et amerikansk FDA-regulert medikamentprodukt
Nei
Studerer et amerikansk FDA-regulert enhetsprodukt
Nei
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