- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on APRT Deficiency in United Kingdom
Total 4565 results
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MedicureRecruitingPyridox(am)Ine 5'-Phosphate Oxidase DeficiencyUnited States, Australia
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Children's Hospital Medical Center, CincinnatiThrasher Research Fund; United Arab Emirates UniversityCompletedVitamin D DeficiencyUnited States, United Arab Emirates
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University of California, DavisCompletedIron Overload | Oxidative Stress | Iron-deficiency AnemiaUnited States
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Paul S. BernsteinCompletedPregnancy Related | Nutrient DeficiencyUnited States
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Beth Israel Deaconess Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)TerminatedShock | Cardiac Arrest | Lactic Acidosis | Thiamin DeficiencyUnited States
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American Regent, Inc.CompletedIron Deficiency Anemia | Impaired Renal FunctionUnited States
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Wayne State UniversityChildren's Hospital of Michigan; American Regent, Inc.WithdrawnIron Deficiency Anemia | Inflammatory Bowel DiseaseUnited States
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University of South FloridaCompletedVitamin D 25 OH DeficiencyUnited States
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Pharmacosmos A/SCompletedIron Deficiency Anemia | Iron Deficiency AnaemiaUnited States
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NYU Langone HealthCompletedVitamin D DeficiencyUnited States
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Vertex Pharmaceuticals IncorporatedActive, not recruitingAlpha-1 Antitrypsin DeficiencyUnited States, United Kingdom, Germany, Ireland
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Cornell UniversityRecruitingHeme and Non-heme Iron Intakes, Gut Microbiota, and Influence on Host Iron Absorption (FeMicrobiome)Iron Overload | Anemia, Iron DeficiencyUnited States
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OctapharmaCompletedCongenital Fibrinogen DeficiencyUnited States, Bulgaria, India, Iran, Islamic Republic of, Lebanon, Russian Federation, Saudi Arabia, Turkey, United Kingdom
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AstraZenecaDaiichi Sankyo Co., Ltd.RecruitingPart 1: Bladder, Biliary Tract, Cervical, Endometrial, Ovarian, Pancreatic Cancer, Rare Tumors, Any Tumor Type Excluding Breast, Gastric, Colorectal Cancer | Part 2: HER2 Expressing/Amplified Solid Tumors Excluding Breast, Gastric, Colorectal CancerCanada, Korea, Republic of, Taiwan, United States, Italy, United Kingdom, Thailand, Russian Federation, India, Belgium, Australia, Poland, Spain, Japan, Brazil, Czechia, Netherlands
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Yale UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedVitamin D DeficiencyUnited States
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University of Wisconsin, MadisonMerck Sharp & Dohme LLCCompletedVitamin D DeficiencyUnited States
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Children's Hospital of PhiladelphiaCompleted
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Momentum DataPfizer; University of Oxford; University of SurreyCompletedMultiple Sclerosis | Pneumonia | Rheumatoid Arthritis | Systemic Lupus Erythematosus | Anxiety Disorders | Psoriasis | Asthma | Type 1 Diabetes | Graves Disease | Celiac Disease | Allergic Rhinitis | Urinary Tract Infections | Crohn Disease | Influenza | Ulcerative Colitis | Herpes Zoster | Herpes Simplex | Atopic Dermatitis | V... and other conditionsUnited Kingdom
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University of Wisconsin, MadisonCompletedCardiovascular Diseases | Vitamin D DeficiencyUnited States
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Vanderbilt UniversityApproved for marketing
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Centers for Disease Control and PreventionCompleted
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University of Wisconsin, MadisonNational Institutes of Health (NIH); National Institute on Aging (NIA)CompletedCalcium Metabolism Disorders | Magnesium DeficiencyUnited States
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University of Massachusetts, WorcesterCompletedObesity | Vitamin D DeficiencyUnited States
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Creighton UniversityCompletedObesity | Vitamin D DeficiencyUnited States
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Bio Products LaboratoryTerminatedFactor X DeficiencyUnited Kingdom, United States, Spain, Turkey
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Ultragenyx Pharmaceutical IncCompletedGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)United States, Spain, Australia, France, Israel, Italy, United Kingdom
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University of California, Los AngelesNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedVitamin D DeficiencyUnited States
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Thomas Jefferson UniversityAuerbach Hematology and OncologyRecruitingPregnancy Related | Anemia, Iron Deficiency | Anemia of PregnancyUnited States
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Stony Brook UniversityRecruiting
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Cornell UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...Active, not recruitingIron Overload | Anemia, Iron DeficiencyUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoRecruiting
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked HypophosphatemiaUnited Kingdom, France, Ireland, Italy
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National Cancer Institute (NCI)Not yet recruitingMetastatic Melanoma | Locally Advanced Melanoma | Metastatic Alveolar Soft Part Sarcoma | Metastatic Non Small Cell Lung Cancer | Metastatic Hepatocellular Carcinoma | Locally Advanced Hepatocellular Carcinoma | Metastatic Small Cell Lung Cancer | Locally Advanced Non Small Cell Lung Cancer | Locally... and other conditionsUnited States
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University of Colorado, DenverUniversity of Pittsburgh; National Institute of General Medical Sciences (NIGMS)CompletedChronic Kidney Diseases | Deficiency, Vitamin DUnited States
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Horizon Pharma USA, Inc.CompletedAldehyde Dehydrogenase-2 (ALDH2) DeficiencyUnited States
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Children's Hospital Medical Center, CincinnatiCompletedVitamin D Deficiency | Hematopoietic Stem Cell Transplantation (HSCT)United States
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Walter Reed National Military Medical CenterTerminated
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Winthrop University HospitalTerminated
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Applied Science & Performance InstituteCompletedIron Deficiency (Without Anemia)United States
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University of Texas Southwestern Medical CenterRecruitingBurns | Vitamin D DeficiencyUnited States
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI); Office of Dietary Supplements...Completed
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Loyola UniversityCompletedHypertension | Vitamin D DeficiencyUnited States
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Vadim Sherman, MDTexas Woman's University; The Methodist Hospital Research InstituteCompletedObesity | Vitamin D DeficiencyUnited States
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Kaiser PermanenteWithdrawnAnemia | Vitamin D DeficiencyUnited States
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University of Illinois at ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationObesity | Iron-deficiency | Pregnancy AnemiaUnited States
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Ultragenyx Pharmaceutical IncCompletedOrnithine Transcarbamylase (OTC) DeficiencyUnited Kingdom, United States, Canada, Spain
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Zymenex A/SEuropean CommissionCompletedA Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-MannosidosisAlpha-MannosidosisDenmark, United Kingdom, France, Germany, Poland
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American Regent, Inc.WithdrawnIron Deficiency, AnaemiaUnited States
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Juan PascualNo longer availableGlucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency SyndromeUnited States