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- US Clinical Trials Registry
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Clinical Trials on Abnormalities, Multiple
Total 33440 results
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Radius Pharmaceuticals, Inc.Benuvia Therapeutics Inc.TerminatedPrader-Willi SyndromeUnited States
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University of MinnesotaCompleted
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Radius Pharmaceuticals, Inc.Withdrawn
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Fundació Sant Joan de DéuCompleted
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Massachusetts General HospitalPatient-Centered Outcomes Research InstituteCompletedDown SyndromeUnited States
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Indiana UniversityIntegrated Listening SystemsTerminated
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Boston Children's HospitalCompleted
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University Hospital, MontpellierAssociation Française contre les Myopathies TelethonCompleted
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Fundació Sant Joan de DéuCompletedPrader-Willi SyndromeSpain
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Samsung Medical CenterSamsung ElectronicsUnknownPrader-Willi SyndromeKorea, Republic of
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University Hospital, ToulouseCompletedPrader-Willi SyndromeFrance
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Assistance Publique - Hôpitaux de ParisTerminatedPrader-Willi SyndromeFrance
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Duke UniversityNovartis; National Institutes of Health (NIH); National Center for Research Resources...TerminatedPrader-Willi SyndromeUnited States
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Samsung Medical CenterCompletedObesity | Prader-Willi Syndrome
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Taichung Veterans General HospitalUnknownPrader-Willi SyndromeTaiwan
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Samsung Medical CenterCompletedObesity | Prader-Willi Syndrome
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National Eye Institute (NEI)CompletedHippel-Lindau DiseaseUnited States
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RenJi HospitalUnknownMultiple Primary NeoplasmChina
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Brittany HoyteRecruitingRib Fractures | Rib Fracture Multiple | Rib TraumaUnited States
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WellSpan HealthRecruitingRib Fracture MultipleUnited States
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsApproved for marketingDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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Pontificia Universidade Catolica de Sao PauloCompletedEar Malformations in the Velocardiofacial Syndrome
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National University Health System, SingaporeCompletedThymic Carcinoid | Multiple Endocrine Neoplasia Type 1 (MEN-1)Singapore
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UMC UtrechtEindhoven University of TechnologyRecruiting22q11.2 Deletion Syndrome | Adolescent Idiopathic ScoliosisNetherlands
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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Hôpital le VinatierCompleted
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State University of New York - Upstate Medical...National Institute of Mental Health (NIMH)CompletedVelocardiofacial SyndromeUnited States
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Duke UniversityNational Institute of Mental Health (NIMH); University of Pittsburgh; Harvard...Completed22q11.2 Deletion Syndrome | Velo-Cardio-Facial SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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IRCCS Policlinico S. MatteoMerck Sharp & Dohme LLC; Menarini GroupUnknown
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Centre Hospitalier Intercommunal CreteilNot yet recruitingPolynesian Bronchiectasis
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Barts & The London NHS TrustLiverpool Heart and Chest Hospital NHS Foundation Trust; Aortic Dissection...RecruitingMarfan Syndrome | Marfan Syndrome Cardiovascular ManifestationsUnited Kingdom
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Forteza, Albert, M.D.Ministry of Health, SpainUnknown
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Sohag UniversityNot yet recruiting
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Stealth BioTherapeutics Inc.CompletedBarth SyndromeUnited States
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Kyongtae Ty Bae, M.D., Ph.D.University of Maryland, Baltimore; United States Department of Defense; University... and other collaboratorsCompletedPolycystic Kidney, Autosomal DominantUnited States
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Mirum Pharmaceuticals, Inc.Clinigen, Inc.Approved for marketingAlagille SyndromeUnited States
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Esther MeijerUnknownPolycystic Kidney, Autosomal Dominant | Autosomal Dominant Polycystic Kidney | ADPKDNetherlands
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Mirum Pharmaceuticals, Inc.CompletedAlagille Syndrome | Progressive Familial Intrahepatic CholestasisUnited States, Canada
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Progenity, Inc.Obstetrix Medical GroupUnknown
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The Cleveland ClinicUniversity Hospitals Cleveland Medical CenterCompletedRelapsing-Remitting Multiple Sclerosis | Secondary Progressive Multiple Sclerosis | Progressive Relapsing Multiple SclerosisUnited States
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Brigham and Women's HospitalFoundation for Prader-Willi ResearchRecruiting
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingCornelia de Lange SyndromeUnited States
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Aardvark Therapeutics, Inc.Children's Hospital Colorado; Stanford UniversityRecruiting
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UMC UtrechtSanquin Research & Blood Bank Divisions; National Institute for Public Health... and other collaboratorsRecruitingDown Syndrome | SARS-CoV-2 VaccinationNetherlands
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University Hospital, ToulouseRecruiting
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedBradycardia | Down SyndromeUnited States
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Soleno Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, United Kingdom
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SanionaWithdrawnPrader-Willi SyndromeUnited States
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Corporacion Parc TauliCompletedPrader-Willi SyndromeSpain