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Clinical Trials on Adrenoleukodystrophy (ALD)
Total 440849 results
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Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
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Mirum Pharmaceuticals, Inc.Children's Hospital Medical Center, CincinnatiCompletedCholestasis | Peroxisomal Disorders | Adrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedWolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Sanfilippo Syndrome | GM1 Gangliosidosis | Globoid Cell Leukodystrophy | Tay Sachs Disease | Sandhoffs Disease | I-Cell DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Shenzhen Sciencare Medical Industries Co., Ltd.Recruiting
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Jian-Jun OuCompleted
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Xinhua Hospital, Shanghai Jiao Tong University...Not yet recruiting
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RANDNational Institute on Alcohol Abuse and Alcoholism (NIAAA)CompletedAOD Misuse | AOD Associated ConsequencesUnited States
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Chen LiSouthwest University, China; Sichuan University ,China; The First Affiliated... and other collaboratorsRecruitingDepressive Disorder | ADHD | ASD | ADChina
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Istituto Nazionale di Ricovero e Cura per AnzianiEuropean UnionNot yet recruiting
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University of CologneUmm Al-Qura UniversityCompletedAOD Effects and ConsequencesGermany
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University of ManchesterCompletedWritten Information | Written Info and Hearing Aid Reminder | Written Info and Planning on Hearing Aid Use | All MaterialsUnited Kingdom
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University of TromsoUniversity Hospital of North Norway; Norsk Folkehjelp; Nasjonal kompetansetjeneste...UnknownTrauma | First Aid | Wounds and Injury | BystanderNorway
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Chen LiRecruiting
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University of ValenciaCompleted
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TC Erciyes UniversityActive, not recruiting
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University Hospital, MontpellierARSLACompleted
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Xinhua Hospital, Shanghai Jiao Tong University...Unknown
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Children's Hospital of Fudan UniversityShanghai Children's Medical Center; Xinhua Hospital of Shanghai Jiaotong UniversityWithdrawnTSC | DMD | X-ALD | XlsmaChina
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University of AarhusRecruiting
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Second Affiliated Hospital, School of Medicine,...Not yet recruiting
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University of FloridaALS AssociationRecruiting
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Hospital for Special Surgery, New YorkTerminated
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Baxter Healthcare CorporationCompletedDiabetes | ESRD | CAPD | APDTaiwan, Korea, Republic of, Singapore, Hong Kong, Russian Federation
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Milton S. Hershey Medical CenterALS AssociationActive, not recruiting
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Mitsubishi Tanabe Pharma America Inc.TerminatedALSUnited States, Korea, Republic of, Canada, Germany, Japan, Italy, Switzerland
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Göteborg UniversityRecruiting
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Norwegian University of Science and TechnologyTrondheim KommuneActive, not recruiting
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Chinese Medical AssociationUnknownMalnutrition | Old AgeChina
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University of NottinghamAjinomoto Co., Inc.Unknown
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Mitsubishi Tanabe Pharma CorporationCompleted
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Amylyx Pharmaceuticals Inc.Active, not recruiting
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Mitsubishi Tanabe Pharma America Inc.TerminatedALSUnited States, Canada, Japan, Germany, Korea, Republic of, Switzerland
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Sabrina Paganoni, M.D.Completed
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Universitair Ziekenhuis BrusselWithdrawnDepression | Old Age
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University of California, Los AngelesCompletedChildren at Risk for ASDUnited States
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Federal University of Rio Grande do SulNot yet recruiting
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The Hong Kong Polytechnic UniversityCompleted
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VISUfarma SpAUnknown
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Indonesia UniversityCompletedNutrition Disorders in Old Age | DisasterIndonesia