- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Alpers syndrom
Total 34828 results
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University of California, Los AngelesBoston Children's Hospital; Duke University; Children's Hospital Medical Center...RecruitingBohring-Opitz Syndrome | ASXL1 Gene Mutation | Shashi-Pena Syndrome | ASXL2 Gene Mutation | Bainbridge-Ropers Syndrome | ASXL3 Gene MutationUnited States
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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PTC TherapeuticsCompletedMitochondrial Diseases | Drug Resistant Epilepsy | Leigh Disease | Leigh Syndrome | Mitochondrial Encephalopathy (MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | Alpers Disease | Alpers SyndromeUnited States, Spain, United Kingdom, Canada, France, Italy, Poland, Sweden, Japan
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Seattle Children...Terminated
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Washington University School of MedicineMassachusetts General Hospital; Ontario Clinical Oncology Group (OCOG); St. Luke...RecruitingDeep Vein Thrombosis | Post Thrombotic Syndrome | Venous Insufficiency | Venous Leg Ulcer | Venous Stasis | Venous RefluxUnited States
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Shanghai Children's HospitalRecruitingAlport Syndrome, X-LinkedChina
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Pamukkale UniversityCompleted
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National University of SingaporeSingapore General Hospital; Duke-NUS Graduate Medical SchoolCompleted
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Tel-Aviv Sourasky Medical CenterUnknownIdiopathic FallersIsrael
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SCRI Development Innovations, LLCNovartis PharmaceuticalsTerminated
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PersImmune, IncUniversity of California, San DiegoUnknown
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Tel-Aviv Sourasky Medical CenterUnknownElderly Idiopathic FallersUnited States, Israel
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TJ Biopharma Co., Ltd.Recruiting
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI)RecruitingMyelodysplastic Syndromes (MDS)United States, Israel
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AbbVieCelgene; Genentech, Inc.CompletedMyelodysplastic Syndromes (MDS)United States, Australia, Germany
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndromes (MDS)United States, Australia, Canada, France, Germany, Italy, United Kingdom
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The First Affiliated Hospital with Nanjing Medical...UnknownMyelodysplastic Syndromes (MDS)China
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Medical University of South CarolinaNational Institute of Nursing Research (NINR)CompletedVenous Insufficiency | Venous Ulcers | Venous Disease | Venous Vascular Diseases and SyndromesUnited States
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National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Assistance Publique - Hôpitaux de ParisCompletedHealthy | Fallers | Thalamic Pain SyndromeFrance
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Ministry of Public Health, Democratic Republic...National Institutes of Health (NIH); Oregon Health and Science University; National... and other collaboratorsCompletedNeurotoxicity Syndrome, Cassava | Neurotoxicity Syndrome, Cyanate | Neurotoxicity Syndrome, Cyanide | Neurotoxicity Syndrome, ThiocyanateCongo, The Democratic Republic of the
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Benjamin TomlinsonRecruitingMyelodysplastic Syndromes | MDS/MPN Crossover SyndromesUnited States
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Novartis PharmaceuticalsCompletedAlport NephropathyUnited States
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University of California, DavisCompletedPsoriasis | Eczema | Rosacea | Actinic Keratosis | Skin Cancer | Atopic Dermatitis | Acne | Leg Ulcers | Foot Ulcers | Dysplastic NeviUnited States
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Dana-Farber Cancer InstituteCompletedMyelodysplastic Syndromes (MDS)United States
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Aston UniversityNot yet recruitingDry Eye Syndromes | Computer Vision Syndrome
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Radboud University Medical CenterRecruitingMyelodysplastic Syndromes (MDS)Denmark, Switzerland, Serbia, Austria, Croatia, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Romania, Spain, Sweden, United Kingdom
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TakedaWithdrawn
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Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
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Azidus BrasilSuspended
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University of ÉvoraSão João de Deus School of Nursing; Horizon 2020 - Portugal 2020 (ALT20-03-0145-FEDER-000007...CompletedFallers | High Risk of FallingPortugal
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University of CreteCompletedIschemic Foot Ulcers
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Rigel PharmaceuticalsRecruitingLow Risk Myelodysplastic SyndromesUnited States
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Bristol-Myers SquibbActive, not recruitingLower-risk Myelodysplastic SyndromesJapan
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The University of QueenslandRoyal Brisbane and Women's HospitalUnknown
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AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
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Nuwacell Biotechnologies Co., Ltd.The First Affiliated Hospital of University of Science and Technology of...Not yet recruitingRelapsed / Refractory Myelodysplastic Syndromes
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
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University Hospital, AngersCompletedEffect of Observation Plus Imagination of Gait on Stride Variability in Young and Older Adults (OBI)Gait Variability; Elders; Fall; Re-educationFrance
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University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
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ALX Oncology Inc.Active, not recruitingHigher Risk Myelodysplastic SyndromesKorea, Republic of, United States, Spain
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The University of Texas Health Science Center,...RecruitingNeuropsychiatric SyndromesUnited States
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Groupe Francophone des MyelodysplasiesUnknownAnemia in Myelodysplastic SyndromesFrance
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Brian JonasNational Cancer Institute (NCI); Celgene; Pharmacyclics LLC.CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Therapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic SyndromeUnited States
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Peking University Third HospitalCompletedParaneoplastic Neurological SyndromeChina
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Herzog HospitalTerminatedBacteremia | Pressure UlcersIsrael
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Sumitomo Pharma America, Inc.TerminatedAnemia in Myelodysplastic SyndromesUnited States
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Taipei Medical UniversityNational Health Research Institutes, TaiwanCompleted
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Erasme University HospitalBrussel Medical Device Center (BMDC)RecruitingBlind Loop Syndrome Postoperative | Candy Cane SyndromeBelgium