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Clinical Trials on Amyloidosis, Familial
Total 1605 results
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University of Texas Southwestern Medical CenterMid America Heart InstituteWithdrawnAortic Valve Stenosis | Cardiac Amyloidosis
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Javier López PaisUnknownAmyloidosis Cardiac | Valve Stenoses, AorticSpain
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IRCCS Policlinico S. MatteoRecruitingAL Amyloidosis | Monoclonal Gammopathy of Undetermined Significance | Smoldering Multiple MyelomaItaly
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Novartis PharmaceuticalsCompletedFamilial Chylomicronemia Syndrome (FCS)South Africa, Spain, France, Germany, United Kingdom, United States, Canada, Netherlands
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Washington University School of MedicineIncyte CorporationNo longer available
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Novartis PharmaceuticalsTerminatedFamilial Chylomicronemia Syndrome (FCS) (HLP Type I)South Africa, Germany, United Kingdom, France, United States, Canada, Netherlands
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Instituto Aragones de Ciencias de la SaludHospital Clinic of Barcelona; Instituto de Salud Carlos IIICompletedObesity | Weight Loss | Familial Hypercholesterolemias | Familial Combined Hypercholesterolemia
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Medical University of ViennaMedical University of South Carolina; IRCCS Azienda Ospedaliero-Universitaria... and other collaboratorsRecruitingAortic Stenosis | Cardiac AmyloidosisAustria, United Kingdom
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University of EdinburghUnknownAortic Stenosis | Transthyretin AmyloidosisUnited Kingdom
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Novartis PharmaceuticalsCompletedPeriodic Fevers SyndromeJapan
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University of Illinois at ChicagoWithdrawnVHL Gene Mutation | Polycythemia; Familial | Erythrocytosis; Familial | HIF-2alpha Erythrocytosis | PHD2 Erythrocytosis | Chuvash Erythrocytosis
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Capital Medical UniversityPeking University First Hospital; The First Affiliated Hospital of Anhui Medical... and other collaboratorsRecruitingAlzheimer Disease | Familial Alzheimer Disease (FAD)China
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University of PennsylvaniaRecruitingCardiac AmyloidosisUnited States
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French Cardiology SocietyPfizer; Henri Mondor University HospitalActive, not recruitingAortic Valve Stenosis | Amyloidosis | Aging | Heart DiseaseFrance
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Brigham and Women's HospitalGlaxoSmithKline; Ionis Pharmaceuticals, Inc.Withdrawn
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University Hospital, Basel, SwitzerlandCompletedMetabolic Syndrome | Familial Combined Hyperlipidemia | Familial HypertriglyceridemiaSwitzerland
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University Hospital, MontpellierCompleted
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Memorial Sloan Kettering Cancer CenterMillennium Pharmaceuticals, Inc.CompletedAmyloidosis | Light Chain Deposition Disease (LCDD or MIDD) | Light Chain and Heavy Chain Deposition Disease (LHCDD or MIDD) | Monoclonal Immunoglobulin Deposition Disease (MIDD)United States
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Steen Hvitfeldt PoulsenCompletedTransthyretin Amyloid Cardiopathy | Mitochondrial PathologyDenmark
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Kyoto UniversityOsaka University; Mie University; Tokushima University; Tokyo Metropolitan Geriatric... and other collaboratorsCompletedFamilial Alzheimer Disease (FAD) | PSEN1 MutationJapan
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University Hospital of FerraraRecruitingAortic Stenosis, Severe | Amyloidosis CardiacItaly
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University Hospital Inselspital, BerneActive, not recruitingAortic Stenosis Symptomatic | Amyloidosis CardiacSwitzerland
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Universitair Ziekenhuis BrusselRecruitingAmyloidosis | PolyneuropathyBelgium
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First Affiliated Hospital Xi'an Jiaotong UniversityEnrolling by invitationMultiple Myeloma | Amyloidosis CardiacChina
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Institute of Health Information and Statistics...Centre of Cardiovascular and Transplantation Surgery, Czech Republic; The Central... and other collaboratorsRecruitingFamilial HypercholesterolaemiaCzechia
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Vanderbilt University Medical CenterRecruitingIdiopathic Pulmonary Fibrosis | Familial Pulmonary Fibrosis | Familial Interstitial PneumoniaUnited States
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Fundación Hipercolesterolemia FamiliarInstituto de Salud Carlos III; Fundación Centro Nacional de Investigaciones...RecruitingFamilial HypercholesterolaemiaSpain
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Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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AmgenCompleted
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Fundación Pública Andaluza para la gestión de la...Recruiting
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Fundación Pública Andaluza para la gestión de la...Unknown
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina
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Beijing Suncadia Pharmaceuticals Co., LtdNot yet recruitingHomozygous Familial Hypercholesterolemia
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Organon and CoCompletedHypercholesterolemia | Heterozygous Familial Hypercholesterolemia
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HeterozygousUnited States, Germany, South Africa, Greece, Italy, Czechia, Taiwan, Slovakia, Turkey, France, Russian Federation, Canada, Spain, Jordan, Switzerland, Hungary, Poland, Netherlands, Norway, United Kingdom, Lebanon, Argentina, Brazil, ... and more
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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Novartis PharmaceuticalsCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaJapan
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AkesoAD Pharmaceuticals Co., Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
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AmgenCompletedHeterozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Norway, Belgium, Turkey, Australia, New Zealand, Austria, Czechia, South Africa, Poland, Spain, Switzerland, Netherlands, Taiwan, Finland, Brazil, Portugal, Slovenia, Russian Federation, Hungary, United... and more
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.TerminatedFamilial Partial LipodystrophyUnited States, Netherlands, Belgium, Brazil, Canada, Germany, Russian Federation
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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Austrian Academic Institute for Clinical NutritionMedical University of ViennaCompletedHeterozygous Familial HypercholesterolemiaAustria
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Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
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Merck Sharp & Dohme LLCCompletedHeterozygous Familial Hypercholesterolemia (HeFH)
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Cerenis Therapeutics, SACompleted
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Jordan Collaborating Cardiology GroupNot yet recruitingAortic Valve Stenosis | Severe Aortic Stenosis | ATTR Amyloidosis Wild Type | Middle East Studies
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...