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Clinical Trials on Angelman Syndrome
Total 34032 results
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Ovid Therapeutics Inc.CompletedPrimary Disease or Condition Being Studied: Angelman Syndrome (AS)United States, Australia, Germany, Israel, Netherlands
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University of OxfordHoffmann-La Roche; Foundation for Angelman Syndrome Therapeutics UKRecruiting
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Fondazione per la Ricerca Ospedale MaggioreCompleted
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Ovid Therapeutics Inc.CompletedAngelman SyndromeUnited States, Israel
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Boston Children's HospitalCompletedAngelman SyndromeUnited States
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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Puerta de Hierro University HospitalParc Taulí Hospital UniversitariRecruiting
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Foundation for Angelman Syndrome Therapeutics,...Queensland University of TechnologyRecruiting
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The Emmes Company, LLCBoston Children's Hospital; Ionis Pharmaceuticals, Inc.CompletedAngelman SyndromeUnited States
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Hoffmann-La RocheActive, not recruitingAngelman SyndromeUnited States, Spain, Netherlands, Italy
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Ionis Pharmaceuticals, Inc.BiogenActive, not recruitingAngelman SyndromeUnited States, Israel, Italy, France, Australia, United Kingdom
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University of Colorado, DenverCompleted
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Neuren Pharmaceuticals LimitedRecruiting
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University of South FloridaCompleted
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Ovid Therapeutics Inc.TerminatedAngelman SyndromeUnited States, Israel
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Wen-Hann TanBaylor College of Medicine; University of California, San Francisco; Vanderbilt... and other collaboratorsCompleted
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Puerta de Hierro University HospitalCompletedAngelman SyndromeSpain
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Boston Children's HospitalBaylor College of Medicine; Vanderbilt University Medical Center; Children's... and other collaboratorsCompleted
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Hoffmann-La RocheCompleted
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Centre Hospitalier Universitaire de LiegeCentre Hospitalier Régional de la Citadelle; SYSNAVRecruitingAngelman SyndromeBelgium
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Hoffmann-La RocheRecruitingAngelman SyndromeUnited States, Australia, Spain, Italy, France, Germany
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... and other collaboratorsRecruiting
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Ultragenyx Pharmaceutical IncActive, not recruitingAngelman SyndromeUnited States, United Kingdom, Canada, Australia, France, Germany, Spain, Israel
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BiogenCompletedAngelman Syndrome | Chromosome 15q Duplication (dup15q) SyndromeUnited States
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IRCCS Eugenio MedeaRecruiting
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Bennett LavensteinCompleted
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IRCCS Eugenio MedeaRecruitingEpilepsy | Angelman Syndrome | Dup15q SyndromeItaly
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University of California, San DiegoBaylor College of Medicine; Boston Children's Hospital; Rare Diseases Clinical... and other collaboratorsCompletedNervous System Diseases | Angelman SyndromeUnited States
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Ovid Therapeutics Inc.Completed
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University of Wisconsin, MadisonUltragenyx Pharmaceutical IncCompletedPrader-Willi Syndrome | Angelman SyndromeUnited States
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Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
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University Hospital, ToulouseRecruitingEpilepsy | Prader-Willi Syndrome | Angelman Syndrome | Smith-Magenis Syndrome | X Fragile SyndromeFrance
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston... and other collaboratorsCompletedPrader-Willi Syndrome | Rett Syndrome | Angelman Syndrome | Sleep ProblemsUnited States
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Institut National de la Santé Et de la Recherche...RecruitingPrader-Willi Syndrome | Angelman Syndrome | Beckwith-Wiedemann Syndrome | Pseudohypoparathyroidism | Silver Russell Syndrome | Transient Neonatal Diabetes Mellitus | Temple Syndrome | Kagami-Ogata Syndrome | Familial Precocious PubertyFrance
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National Institute of Neurological Disorders and...Baylor College of MedicineCompletedPrader-Willi Syndrome | DiGeorge Syndrome | Williams Syndrome | Angelman Syndrome | Smith-Magenis Syndrome | Chromosome Abnormalities | Shprintzen SyndromeUnited States
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RTI InternationalUniversity of North Carolina, Chapel HillEnrolling by invitationTuberous Sclerosis | Down Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Rett Syndrome | Turner Syndrome | Williams Syndrome | Angelman Syndrome | Chromosome 22q11.2 Deletion Syndrome | Klinefelter Syndrome | Phelan-McDermid Syndrome | Dup15Q Syndrome | Smith Magenis SyndromeUnited States
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TJ Biopharma Co., Ltd.Recruiting
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI)RecruitingMyelodysplastic Syndromes (MDS)United States, Israel
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AbbVieCelgene; Genentech, Inc.CompletedMyelodysplastic Syndromes (MDS)United States, Australia, Germany
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndromes (MDS)United States, Australia, Canada, France, Germany, Italy, United Kingdom
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The First Affiliated Hospital with Nanjing Medical...UnknownMyelodysplastic Syndromes (MDS)China
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SCRI Development Innovations, LLCNovartis PharmaceuticalsTerminated
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PersImmune, IncUniversity of California, San DiegoUnknown
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Natera, Inc.Children's Hospital of Philadelphia; Montefiore Medical Center; University of... and other collaboratorsCompletedPrader-Willi Syndrome | DiGeorge Syndrome | 22q11 Deletion Syndrome | Angelman Syndrome | Trisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy X | Sex Chromosome Abnormalities | 1p36 Deletion Syndrome | Cri-du-Chat SyndromeUnited States, Australia, Ireland, Spain, Sweden, United Kingdom
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Benjamin TomlinsonRecruitingMyelodysplastic Syndromes | MDS/MPN Crossover SyndromesUnited States
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Ministry of Public Health, Democratic Republic...National Institutes of Health (NIH); Oregon Health and Science University; National... and other collaboratorsCompletedNeurotoxicity Syndrome, Cassava | Neurotoxicity Syndrome, Cyanate | Neurotoxicity Syndrome, Cyanide | Neurotoxicity Syndrome, ThiocyanateCongo, The Democratic Republic of the
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Dana-Farber Cancer InstituteCompletedMyelodysplastic Syndromes (MDS)United States