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Clinical Trials on Autosomal Dominant Optic Atrophy
Total 240 results
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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Santhera PharmaceuticalsWithdrawnLeber's Hereditary Optic Neuropathy
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant HypocalcemiaUnited States, France, Denmark, Australia, Japan, Belgium, Canada, Italy, Netherlands, United Kingdom, Portugal, Finland, Germany
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Kadmon, a Sanofi CompanyCompletedPolycystic Kidney, Autosomal DominantUnited States
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Carolina CannilloCompletedPolycystic Kidney, Autosomal DominantDenmark
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PfizerCompletedPolycystic Kidney, Autosomal DominantUnited States, Canada, Australia, Sweden, Spain, Poland, Korea, Republic of, Switzerland, United Kingdom, Moldova, Republic of, Italy, Czech Republic, Hungary, Lithuania, Romania, Slovakia, Turkey
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
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GenSight BiologicsActive, not recruitingLeber Hereditary Optic NeuropathyBelgium, Spain, United States, France, United Kingdom, Taiwan, Italy
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)Italy, Germany, France, Austria, Greece, Netherlands
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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Huazhong University of Science and TechnologyShiyan Taihe HospitalActive, not recruitingLeber Hereditary Optic NeuropathyChina
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyFrance
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Santhera PharmaceuticalsEuropean Vision Institute Clinical Research NetworkCompletedLeber Hereditary Optic Neuropathy (LHON)Belgium, France, Denmark, Italy, Slovenia
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Radboud University Medical CenterAcademisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)CompletedPolycystic Kidney, Autosomal Dominant | Polycystic Liver DiseaseNetherlands, Spain
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Assistance Publique - Hôpitaux de ParisCompletedSpinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia, Autosomal Recessive 3 | Episodic Ataxia, Type 7France
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Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney, Autosomal DominantJapan
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Otsuka Pharmaceutical Development & Commercialization...CompletedPolycystic Kidney, Autosomal DominantBelgium, Germany, Italy, Spain, Sweden, United States, Canada, Australia, Netherlands, Czechia, Poland, Denmark, Israel, Hungary, Russian Federation, South Africa, United Kingdom, Romania, Argentina, Norway
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Canada, Brazil, Taiwan, Singapore, South Africa, United Kingdom
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore
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Hôpital Necker-Enfants MaladesEuropean Georges Pompidou Hospital; CLAIROPCompletedSafety Issues | Efficacy, SelfFrance
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Edison Pharmaceuticals IncNo longer availableLeber's Hereditary Optic NeuropathyUnited States
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Santhera PharmaceuticalsNo longer availableLeber's Hereditary Optic Neuropathy
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Stealth BioTherapeutics Inc.CompletedLeber's Hereditary Optic NeuropathyUnited States
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Quark PharmaceuticalsCompletedOptic Atrophy | Non-arteritic Anterior Ischemic Optic NeuropathyUnited States, Israel
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Bin LiHuazhong University of Science and TechnologyCompletedLeber Hereditary Optic NeuropathyChina
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Kyongtae Ty Bae, M.D., Ph.D.University of Maryland, Baltimore; United States Department of Defense; University... and other collaboratorsCompletedPolycystic Kidney, Autosomal DominantUnited States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, United Kingdom, Denmark, Italy, France, Japan, Taiwan, Canada, Czechia, Netherlands
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MD Stem CellsRecruitingGlaucoma | Age-Related Macular Degeneration | Macular Degeneration | Retinitis Pigmentosa | Leber Hereditary Optic Neuropathy | Optic Atrophy | Blindness | Optic Neuropathy | Vision, Low | Retinal Disease | Stargardt Disease | Maculopathy | Retinopathy | Optic Nerve Disease | Nonarteritic Ischemic Optic Neuropathy | Vision... and other conditionsUnited States, United Arab Emirates
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Centre Hospitalier National d'Ophtalmologie des...StreetlabCompletedRetinitis Pigmentosa | Leber's Hereditary Optic Neuropathy | Stargardt DiseaseFrance
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Argo SanteGenSight BiologicsCompleted
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University of Colorado, DenverPKD FoundationCompletedPolycystic Kidney, Autosomal DominantUnited States
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The Rogosin InstituteWeill Medical College of Cornell University; Rockefeller UniversityCompletedChronic Kidney Disease | Polycystic Kidney, Autosomal DominantUnited States
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Radboud University Medical CenterIpsenCompletedLiver Diseases | Polycystic Kidney, Autosomal Dominant | Hepatomegaly | Polycystic Liver DiseaseNetherlands, Belgium
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Mario Negri Institute for Pharmacological ResearchRecruitingDeveloping a Pipeline to Employ RNA-Seq as a Complementary Diagnostic Tool in Rare Diseases (ANTHEM)Healthy | Autosomal Dominant Polycystic Kidney | Atypical Hemolytic Uremic Syndrome | Membranoproliferative GlomerulonephritisItaly
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Reata, a wholly owned subsidiary of BiogenTerminatedChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney | Alport SyndromeUnited States, France, Australia, Japan, Spain, Puerto Rico
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis | Eye Diseases, Hereditary | Retinal Dystrophies | Vision Disorders | Retinal Disease | Autosomal Dominant Retinitis Pigmentosa | Vision TunnelUnited States
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National Institute on Deafness and Other Communication...Recruiting
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Hoffmann-La RocheNational Institute on Aging (NIA); Banner Alzheimer's InstituteCompleted
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Genentech, Inc.National Institute on Aging (NIA); Banner Alzheimer's InstituteCompleted
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University of Colorado, DenverUniversity of MarylandRecruitingPolycystic Kidney, Autosomal DominantUnited States
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Regional Hospital HolstebroCompletedChronic Kidney Diseases | Polycystic Kidney, Autosomal DominantDenmark
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedPolycystic Kidney, Autosomal DominantUnited States
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Randy KardonRecruitingLeber Hereditary Optic Neuropathy | Ischemic Optic Neuropathy | Hemianopia | Branch Retinal Artery Occlusion | Acute Zonal Occult Outer RetinopathyUnited States
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedPolycystic Kidney, Autosomal DominantUnited States
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University Hospital TuebingenRecruitingHereditary Spastic Paraplegia | Hereditary, Spastic Paraplegia, Autosomal DominantGermany
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QLT Inc.CompletedRetinitis Pigmentosa (RP)Canada, Ireland
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University of AarhusUnknownPseudohypoparathyroidism | Idiopathic Hypoparathyroidism | Autosomal Dominant HypocalcaemiaDenmark
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ShireTerminatedRetinitis PigmentosaUnited States
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Assistance Publique - Hôpitaux de ParisAventis PharmaceuticalsCompletedEHLERS-DANLOS SYNDROME, TYPE IV, AUTOSOMAL DOMINANT | CHROMOSOME 2q31.2 DELETION SYNDROME