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Clinical Trials on Beta Thalassemia Major Anemia
Total 426 results
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Julia FinkelCompletedSCD With Severe Phenotype (HbSS, HbSβ0 Thalassemia, HbSOARab)United States
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Novo Nordisk A/SRecruitingHealthy Volunteers Sickle Cell Disease, ThalassemiaUnited States
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Klein Buendel, Inc.National Institute on Minority Health and Health Disparities (NIMHD); Hilton...CompletedSickle Cell Disease | Sickle Cell Anemia in Children | Sickle Cell Thalassemia | Sickle Cell SC DiseaseUnited States
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HaEmek Medical Center, IsraelWolfson Medical CenterCompletedMRI | Iron Overload | Sickle Cell Anemia | Sickle Cell ThalassemiaIsrael
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | Sickle Cell ThalassemiaIsrael
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The University of Hong KongCompletedHomozygous αº-thalassemia | Hb Bart's DiseaseChina
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Shiraz University of Medical SciencesCompleted
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Sidney Kimmel Cancer Center at Thomas Jefferson...National Heart, Lung, and Blood Institute (NHLBI)TerminatedSickle Cell Anemia | Sickle Cell-hemoglobin C Disease | Sickle Cell-β0-thalassemiaUnited States
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Novartis PharmaceuticalsWithdrawnFocus on Transfusion Dependent Thalassemia Patients Who Are Inadequate Responders to Deferasirox > 35mg/kgQD
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University of Campania "Luigi Vanvitelli"CompletedIron Overload | Endocrine; Complications | Transfusion-dependent ThalassemiaItaly
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Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaGreece, Taiwan, Italy, United Kingdom, Lebanon, Turkey, Malaysia, Thailand, United States
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Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
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Reproductive & Genetic Hospital of CITIC-XiangyaCompletedThalassemia,Embryonic Development,Reproductive Sterility and InfertilityChina
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University of Milano BicoccaComitato Maria Letizia Verga,ItalyRecruitingLymphoma, Non-Hodgkin | Leukemia, Myeloid, Acute | Leukemia, B-cell | Adrenoleukodystrophy | Lymphoma, Hodgkin | Thalassemia Major | Leukemia, T Cell | DrepanocytosisItaly
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Tennessee; Assisi...Completed
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | ThalassemiaIsrael
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HaEmek Medical Center, IsraelMinistry of Health, IsraelCompletedSickle Cell Anemia | ThalassemiaIsrael
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Lundquist Institute for Biomedical Innovation at...Emmaus Medical, Inc.Terminated
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Emmaus Medical, Inc.FDA Office of Orphan Products DevelopmentCompletedSickle Cell Anemia | ThalassemiaUnited States
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Bristol-Myers SquibbRecruitingAnemiaThailand, China, Canada, Turkey, Greece, Taiwan, Italy, Hong Kong
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...CompletedThalassemiaUnited States, Greece, Italy, Lebanon, Thailand, United Kingdom
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UCSF Benioff Children's Hospital OaklandChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsCompleted
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Ionis Pharmaceuticals, Inc.Completed
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
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Baylor College of MedicineThe Methodist Hospital Research InstituteTerminatedSickle Cell Anemia | Thalassemia | HemoglobinopathyUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedSickle Cell Anemia | Thalassemia | HemoglobinopathyUnited States
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Reem Ali ShakerRecruiting
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Menoufia UniversityCompleted
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Baylor College of MedicineTerminated
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The First Affiliated Hospital, Guangzhou University...Unknown
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Yanfang LiUnknown
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)Completed
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Novartis PharmaceuticalsCompleted
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedThalassemiaUnited States, Canada, United Kingdom
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Columbia UniversityNational Heart, Lung, and Blood Institute (NHLBI)Terminated
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University of PittsburghCompletedSickle Cell Disease | Hemoglobinopathies | ThalassemiaUnited States
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Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
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Fakultas Kedokteran Universitas IndonesiaNot yet recruiting
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Agios Pharmaceuticals, Inc.Active, not recruitingThalassemiaUnited States, Canada, United Kingdom
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Hangzhou Zede Pharma-Tech Co., Ltd.Completed
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Blood Diseases ClinicUniversity of PeshawarCompleted
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Hangzhou Zede Pharma-Tech Co., Ltd.Completed
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Guang'anmen Hospital of China Academy of Chinese...Completed
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National Heart, Lung, and Blood Institute (NHLBI)Children's National Research InstituteRecruitingSickle Cell Disease | Thalassemia | HemoglobinopathyUnited States
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Mersin UniversityCompleted
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The First Affiliated Hospital, Guangzhou University...National Natural Science Foundation of ChinaUnknownPregnancy | ThalassemiaChina