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Clinical Trials on Childhood Myotonic Dystrophy
Total 3340 results
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Susan McDowellFoundation for Physical Medicine and RehabilitationTerminatedComplex Regional Pain Syndromes | Spinal Cord Injuries | Phantom Limb Pain | Pain, NeuropathicUnited States
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J&M ShulerTerminatedEdema | Complex Regional Pain Syndrome | Post-traumatic Carpal Tunnel SyndromeUnited States
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Soroka University Medical CenterWithdrawnDiabetic Neuropathies | Complex Regional Pain Syndrome Type II | Resistant Peripheral Neuropathic Pain | Chemotherapy Induced Pain NeuropathyIsrael
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Amryt PharmaChiesi Farmaceutici S.p.A.Not yet recruitingEpidermolysis Bullosa, Junctional | Epidermolysis Bullosa, Dystrophic
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophies | Inherited Neuromuscular Conditions | Inherited Neuropathies | Muscle Myopathies | Hereditary Spastic ParaplegiasUnited States
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Brock UniversityCompletedMultiple Sclerosis | Inflammation | Muscular Dystrophies | Spinal Cord Injuries | Diet HabitCanada
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Children's Hospital Medical Center, CincinnatiUniversity of BarcelonaRecruitingMusculoskeletal Pain | Fibromyalgia | Complex Regional Pain Syndromes | Functional Abdominal Pain Syndrome | Migraine in ChildrenUnited States
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National Institutes of Health Clinical Center (CC)RecruitingCerebral Palsy | Muscular Dystrophy | Spina Bifida | Incomplete Spinal Cord InjuryUnited States
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National Institutes of Health Clinical Center (CC)RecruitingCerebral Palsy | Muscular Dystrophy | Spina Bifida | Incomplete Spinal Cord InjuryUnited States
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Seoul National UniversitySMG-SNU Boramae Medical CenterCompletedComplex Regional Pain Syndromes | Neuropathic Pain | Phantom Limb Pain | Postherpetic Neuralgia | Post-Traumatic Neuralgia | Chronic Post Surgical PainKorea, Republic of
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University of New MexicoCompletedRetinitis Pigmentosa | Age Related Macular Degeneration | Congenital Stationary Night Blindness | ColorblindnessUnited States
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RTI InternationalUniversity of North Carolina, Chapel HillEnrolling by invitationTuberous Sclerosis | Down Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Rett Syndrome | Turner Syndrome | Williams Syndrome | Angelman Syndrome | Chromosome 22q11.2 Deletion Syndrome | Klinefelter Syndrome | Phelan-McDermid Syndrome | Dup15Q Syndrome | Smith Magenis SyndromeUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)TerminatedSarcoma | Lymphoma | Kidney Cancer | Unspecified Childhood Solid Tumor, Protocol Specific | Testicular Germ Cell Tumor | Ovarian Cancer | Brain and Central Nervous System Tumors | Neuroblastoma | Liver Cancer | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited States
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University of MinnesotaChildren's Cancer Research Fund United StatesTerminatedLymphoblastic Lymphoma | Brain Tumors | Lymphoblastic Leukemia, Acute, Childhood | Lymphoblastic Leukemia | Leukemia, Lymphocytic, Acute | Leukemia, Lymphoblastic, Acute | Brain Neoplasms, Malignant | ALL, Childhood | Leukemia, Lymphoblastic, Acute, Philadelphia-Positive | Lymphoblastic Leukemia, Acute | Leukemia... and other conditionsUnited States
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Hangzhou Jiayin Biotech LtdRecruitingSpinal Muscular Atrophy Type IChina
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Assistance Publique Hopitaux De MarseilleRecruitingSpinal Muscular AtrophyFrance
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Children's Oncology GroupNational Cancer Institute (NCI)WithdrawnClear Cell Renal Cell Carcinoma | Rhabdoid Tumor of the Kidney | Congenital Mesoblastic Nephroma | Childhood Kidney NeoplasmUnited States
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University of South FloridaNational Cancer Institute (NCI)TerminatedLymphoma | Unspecified Childhood Solid Tumor, Protocol Specific | Myelodysplastic Syndromes | Leukemia | Malnutrition | Weight Changes
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Institut de Myologie, FranceCompletedSpinal Muscular Atrophy
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Children's Cancer and Leukaemia GroupUnknownOvarian Cancer | Brain and Central Nervous System Tumors | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited Kingdom, Ireland
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type IUnited States
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Lenus Therapeutics, LLCTerminatedDystrophic Epidermolysis Bullosa | Junctional Epidermolysis BullosaUnited States
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Kun SunRecruitingSpinal Muscular Atrophy 1China
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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University of Geneva, SwitzerlandAll India Institute of Medical Sciences, New Delhi; Swiss National Science... and other collaboratorsRecruitingPharmacogenomic Association Study in Indian Children With Acute Lymphoblastic Leukemia (MPGx-INDALL)Drug Effect | Pediatric Cancer | Adverse Drug Event | Drug Interaction | ALL, Childhood | Drug Toxicity | Toxicity, Drug | Relapse LeukemiaIndia
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Stanford UniversityCompletedMuscular Atrophy, SpinalUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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UMC UtrechtCompletedSpinal Muscular Atrophy | SMA | Kugelberg-Welander DiseaseNetherlands
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St. Jude Children's Research HospitalNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Colorectal Cancer | Unspecified Adult Solid Tumor, Protocol Specific | Carcinoma of Unknown PrimaryUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Leukemia | Brain and Central Nervous System Tumors | Unspecified Adult Solid Tumor, Protocol Specific
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Dana-Farber Cancer InstituteNational Cancer Institute (NCI); Boston Children's HospitalCompletedSarcoma | Lymphoma | Unspecified Childhood Solid Tumor, Protocol Specific | Leukemia | Neuroblastoma | Central Nervous System Tumor, PediatricUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Eastern Cooperative Oncology Group; Southwest... and other collaboratorsCompletedTesticular Germ Cell Tumor | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited States, Puerto Rico, Australia, Peru
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Teresa Moreno CasbasThe Spanish Centre for Evidence Based Nursing and HealthcareActive, not recruiting
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Stanford UniversityCompletedA Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy PatientsMuscular Atrophy, SpinalUnited States
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University of UtahLeadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular Atrophy Type IUnited States, Canada, Germany
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Children's Oncology GroupNational Cancer Institute (NCI)WithdrawnLymphoma | Unspecified Childhood Solid Tumor, Protocol Specific | Leukemia | Brain and Central Nervous System Tumors
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Enzon Pharmaceuticals, Inc.National Cancer Institute (NCI)WithdrawnLymphoma | Unspecified Childhood Solid Tumor, Protocol Specific | Myelodysplastic Syndromes | Leukemia | Neutropenia | Infection | Fever, Sweats, and Hot FlashesUnited States
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OrganogenesisTerminatedEpidermolysis Bullosa Dystrophica | Epidermolysis Bullosa, JunctionalUnited States
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Sidney Kimmel Cancer Center at Thomas Jefferson...CompletedPrimary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent... and other conditionsUnited States
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Karunesh GangulyNational Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingStroke | Multiple Sclerosis | Muscular Dystrophies | ALS | SCI - Spinal Cord InjuryUnited States
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Sanko UniversityCompletedCerebral Palsy | Muscular Dystrophy | Down Syndrome | Parents | Spina BifidaTurkey
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Egyptian Atomic Energy AuthorityWaleed Nemr,Egyptian Atomic Energy AuthorityCompletedEpidermolysis Bullosa | Chronic Skin UlcerEgypt
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Olof SkoldenbergThe Swedish Association for Survivors of Accident and InjuryRecruitingOsteoarthritis | Tendon Injuries | Surgery | Surgery--Complications | Surgical Site Infection | Radius Fracture Distal | Dislocation | CRPS Type I | Tendon Rupture | Treatment Complication | CRPS Type IISweden
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Beth Israel Deaconess Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)CompletedAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Radiculopathy | Trauma Injury | Orthopedic Disorder | Myopathy | Polyneuropathy and MononeuropathiesUnited States
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Gaziosmanpasa Research and Education HospitalCompletedCOVID-19 | Cerebral Palsy | Muscular Dystrophies | Disabilities MultipleTurkey