- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Cholesterol Ester Storage Disease
Total 7591 results
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Monash University MalaysiaRecruiting
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Kansas State UniversityMGP Ingredients, Inc.WithdrawnOverweight or Obesity | Cholesterol, ElevatedUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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CENTOGENE GmbH RostockWithdrawnFructose Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease | Glycogen Storage Disease Type V | Glycogen Storage Disease Type I | Glycogen Storage Disease Type III | Glycogen Storage Disease Type VII | Glycogen Storage Disease Type IV | Glycogen Storage Disease Type... and other conditionsGermany, India, Sri Lanka
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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John MitchellCompletedGlycogen Storage Disease Type III | Glycogen Storage Disease Type IA | Glycogen Storage Disease Type IB | Glycogen Storage Disease Type 0Canada
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Mercer UniversityMerck Sharp & Dohme LLC; Emory University; Celera GenomicsCompletedType 2 Diabetes | Cholesterol | African American | Lipoprotein | ApolipoproteinUnited States
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AstraZenecaCompletedDiabetes Mellitus Type 2 | LDL Cholesterol | Observational | Crestor, RosuvastatinNetherlands
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University Medical Center GroningenUltragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IANetherlands
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IAUnited States, Brazil, Canada, Denmark, Germany, Italy, Netherlands, Spain
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Northern Ontario School of MedicineRecruitingHeart Diseases | Hypertension | Obesity | Diabetes | High CholesterolCanada
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Duke UniversityTerminatedChronic Kidney Disease | High Cholesterol
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University of TorontoUnknownCardiovascular Risk Factor | Cholesterol; LipidosisCanada
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AstraZenecaCompletedLow Density Lipoprotein Cholesterol Goal AchievementKorea, Republic of
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Baylor College of MedicineThe Methodist Hospital Research InstituteTerminatedInherited Metabolic Storage DiseasesUnited States
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Children's Mercy Hospital Kansas CityRecruiting
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IA | Von Gierke's Disease (GSD Type Ia)Netherlands, United States, Canada, Spain
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University of California, San DiegoMerck Sharp & Dohme LLCTerminatedCoronary Artery Disease | High CholesterolUnited States
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Rigshospitalet, DenmarkDanish Research Center for Magnetic ResonanceRecruitingGlycogen Storage Disease | Pompe Disease (Late-onset) | McArdle DiseaseDenmark
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Sanguine BiosciencesTerminatedGlycogen Storage Disease Type IBUnited States
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Fonds de la Recherche en Santé du QuébecUniversité de MontréalCompletedHypertension | Diabetes Mellitus, Type 2 | Dyslipidemias | Cholesterol, LDL | ComorbitdityCanada
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McMaster UniversityNot yet recruitingObesity | Lysosomal Storage Diseases | Muscle Loss | Glycogen Storage Disease Type II | Pompe Disease | Nutrition Poor | Glycogen Storage Disease Type II, Adult | Glycogen Storage Disease Type II Late Onset
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University of FloridaAmicus TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type II | Pompe DiseaseUnited States
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Ultragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IANetherlands, United States
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Novo Nordisk A/SCompletedHealthy Volunteers | Elevated Cholesterol | Established Atherosclerotic Cardiovascular Disease (ASCVD) or ASCVD RiskGermany
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NYU Langone HealthWithdrawnChronic Kidney Diseases | High CholesterolUnited States
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Spark TherapeuticsActive, not recruitingLysosomal Storage Diseases | Glycogen Storage Disease Type II | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Canada, Netherlands, France, Denmark, Germany, Italy, United Kingdom
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Institute of Liver and Biliary Sciences, IndiaNot yet recruitingGlycogen Storage DiseasesIndia
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Spark TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Italy, United Kingdom, Netherlands, France, Germany
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Massachusetts General HospitalNot yet recruitingHeart Diseases | Cardiovascular Diseases | Vascular Diseases | Stroke | Atherosclerosis | Transient Ischemic Attack | Carotid Artery Diseases | Carotid Atherosclerosis | Cerebrovascular Accident | Atherosclerotic Cardiovascular Disease | Vascular Calcification | Heart Attack | Vascular Disease, Peripheral | Arterial... and other conditionsUnited States
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Baskent UniversityCompletedCardiovascular Disease | Type 2 Diabetes Mellitus | Cognition | LDL Cholesterol
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Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical ResearchRecruitingFamilial Hypercholesterolemia | Genetic Disease | Cholesterol, ElevatedUnited States
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Duke UniversityCompleted
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University Medical Center GroningenUniversity of Oxford; University of the Faroe Islands; Stichting Stofwisselkracht and other collaboratorsCompleted
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Hospital de Clinicas de Porto AlegreConselho Nacional de Desenvolvimento Científico e Tecnológico; Fundação Médica...CompletedGlycogen Storage Disease Type IBrazil
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Amicus TherapeuticsRecruitingGlycogen Storage Disease Type II Infantile OnsetTaiwan, United States, France, Germany, Italy, United Kingdom
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Medical University of ViennaRecruitingPompe Disease | McArdle DiseaseAustria
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Laval UniversityRecruitingFamilial Hypercholesterolemia | Cholesterol, Elevated | Nutrition, HealthyCanada
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Jena University HospitalNot yet recruitingST Elevation Myocardial Infarction | Non-ST Elevation Myocardial Infarction | LDL-cholesterolGermany
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Wake Forest University Health SciencesCompletedCardiovascular Diseases | Diabetes | Metabolic Syndrome | Liver Fat | Cardiovascular Risk Factor | Diet Habit | Dietary Modification | High Cholesterol | Triglycerides High | Low-density-lipoprotein-type | HDL Cholesterol, Low Serum | High Blood Sugar | Intra-abdominal Fat | High Density Lipoprotein DeficiencyUnited States
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Assistance Publique - Hôpitaux de ParisRecruiting
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II Pompe DiseaseUnited States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
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Genzyme, a Sanofi CompanyActive, not recruitingGlycogen Storage Disease Type II-Pompe's DiseaseUnited States, France, Japan, Taiwan, United Kingdom
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II;Pompe's DiseaseCzechia, Taiwan, Belgium, Germany, Korea, Republic of, United States, Argentina, Australia, Austria, Brazil, Canada, Denmark, France, Hungary, Italy, Japan, Mexico, Netherlands, Poland, Portugal, Russian Federation, Spain, Switzerland, Turk... and more
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UMC UtrechtRecruitingDiabetes Mellitus, Type 2 | Blood Pressure | Diet Therapy | Cholesterol, LDL | Glycemic Control | Diet, Vegetarian | Diet, Vegan | Cardiometabolic Risk FactorsNetherlands
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Genzyme, a Sanofi CompanyCompletedPompe Disease | Glycogen Storage Disease Type II (GSD II) | Acid Maltase DeficiencyUnited States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
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Genzyme, a Sanofi CompanyCompletedPompe Disease | Glycogen Storage Disease Type II (GSD II)United States, Russian Federation, United Kingdom, Bulgaria, India, Ukraine
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Areeg El-GharbawyUltragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IUnited States
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Richard E. Ostlund Jr., MDNational Heart, Lung, and Blood Institute (NHLBI)CompletedCardiovascular Disease | Dyslipidemia | Coronary Heart Disease | Disorder of Cholesterol MetabolismUnited States
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ModernaTX, Inc.RecruitingGlycogen Storage DiseaseUnited States, Canada