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Clinical Trials on Congenital Lymphedema in Canada
Total 592 results
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Fundación Pública Andaluza Progreso y SaludCompletedArteriovenous Fistula Renal Dialysis Devices ObstructionSpain
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Sideris PharmaceuticalsTerminatedIron Overload | Beta-ThalassemiaUnited States, Canada, Lebanon, Thailand, Turkey
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... and other collaboratorsRecruiting
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, United Kingdom, Canada, Germany, Italy
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GLWL Research Inc.CompletedPrader-Willi SyndromeUnited States, Canada
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Abbott Medical DevicesRecruitingStroke | Patent Foramen OvaleUnited States, Germany, Canada, Switzerland, Italy, Portugal, United Kingdom
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingBiliary Atresia | Neonatal CholestasisUnited States, Canada
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GlaxoSmithKlineTerminatedTelangiectasia, Hereditary HemorrhagicUnited States, Canada
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Otsuka Canada Pharmaceutical Inc.RecruitingAutosomal Dominant Polycystic Kidney Disease (ADPKD)Canada
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AlbireoEnrolling by invitationBiliary AtresiaSpain, United States, Netherlands, Malaysia, Canada, Germany, Turkey, Italy, France, Australia, Poland, New Zealand
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Novartis PharmaceuticalsCompletedSickle Cell AnemiaTurkey, United States, Germany, Canada, United Kingdom, Israel, South Africa
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University of California, DavisUniversity of Alberta; St. Justine's HospitalRecruitingNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXS | Mental Retardation, X LinkedUnited States, Canada
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ShireTerminatedBeta-Thalassemia | Transfusional Iron OverloadUnited States, Lebanon, Canada, Italy, Turkey
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Spain, Japan, Canada, United Kingdom, Korea, Republic of, Ireland, Thailand, Italy, Turkey, Denmark, Brazil, France, Germany, Netherlands, Switzerland
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedHepatitis C | ThalassemiaUnited States, United Kingdom, Canada
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Pediatric Spine FoundationColumbia UniversityRecruitingEarly-Onset Scoliosis Deformity of SpineUnited States, Canada, Finland, Hong Kong
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Forma Therapeutics, Inc.RecruitingSickle Cell Disease | ThalassemiaUnited States, Lebanon, Canada
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University of North Carolina, Chapel HillThe Hospital for Sick Children; Washington University School of Medicine; McGill... and other collaboratorsRecruitingPrimary Ciliary Dyskinesia | Kartagener Syndrome | Primary Immune DeficiencyUnited States, Canada
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McGill University Health Centre/Research Institute...RecruitingDiabetes Mellitus, Type 1 | Wolfram Syndrome | Neonatal Diabetes | Monogenic Diabetes | Maturity-onset Diabetes in the Young (MODY) | Wolcott-Rallison Syndrome | Mitochondrial DiabetesCanada
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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CSL BehringCompletedCongenital Fibrinogen DeficiencyUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Hematological DiseasesUnited States, Belgium, Canada, France, Germany, Italy, United Kingdom
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Sharp HealthCareUniversity of Alabama at Birmingham; University of Pittsburgh; University of... and other collaboratorsRecruitingNeurodevelopmental AbnormalityUnited States, Ireland, Canada, Germany
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, Spain, Switzerland, Turkey, Germany, France, United Kingdom, Japan, Netherlands, Brazil, Canada, Czechia, Denmark, Italy, Korea, Republic of, Thailand
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI); National Center for Research... and other collaboratorsCompletedPrimary Ciliary DyskinesiaUnited States, Canada
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Novartis PharmaceuticalsCompletedTumors Characterized by Genetic Abnormalities of ALKAustralia, Belgium, Germany, Netherlands, Spain, Italy, Singapore, Korea, Republic of, United Kingdom, United States, Canada
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Active, not recruitingPortal Hypertension | Cholestasis | Liver Fibrosis | Biliary Atresia | Alagille Syndrome | Alpha1 Anti-Trypsin DeficiencyUnited States, Canada
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Novartis PharmaceuticalsActive, not recruitingSickle Cell Disease (SCD)United States, United Kingdom, Germany, Spain, Greece, Italy, Brazil, Lebanon, Turkey, Belgium, France, Jordan, India, Finland, Canada, Colombia, Netherlands, Oman, South Africa, Panama, Ghana
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McGill University Health Centre/Research Institute...RecruitingPeroxisome Biogenesis Disorder | Zellweger Spectrum Disorder | RCDP - Rhizomelic Chondrodysplasia Punctata | D-Bifunctional Protein Deficiency | Alpha-Methylacyl-CoA Racemase Deficiency | Peroxisomal Acyl-CoA Oxidase Deficiency | Peroxisomal Acyl-CoA Oxidase 2 Deficiency | ATP Binding Cassette Subfamily... and other conditionsCanada
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, United Kingdom, France, Greece, Italy, Spain, Belgium, Canada, Germany, Poland
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RezoluteCompletedCongenital HyperinsulinismUnited States, Denmark, United Kingdom, Russian Federation, Spain, Bulgaria, Canada, Georgia, Germany, Israel, Turkey
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Prolong PharmaceuticalsCompleted
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Merck KGaA, Darmstadt, GermanyMerck Serono S.A., GenevaCompletedTurner Syndrome | Idiopathic Growth Hormone DeficiencySpain, France, Canada, United Kingdom, Czech Republic, Argentina, Germany, Italy, Sweden
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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University Hospital, LilleCompletedGastroesophageal Reflux | Esophagus, BarrettFrance, Belgium, Canada, Luxembourg
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University of North Carolina, Chapel HillNational Institutes of Health (NIH); National Center for Research Resources... and other collaboratorsCompletedCystic Fibrosis | Primary Ciliary Dyskinesia | Kartagener Syndrome | PseudohypoaldosteronismUnited States, Canada
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Agios Pharmaceuticals, Inc.RecruitingPyruvate Kinase DeficiencyUnited States, Germany, Spain, Italy, United Kingdom, Czechia, France, Canada, Korea, Republic of, Netherlands, Turkey, Portugal, Denmark, Ireland, Switzerland, Thailand
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RezoluteRecruitingCongenital HyperinsulinismBulgaria, Canada, Denmark, France, Georgia, Germany, Greece, Israel, Oman, Qatar, Saudi Arabia, Spain, Turkey, United Arab Emirates, United Kingdom, Vietnam
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Shire Regenerative Medicine, Inc.TerminatedEpidermolysis BullosaUnited States, Spain, Austria, Canada, France, Germany, Poland, Portugal
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Duke UniversityEnrolling by invitationCleft Lip and Palate | Cleft Palate | Cleft LipUnited States, Canada
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Novartis PharmaceuticalsTerminatedSickle Cell DiseaseUnited Arab Emirates, Bahrain, Kuwait, Qatar, Saudi Arabia
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ApoPharmaTerminatedIron Overload | Sickle Cell Disease | Other AnemiasUnited States, United Kingdom, Egypt, Canada, Saudi Arabia
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
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Emory UniversityRecruitingSickle Cell DiseaseUnited States, Canada