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Clinical Trials on Congenital Myotonia in South Africa
Total 338 results
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Novartis PharmaceuticalsActive, not recruitingSickle Cell Disease (SCD)United States, United Kingdom, Germany, Spain, Greece, Italy, Brazil, Lebanon, Turkey, Belgium, France, Jordan, India, Finland, Canada, Colombia, Netherlands, Oman, South Africa, Panama, Ghana
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ArQule, Inc. (a wholly owned subsidiary of Merck...Worldwide Clinical TrialsTerminatedPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus SyndromeUnited States, Australia, Italy, Spain
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Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
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Duke UniversityNational Heart, Lung, and Blood Institute (NHLBI); RTI InternationalCompletedHematologic Diseases | Sickle Cell Disease | Anemia, Sickle Cell | Genetic DiseaseUnited States
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); St. Jude Children... and other collaboratorsEnrolling by invitationAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia | Multisystem ProteinopathyUnited States, South Africa, Germany
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Castle Creek Pharmaceuticals, LLCTerminatedEpidermolysis Bullosa SimplexUnited States, Israel, Australia, Austria, France, Germany, Netherlands, United Kingdom
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Women and Infants Hospital of Rhode IslandPerkinElmer, Inc.CompletedDown Syndrome | Trisomy 18 | Trisomy 13United States, Canada, Italy
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Hoffmann-La RocheRecruitingAngelman SyndromeUnited States, Australia, Spain, Italy, France, Germany
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Abbott Medical DevicesActive, not recruitingVentricular Septal DefectsUnited States, Canada
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Netherlands, Portugal
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Micelle BioPharma IncUnknownSickle Cell DiseaseUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsFrance, United States, Sweden, Serbia, Turkey, United Kingdom, Malaysia, Brazil, Former Serbia and Montenegro, Japan, South Africa
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SCAD AlliancePERFUSE Study GroupRecruitingSpontaneous Coronary Artery DissectionUnited States, Australia
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Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom
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Wake Forest University Health SciencesPatient-Centered Outcomes Research Institute; Atrium Health Levine Cancer InstituteCompletedSickle Cell DiseaseUnited States
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Mast Therapeutics, Inc.CompletedSickle Cell DiseaseUnited States
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Sydney Children's Hospitals NetworkJohns Hopkins University; Children's Hospital of Philadelphia; University of... and other collaboratorsUnknownCharcot-Marie-Tooth DiseaseUnited States, Australia, Italy
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bluebird bioCompletedSickle Cell DiseaseUnited States
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QED Therapeutics, Inc.RecruitingHypochondroplasiaUnited States, Australia, Norway, Portugal, Singapore, Spain, Canada, France, Germany, Sweden, United Kingdom
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Novartis PharmaceuticalsCompletedSickle Cell Disease (SCD)United States
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Scioderm, Inc.Amicus TherapeuticsTerminatedEpidermolysis BullosaPoland, Spain, Serbia, Netherlands, United States, Austria, Australia, Israel, Germany, France, United Kingdom, Lithuania
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CSL BehringCompletedSickle Cell DiseaseUnited States, United Kingdom, Netherlands
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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Johns Hopkins UniversityMedtronicCompletedTetralogy of Fallot | Pulmonary Regurgitation | Pulmonary StenosisUnited States
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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Medtronic EndovascularCompletedFistula | Arteriovenous Fistula | Arteriovenous Fistula Stenosis | Arteriovenous Fistula OcclusionNew Zealand, United States, Japan
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Ovid Therapeutics Inc.CompletedAngelman SyndromeUnited States, Israel
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health (NIH)CompletedSickle Cell AnemiaUnited States
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Pediatric Spine FoundationColumbia UniversityRecruitingEarly-Onset Scoliosis Deformity of SpineUnited States, Canada, Finland, Hong Kong
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Imara, Inc.TerminatedSickle Cell DiseaseUnited States, Oman, Italy, United Kingdom, Lebanon, Greece, Morocco, Tunisia, Ghana, Kenya, Netherlands, Senegal, Uganda
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ShireTakeda Development Center Americas, Inc.Completed
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Beam Therapeutics Inc.RecruitingSickle Cell DiseaseUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle CellUnited States
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaItaly, Spain, Serbia, United States, Australia, Netherlands, Austria, Germany, Israel, Lithuania, France, United Kingdom, Poland
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AstraZenecaCompletedSickle Cell DiseaseUnited States, Italy, France, United Kingdom, Turkey, Egypt, Lebanon, Kenya
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bluebird bioEnrolling by invitationSickle Cell DiseaseUnited States, France
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle CellUnited States
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Vifor (International) Inc.FortreaCompletedSickle Cell DiseaseUnited States, France, Greece, Lebanon, United Kingdom
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W.L.Gore & AssociatesRecruitingStroke | PFO - Patent Foramen OvaleUnited States
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Amryt Research LimitedCompletedEpidermolysis BullosaUnited States, Spain, Israel, Australia, France, Denmark, Switzerland, Italy, Hong Kong, Argentina, Austria, Brazil, Chile, Colombia, Czechia, Georgia, Germany, Greece, Hungary, Ireland, Romania, Russian Federation, Serbia, Singapore, U... and more
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bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
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ApoPharmaTerminatedIron Overload | Sickle Cell Disease | Other AnemiasUnited States, United Kingdom, Egypt, Canada, Saudi Arabia
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University of Alabama at BirminghamMedtronic; The Children's Tumor FoundationTerminatedNF1 | Congenital Pseudarthrosis of TibiaUnited States, Australia
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Sequenom, Inc.PRA Health SciencesCompletedPregnancy | Down Syndrome | Aneuploidy | Edwards SyndromeUnited States, France
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rEVO BiologicsCompletedAntithrombin Deficiency, CongenitalFrance, United Kingdom, Germany, United States, Sweden, Italy
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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QOL Medical, LLCRecruitingCongenital Sucrase-Isomaltase Deficiency | CSID | Sucrase Isomaltase DeficiencyUnited States
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Seoul National University HospitalAsan Medical Center; Johannes Gutenberg University Mainz; Gyeongsang National... and other collaboratorsActive, not recruitingIntracerebral Hemorrhage | Cerebral Cavernous MalformationKorea, Republic of
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CelgeneAcceleron Pharma Inc. (a wholly owned subsidiary of Merck Sharp and Dohme...CompletedBeta-Thalassemia | Erythrocyte TransfusionUnited States, Israel, Australia, Turkey, Taiwan, Malaysia, United Kingdom, Canada, Thailand, France, Lebanon, Italy, Bulgaria, Greece, Tunisia