- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital Myotonic Dystrophy in Australia
Total 331 results
-
Melbourne HealthCompletedRenal Failure | Left Ventricular HypertrophyAustralia
-
IpsenCompletedCervical DystoniaFrance, Belgium, Czechia, Australia, Poland, Portugal, Ukraine, Hungary, Russian Federation, Austria, Germany
-
Ethicare GmbHUnknownHeart Failure | Dilated Cardiomyopathy | Congenital Heart DiseaseAustria, United Kingdom, Netherlands, Serbia, Hungary
-
ActelionCompletedPulmonary Arterial HypertensionCanada, United Kingdom, Italy, United States, Netherlands, Australia, Austria, Belgium, France, Germany, Spain
-
PTC TherapeuticsCooperative International Neuromuscular Research Group; The John Walton Muscular...Active, not recruitingMuscular Dystrophy, DuchenneGermany, France, United Kingdom, Brazil, Italy, Austria, Sweden, Czechia, Greece, Hungary, Israel, Latvia, Norway, Portugal, Romania, Slovenia
-
Children's Hospital Medical Center, CincinnatiUniversity of Pittsburgh; Vanderbilt University Medical Center; Children's Hospital... and other collaboratorsNot yet recruitingDepression, Postpartum | Neurodevelopmental Disorders | Heart Defects, Congenital | Trauma, Psychological | Anxiety in PregnancyUnited States, Australia
-
NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
-
Medical University of GrazUnknownEsophageal AtresiaAustria
-
ActelionCompletedPulmonary Arterial Hypertension Related to Eisenmenger PhysiologyCanada, United Kingdom, Italy, United States, Netherlands, Australia, Austria, Belgium, France, Germany, Spain
-
Philip MoonsCompletedHeart Defects, CongenitalNorway, Taiwan, Belgium, Netherlands, United States, Sweden, Switzerland, Canada, Argentina, Australia, France, India, Italy, Japan, Malta
-
Axsome Therapeutics, Inc.UnknownReflex Sympathetic Dystrophy | Complex Regional Pain SyndromeUnited States, United Kingdom, Australia, Canada
-
Kirby InstituteNational Heart, Lung, and Blood Institute (NHLBI); St Vincent's Hospital, Sydney and other collaboratorsCompletedGlucose Metabolism Disorders | Metabolic Diseases | HIV Infections | Cardiovascular Disease | Dyslipidemias | LipodystrophyAustralia
-
Garvan Institute of Medical ResearchCompletedPrader-Willi SyndromeAustralia
-
PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
-
ActelionCompletedClinical Study Assessing the Efficacy and Safety of Macitentan in Fontan-palliated Subjects (RUBATO)Congenital Heart DiseaseUnited States, United Kingdom, Taiwan, Germany, France, Poland, China, Australia, Czechia, Canada, Denmark, New Zealand
-
Cardiac Regeneration Technologies, LLCUnknownReduced Left Ventricular Function Defined as LVEF < 50% | Regional Left Ventricular Wall Motion AbnormalitiesAustria
-
Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Basal Cell CarcinomaAustralia
-
Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
-
Medacta International SARecruitingArthrosis | Congenital Hip Dysplasia | Traumatic Arthritis | Rheumatoid Polyarthritis | Avascular Necrosis of the Femoral HeadAustria, Italy, Switzerland, United Kingdom
-
KU LeuvenCompletedCongenital Heart DiseaseBotswana, United States, Korea, Republic of, Belgium, Sweden, France, Switzerland, Denmark, Pakistan, Norway, Taiwan, Malta, Brazil, Bulgaria, India, Austria, Argentina, Australia, Cameroon, Canada, Chile, Colombia, Ethiopia, Greece, Italy and more
-
Zimmer BiometActive, not recruitingAvascular Necrosis | Inflammatory Arthritis | Osteoarthritis, Hip | Congenital Hip Dysplasia | Post-traumatic; Arthrosis | Rheumatoid Arthritis With Adequate Bone QualityNetherlands, Finland, Belgium, France, Spain, Australia, Canada, United Kingdom
-
University of ZurichActive, not recruitingTransposition of Great VesselsSpain, Switzerland, Austria, Netherlands, France
-
PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
-
Encoded TherapeuticsTerminatedDravet SyndromeUnited States, Spain, Australia, United Kingdom
-
PYC TherapeuticsNot yet recruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
-
The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
-
Sydney Local Health DistrictEnrolling by invitationClass III Malocclusion | UnderbiteAustralia
-
Murdoch Childrens Research InstituteNational Health and Medical Research Council, Australia; Royal Children's Hospital and other collaboratorsRecruitingCommunicable Diseases | Quality of Life | Inflammation | Obesity | Congenital Abnormalities | Genetics | Healthy Aging | Child Development | Diet | Mental Health | Disability | Injuries | Cognition | Child Health | Environmental Exposure | Noncommunicable Diseases | Physical Fitness | Intergenerational Relations | Social Determinants... and other conditionsAustralia
-
RHEACELL GmbH & Co. KGRecruiting
-
Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
-
Eloxx Pharmaceuticals, Inc.Recruiting
-
LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
-
Neuren Pharmaceuticals LimitedRecruiting
-
Paragonix TechnologiesEnrolling by invitationHeart Diseases | Heart Failure | Heart Defects, CongenitalUnited States, Spain, Austria, United Kingdom
-
Medical University InnsbruckCompletedPectus Excavatum | Pectus CarinatumAustria
-
University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
-
Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminated
-
Nacuity Pharmaceuticals, Inc.Foundation Fighting BlindnessActive, not recruitingUsher SyndromesAustralia
-
Medical University of GrazRecruitingMissing ToothAustria
-
IpsenCompletedIdiopathic Cervical DystoniaBelgium, France, United Kingdom, Portugal, Germany, Australia, Czechia, Netherlands, Russian Federation
-
Murdoch Childrens Research InstituteRoyal Children's Hospital; Peter MacCallum Cancer Centre, AustraliaNot yet recruitingArteriovenous Malformations | Vascular Malformations | MAP2K1 Gene Mutation | PIK3CA-related Overgrowth Spectrum | Vascular Anomalies | Lymphangioma | Lymphatic Malformation | KRAS G12D | Venous Malformation | Vascular Anomaly | KRAS G12C | PI3K Gene Mutation | Slow-Flow Vascular Malformation | Fast-Flow Vascular... and other conditionsAustralia
-
Paracelsus Medical UniversityMedAlliance Swiss Medical TechnologyActive, not recruiting
-
University of ZurichCompleted
-
Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Austria, Netherlands, Portugal
-
DePuy InternationalTerminatedOsteoarthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral Fractures | Perthes DiseaseAustria, Germany, Italy
-
Queen Silvia Children's Hospital, Gothenburg, SwedenSahlgrenska University Hospital, Sweden; Swedish Heart Lung FoundationRecruitingAortic Valve Stenosis | Congenital Heart Disease | Hypoplastic Left Heart Syndrome | Fetal Cardiac DisorderUnited States, Austria, Canada, Finland, Germany, Poland, Spain, Sweden
-
Premier Specialists, AustraliaUnknownEpidermolysis Bullosa Simplex | Epidermolysis Bullosa Simplex Kobner | Weber-Cockayne SyndromeAustralia
-
Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
-
bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand