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Clinical Trials on Congenital Bone Marrow Failure Syndromes
Total 12502 results
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Institute of Hematology & Blood Diseases HospitalRecruitingSevere Aplastic AnemiaChina
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Novartis PharmaceuticalsCompletedSevere Aplastic AnemiaSpain, Italy, Hong Kong, Thailand, Korea, Republic of, Mexico, Turkey, India, Brazil
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Michael Pulsipher, MDActive, not recruitingSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic AnemiaUnited States
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Institute of Hematology & Blood Diseases HospitalTerminatedRefractory Aplastic AnemiaChina
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European Society for Blood and Marrow TransplantationEnrolling by invitationSevere Aplastic AnemiaFrance
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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European Society for Blood and Marrow TransplantationNovartis; PfizerCompletedSevere Aplastic AnemiaSwitzerland, Netherlands, France, Italy, Spain, United Kingdom
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Wu XiaoxiongUnknown
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Sidney Kimmel Comprehensive Cancer Center at Johns...TerminatedSevere Aplastic AnemiaUnited States
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Cancer Institute and Hospital, Chinese Academy...UnknownSevere Aplastic AnemiaChina
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Asan Medical CenterUnknownAcquired Aplastic AnemiaKorea, Republic of
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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Jiangsu HengRui Medicine Co., Ltd.Recruiting
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Institute of Hematology & Blood Diseases HospitalRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States
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National Institutes of Health Clinical Center (CC)National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAgranulocytosis | Anemia, Aplastic | Blood Disease
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Stanford UniversityNational Institutes of Health (NIH)CompletedMyelodysplastic Syndromes | Myeloproliferative Disorders | Myelodysplastic Syndromes (MDS) | Blood and Marrow Transplant (BMT) | Myeloproliferative Disorders (MPD)United States
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Dana-Farber Cancer InstituteCompletedMyelodysplastic Syndromes (MDS)United States
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Burnasyan Federal Medical Biophysical CenterUnknownNeutropenic Enterocolitis | Myeloablative Chemotherapy Induced Bone Marrow AplasiaRussian Federation
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University of RochesterRecruitingLymphoma | Myelodysplastic Syndromes | Multiple Myeloma | Solid Tumor | Acute Leukemia | Aplastic Anemia | Chronic Leukemia | Immune Deficiency Disorder | Congenital Hematological Disorder | Metabolism DisorderUnited States
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Institute of Hematology & Blood Diseases Hospital...Jiangsu Hengrui Pharmaceuticals Co.,LtdRecruitingNon Severe Aplastic Anemia | UntreatedChina
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Jiangsu HengRui Medicine Co., Ltd.RecruitingTreatment-naive Severe Aplastic AnemiaChina
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Peking Union Medical College HospitalNot yet recruitingNon Severe Aplastic AnemiaChina
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AmgenWithdrawn
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New York Medical CollegeCompletedLymphoma | Leukemia | Sickle Cell Disease | Histiocytosis | Immunodeficiencies | Inborn Errors of Metabolism | Bone Marrow Failure | Beta ThalassemiaUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Radboud University Medical CenterRecruitingMyelodysplastic Syndromes (MDS)Denmark, Switzerland, Serbia, Austria, Croatia, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Romania, Spain, Sweden, United Kingdom
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TakedaWithdrawn
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TJ Biopharma Co., Ltd.Recruiting
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI)RecruitingMyelodysplastic Syndromes (MDS)United States, Israel
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AbbVieCelgene; Genentech, Inc.CompletedMyelodysplastic Syndromes (MDS)United States, Australia, Germany
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndromes (MDS)United States, Australia, Canada, France, Germany, Italy, United Kingdom
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The First Affiliated Hospital with Nanjing Medical...UnknownMyelodysplastic Syndromes (MDS)China
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National Cancer Institute (NCI)RecruitingMyelodysplastic SyndromesUnited States
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National Cancer Institute (NCI)RecruitingMyelodysplastic SyndromesUnited States
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Mikkael Sekeres, MDBristol-Myers Squibb; CelgeneRecruitingMyelodysplastic SyndromesUnited States
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Josep Carreras Leukaemia Research InstituteCelgeneRecruitingMyelodysplastic SyndromesSpain
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University of Erlangen-Nürnberg Medical SchoolNovartis PharmaceuticalsTerminated
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Centre Hospitalier Universitaire, AmiensUnknownMyelodysplastic SyndromesFrance
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Memorial Sloan Kettering Cancer CenterWeill Medical College of Cornell University; YUKIGUNI COMPANYCompletedMyelodysplastic SyndromeUnited States
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Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
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Peking Union Medical College HospitalNot yet recruitingMyelodysplastic SyndromesChina
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McMaster UniversityCBSRecruitingMyelodysplastic SyndromeCanada
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Stanford UniversityNotable Labs Inc.Active, not recruitingMyelodysplastic SyndromesUnited States
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Michael PfeilstöckerCelgene CorporationCompletedMyelodysplastic SyndromesAustria