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Clinical Trials on Congenital Hemolytic Anemia
Total 11828 results
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Chinook Therapeutics U.S., Inc.Active, not recruitingDiabetic Kidney Disease | Focal Segmental Glomerulosclerosis | Immunoglobulin A Nephropathy | IgA Nephropathy | Diabetic Nephropathy Type 2 | Alport SyndromeUnited States, Spain, Korea, Republic of, Australia, Italy, United Kingdom
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UNC Lineberger Comprehensive Cancer CenterLantheus Medical ImagingCompletedKidney Disease, Chronic | Von-Hippel LindauUnited States
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Reata, a wholly owned subsidiary of BiogenTerminatedChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney | Alport SyndromeUnited States, France, Australia, Japan, Spain, Puerto Rico
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CENTOGENE GmbH RostockWithdrawnLung Diseases | Eye Abnormalities | Lysosomal Storage Disease | Macroglossia | Obstructive Sleep ApnoeaGermany, India, Sri Lanka, Egypt
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Azienda Ospedaliero-Universitaria Consorziale Policlinico...Institute of Biomembranes, Bioenergetics and Molecular Biotechnologies; Istituti... and other collaboratorsCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD) | IgA Nephropathy (IgAN) | Diabetic Kidney Disease (DKD) | Advanced-Chronic Kidney Disease (CKD)Italy
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MedDay Pharmaceuticals SACompletedCharcot-Marie-Tooth Disease | Peripheral Neuropathy | Chronic Inflammatory Demyelinating Polyneuropathy | Charcot-Marie-Tooth Disease Type 1A | Charcot-Marie-Tooth Disease, Type 1B | Anti-MAG NeuropathyFrance
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Oregon Health and Science UniversityTerminatedSmith-Lemli-Opitz SyndromeUnited States
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Heart of England NHS TrustUniversity of Warwick; University of BirminghamCompletedLung Neoplasms | Pulmonary Disease, Chronic Obstructive | Surgery | Cystic Fibrosis | Mesothelioma | Empyema, Pleural | Pectus Excavatum | Pectus CarinatumUnited Kingdom
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Eunice Kennedy Shriver National Institute of Child...WithdrawnSmith-Lemi-Opitz Syndrome
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University of ZurichUniversity Children's Hospital, Zurich; Ehlers-Danlos Network, SwitzerlandCompletedObstructive Sleep Apnea | Ehler's Danlos SyndromeSwitzerland
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University of ZurichUniversity Children's Hospital, Zurich; Ehlers-Danlos Network, SwitzerlandCompletedObstructive Sleep Apnea | Ehlers-Danlos SyndromeSwitzerland
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French National Agency for Research on AIDS and...Celgene CorporationTerminatedHIV Infection Associated Kaposi DiseaseFrance
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Eunice Kennedy Shriver National Institute of Child...CompletedPregnancy | Smith-Lemli-Opitz SyndromeUnited States
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National Center for Research Resources (NCRR)Oregon Health and Science UniversityUnknownSmith-Lemli-Opitz SyndromeUnited States
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Anagnostou, Evdokia, M.D.The Hospital for Sick Children; Canadian Institutes of Health Research (CIHR); Alberta Health services and other collaboratorsNot yet recruitingAnxiety Disorders | Generalized Anxiety Disorder | Anxiety | Tuberous Sclerosis | ADHD | Neurodevelopmental Disorders | Autism Spectrum Disorder | Fragile X Syndrome | Social Anxiety | Social Anxiety Disorder | Agoraphobia | Tourette Syndrome | Tic Disorders | Autism | ADHD Predominantly Inattentive Type | ADHD - Combined... and other conditionsCanada
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Prehospital Center, Region ZealandNot yet recruitingDrowning | Drowning; Anoxia | Drowning, Near | Drowning; Asphyxia | Drowning and Nonfatal Submersion | Drowning or Immersion of Unknown Intent | Drowning and Submersion, Undetermined Intent | Drowning and Submersion While in Bath-Tub | Drowning and Submersion While in Natural Water | Drowning and Submersion... and other conditionsDenmark
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Prehospital Center, Region ZealandNot yet recruitingDrowning | Drowning; Anoxia | Drowning, Near | Drowning; Asphyxia | Drowning or Immersion of Unknown Intent | Drowning and Submersion, Undetermined Intent | Drowning and Submersion While in Bath-Tub | Drowning and Submersion While in Natural Water | Drowning and Submersion Due to Sailboat Sinking | Drowning... and other conditionsDenmark
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Pamlab, Inc.InfoMedics, Inc.CompletedMild Cognitive Impairment | Vascular Dementia | Alzheimer's Disease | Early Memory LossUnited States
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St. Jude Children's Research HospitalWallace H. Coulter FoundationRecruitingIdentifying the Determinants of Bleeding and Hypermobility in Patients With Heavy Menstrual BleedingHypermobile Ehlers-Danlos Syndrome | Heavy Menstrual Bleeding | Hypermobility Syndrome (Disorder)United States
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Chinese University of Hong KongHong Kong Children's Hospital; Hong Kong Young Women's Christian AssociationRecruitingGastrointestinal Diseases | Vascular Diseases | Urologic Diseases | Neurodevelopmental Disorders | Autism Spectrum Disorder | Cleft Lip and Palate | Attention Deficit Hyperactivity Disorder | Developmental DelayHong Kong
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Medical College of WisconsinUniversity College, London; Indiana UniversityRecruitingFunctional Gastrointestinal Disorders | Postural Orthostatic Tachycardia Syndrome | Hypermobile Ehlers-Danlos Syndrome | Autonomic Nervous System Disease | Autonomic Nervous System ImbalanceUnited States
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RWTH Aachen UniversityDLR German Aerospace CenterRecruitingPostural Tachycardia Syndrome | Autonomic Neuropathy | Small Fiber Neuropathy | Ehlers-Danlos Syndrome Hypermobility TypeGermany
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Oslo University HospitalUniversity of Oslo; Ullevaal University Hospital; University Hospital, AkershusWithdrawnMicrocephaly | Hearing Loss | Mental Retardation | ChorioretinitisNorway
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Center for Vascular Pathology, MoscowCompletedVascular Diseases | Port-Wine Stain | Sturge-Weber Syndrome | Vascular Malformation | Capillary Malformation-Arteriovenous Malformation | Vascular TumorRussian Federation
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McGill University Health Centre/Research Institute...CompletedFamilial Dysautonomia | Tay Sachs Disease | Canavan DiseaseCanada
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Eunice Kennedy Shriver National Institute of Child...CompletedSmith-Lemli-Opitz SyndromeUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedEstimation of the Carrier Frequency and Incidence of Smith-Lemli-Opitz Syndrome in African AmericansSmith-Lemli-Opitz SyndromeUnited States
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Cambridge University Hospitals NHS Foundation TrustImperial College Healthcare NHS Trust; Royal Cornwall Hospitals TrustUnknownQuality of Life | Anosmia | SARS-CoV-2 | COVID19 | Olfactory Disorder | Microsomia | Smell DisorderUnited Kingdom
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Hospital Universitari de BellvitgeInstitut d'Investigació Biomèdica de BellvitgeUnknownHiv | Anal Cancer | HPV - Anogenital Human Papilloma Virus Infection | HSIL, High Grade Squamous Intraepithelial LesionsSpain
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Klinikum Oldenburg gGmbHDeutsche Gesellschaft für Kinderendokrinologie und Diabetologie (DGKED); Deutsche... and other collaboratorsRecruiting
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National Cancer Institute (NCI)RecruitingKidney Cancer | Renal Cell Carcinoma | Urologic Malignant Disorders | Familial Renal Cancer (FRC) | Clear Cell Renal CancerUnited States
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M.D. Anderson Cancer CenterPfizerTerminatedRenal Cell Carcinoma | Von Hippel-Lindau Syndrome | HemangioblastomaUnited States
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The Cleveland ClinicRecruitingCardiovascular Diseases | Lymphedema | Thrombosis | Vasculitis | Peripheral Artery Disease | Metabolic Disease | Lipedema | Thoracic Outlet Syndrome | Vasospasm | Venous Disease | Fibromuscular Dysplasia | May-Thurner Syndrome | Carotid Disease | Aneurysmal Disease | Non-Atherosclerotic Chronic Arterial Occlusive Disease and other conditionsUnited States
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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University of NebraskaCompletedSjogren-Larsson Syndrome (SLS)United States
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University of Alabama at BirminghamLakeshore Foundation; YMCA of Greater BirminghamActive, not recruitingStroke | Multiple Sclerosis | Cerebral Palsy | Parkinson Disease | Traumatic Brain Injury | Spinal Cord Injuries | Spina BifidaUnited States
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Aldeyra Therapeutics, Inc.CompletedSjögren-Larsson SyndromeUnited States
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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University of Split, School of MedicineGeneral Hospital ZadarUnknownEpilepsy | Cerebral Palsy | Diabetes Mellitus, Type 1 | Stress | Asthma | Chronic Disease | Autism Spectrum Disorder | Down Syndrome | Developmental Disability | Pervasive Developmental DisorderCroatia
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Novartis PharmaceuticalsCompletedLymphangioleiomyomatosis (LAM) | Tuberous Sclerosis Complex (TSC)United States, United Kingdom, Germany, Italy, Russian Federation, Netherlands, Japan, Canada, Poland, France, Spain
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Joanne Kurtzberg, MDAvailableCerebral Palsy | Apraxia of Speech | Hydrocephalus | Hypoxia Ischemia, Cerebral | Drowning; AnoxiaUnited States
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Motric BioRecruitingStroke | Multiple Sclerosis | Cerebral Palsy | Spinal Cord Injuries | Dystonia | Muscle Spasticity | Hereditary Spastic Paraplegia | Hypertonia, MuscleUnited States
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Jazz PharmaceuticalsRecruitingSeizure in Participants With Tuberous Sclerosis Complex | Seizure in Participants With Dravet Syndrome | Seizure in Participants With Lennox-Gastaut SyndromeUnited States
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Centre Hospitalier Universitaire VaudoisSwiss National Science FoundationRecruitingKallmann Syndrome | Hypogonadotropic Hypogonadism | Hypothalamic Amenorrhea | Polycystic Ovarian Syndrome | Precocious Puberty | Cleft Lip and Palate | Cleft Palate | Cleft LipSwitzerland
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National Institutes of Health Clinical Center (CC)Enrolling by invitationAdenocarcinoma | Renal Cell Carcinoma | Prostate Cancer | Prostate Neoplasms | Von Hippel Lindau DiseaseUnited States
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Assistance Publique - Hôpitaux de ParisCompletedSeckel Syndrome | Microcephalic Osteodysplastic Primordial Dwarfism Type IIFrance
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Boston Children's HospitalCompletedSmith-Lemli-Opitz SyndromeUnited States
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Forbes Porter, M.D.Eunice Kennedy Shriver National Institute of Child Health and Human Development...Completed
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Medical University of GrazCompletedSkin Cancer | Basal Cell Nevus Syndrome | Xeroderma PigmentosumAustria
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Alexey Danilov, MDGilead Sciences; Oregon Health and Science UniversityCompletedAnemia | Mantle Cell Lymphoma | Marginal Zone Lymphoma | Lymphoplasmacytic Lymphoma | Recurrent Small Lymphocytic Lymphoma | Refractory Chronic Lymphocytic Leukemia | Hairy Cell Leukemia | Richter Syndrome | Recurrent Chronic Lymphocytic Leukemia | Refractory Small Lymphocytic Lymphoma | Grade 1 Follicular... and other conditionsUnited States