- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Congenital Malformations
Total 8890 results
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Montefiore Medical CenterNovartis PharmaceuticalsWithdrawnHyperinsulinism | Insulinoma | Congenital Hyperinsulinism
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The Hospital for Sick ChildrenCompletedZellweger Syndrome | Peroxisome Biogenesis DisordersCanada
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University of ThessalyCompletedDiabetes Mellitus, Type 2 | Insulin Resistance | PreDiabetes | Beta-ThalassemiaGreece
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St. Joseph's Hospital and Medical Center, PhoenixBanner Alzheimer's Institute, Phoenix; Translational Genomics Research Institute...CompletedDown Syndrome | Alzheimer's DementiaUnited States
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University of AarhusAarhus University Hospital; University of Southern Denmark; Sygehus Lillebaelt; Hospital of South West JutlandCompleted
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University Hospital, BonnCompletedPseudoxanthoma ElasticumGermany
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney DiseaseNetherlands
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CorinWithdrawnRheumatoid Arthritis | Osteoarthritis, Knee | Post-Traumatic Osteoarthritis of Knee | Varus Deformity, Not Elsewhere Classified, Knee | Valgus Deformity, Not Elsewhere Classified, Knee | Flexion Deformity, Knee | Fracture of Distal End of Femur | Fracture of Upper End of Tibia
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Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney DiseaseJapan
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCerebrovascular Disorders | Anemia, Sickle Cell | Blood Disease | Cerebral Embolism and Thrombosis
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University Hospital, Basel, SwitzerlandUniversity Hospital Inselspital, Berne; Desirée and Niels Yde's Foundation,...CompletedEndogenous Hyperinsulinaemic HypoglycaemiaSwitzerland
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Nationwide Children's HospitalCompletedAdrenal Insufficiency | Prader Willi SyndromeUnited States
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Bezmialem Vakif UniversityCompleted
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Hospices Civils de LyonUnknownEhlers-Danlos Syndrome Hypermobility TypeFrance
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Institut Universitari DexeusCompletedPolycystic Ovary Syndrome | Hyperandrogenism | Anovulation
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Kyorin UniversityOtsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney DiseaseJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsJapan
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Singapore General HospitalShanghai Yueyang Integrated Medicine Hospital; Singapore Bao Zhong Tang TCM...CompletedMyelodysplastic Syndrome (MDS) | Myelofibrosis (MF) | Thalassemia Intermedia | Aplastic Anaemia (AA)Singapore
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsFrance
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsFrance, United Kingdom, Spain, Israel, Poland, Turkey, Hungary
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States, Denmark, France, United Kingdom
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Children's Oncology GroupNational Cancer Institute (NCI)Completed
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Assistance Publique - Hôpitaux de ParisCompleted
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Washington University School of MedicineNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Sickle Cell AnemiaUnited States
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University of KansasCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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French Cardiology SocietyNational Research Agency, France; Société Française de Médecine VasculaireCompletedHealthy Volunteers | Vascular Ehlers Danlos SyndromeFrance
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Taipei Medical University WanFang HospitalCompleted
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University of KansasCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Noonan Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Adult Growth Hormone Deficiency | Genetic Disorder | Foetal Growth Problem | Small for Gestational AgeIsrael, Saudi Arabia, Spain, Argentina, Russian Federation, Germany, Netherlands, Italy, Belgium, United Kingdom, Slovenia, Ireland, Sweden, Denmark, Hungary, Finland, Norway, France, Czechia, Lithuania, Luxembourg, Serbia, Switzerland
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Children's Hospital Medical Center, CincinnatiRecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello Syndrome | SYNGAP1-Related Intellectual Disability | DLG4 | RAS Mutation | Noonan Syndrome With Multiple Lentigines | Noonan Neurofibromatosis Syndrome | Smith-Kingsmore Syndrome | MTOR Gene Mutation | GATOR-1 Gene... and other conditionsUnited States
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Masonic Cancer Center, University of MinnesotaNational Cancer Institute (NCI)TerminatedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Graft Versus Host Disease | Diamond-blackfan AnemiaUnited States
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Milton S. Hershey Medical CenterUnknownSarcoma | Lymphoma | Unspecified Childhood Solid Tumor, Protocol Specific | Myelodysplastic Syndromes | Leukemia | Fanconi Anemia | Neuroblastoma | Childhood Langerhans Cell HistiocytosisUnited States
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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University of Colorado, DenverUniversity of MarylandRecruitingPolycystic Kidney, Autosomal DominantUnited States
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Dufresne, Craig, MD, PCRecruitingFreeman-Sheldon Syndrome | Whistling Face Syndrome | Freeman-Sheldon Syndrome Variant | Sheldon-Hall Syndrome | Gordon Syndrome | Arthrogryposis Distal Type 3 | Arthrogryposis Distal Type 1 | Freeman-Burian SyndromeUnited States
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Murdoch Childrens Research InstituteNational Health and Medical Research Council, Australia; Royal Children's Hospital and other collaboratorsRecruitingCommunicable Diseases | Quality of Life | Inflammation | Obesity | Congenital Abnormalities | Genetics | Healthy Aging | Child Development | Diet | Mental Health | Disability | Injuries | Cognition | Child Health | Environmental Exposure | Noncommunicable Diseases | Physical Fitness | Intergenerational Relations | Social Determinants... and other conditionsAustralia
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Vanderbilt University Medical CenterVanderbilt Kennedy CenterRecruitingAlzheimer Disease | Down Syndrome | Down Syndrome, Partial Trisomy 21United States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Centre Hospitalier Intercommunal CreteilEtablissement Français du Sang; Centre National de la Recherche Scientifique...RecruitingSickle Cell Disease | Stenosis | Cerebral IschemiaFrance
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Inspire Medical Systems, Inc.National Institutes of Health (NIH); National Institute on Deafness and Other...RecruitingObstructive Sleep Apnea | Down SyndromeUnited States
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...CompletedBody Weight Changes | Sarcopenia | Prader Labhart Willi SyndromeTaiwan
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McMaster UniversityCompletedPolyuria | Autosomal Dominant Polycystic KidneyCanada
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Zagazig UniversityCompletedVitamin D Deficiency | Sickle Cell Disease | Bone Mineral Density | Health Related Quality of Life | Hand Grip StrengthEgypt
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationObstructive Sleep Apnea | Down SyndromeUnited States
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University Hospital, GrenobleCompletedSleep Apnea, Obstructive | Down Syndrome | PolysomnographyFrance
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Servei Central d' AnestesiologiaCompletedEhlers-Danlos Syndrome | Craniocervical SyndromeSpain
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Regional Hospital HolstebroCompletedChronic Kidney Diseases | Polycystic Kidney, Autosomal DominantDenmark
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Bezmialem Vakif UniversityCompletedCystic Fibrosis | Primary Ciliary DyskinesiaTurkey
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National Heart, Lung, and Blood Institute (NHLBI)CompletedDiabetes Mellitus | Heart Disease | Thalassemia | HemochromatosisUnited States
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Hospices Civils de LyonUnknownWilliams-Beuren Syndrome | Micro-duplication 7q11.23 Syndrome | VasculopathyFrance