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Clinical Trials on Crigler Najjar-szindróma, 1. típus
Total 12 results
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Assistance Publique - Hôpitaux de ParisUnknownChildren | Crigler Najjar SyndromeFrance
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Promethera TherapeuticsCompletedUrea Cycle Disorders | Crigler Najjar SyndromeBelgium
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University Medical Center GroningenErasmus Medical Center; De Najjar StichtingCompleted
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Promethera TherapeuticsCompletedUrea Cycle Disorders | Crigler Najjar SyndromeIsrael, United Kingdom, Belgium, France, Italy
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Audentes TherapeuticsCompletedCrigler-Najjar SyndromeIsrael, United States, United Kingdom
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Audentes TherapeuticsTerminatedCrigler-Najjar SyndromeIsrael, United States, United Kingdom
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GenethonRecruitingCrigler-Najjar SyndromeItaly, France, Netherlands
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Cellaion SAEnrolling by invitationUrea Cycle Disorder | Crigler-Najjar Syndrome | Acute on Chronic Liver FailureBelgium, Spain, France, Bulgaria, Poland
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Swedish Medical CenterWithdrawnLevator Ani SyndromeUnited States
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Walter Reed Army Medical CenterUnknownLevator Ani Syndrome With Pain and/or Constipation Symptoms.United States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium