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Clinical Trials on Disease or R Group Histiocytoses in New Zealand
Total 3694 results
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Smith & Nephew, Inc.RecruitingAvascular Necrosis | Non-inflammatory Degenerative Joint Disease, Including Osteoarthritis | Requires Correction of Functional Deformity | Requires Treatment of Fractures That Were Unmanageable Using Other TechniquesNew Zealand, Australia, Hong Kong
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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Intellia TherapeuticsNot yet recruitingHereditary AngioedemaFrance, New Zealand, United Kingdom
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FibroGenAstraZeneca; Astellas Pharma IncTerminatedPrimary MDS (Very Low, Low or Intermediate IPSS-R With <5% Blasts)United States, Australia, Belgium, Germany, Israel, Italy, Korea, Republic of, Russian Federation, Spain, United Kingdom, France, Turkey, Canada, Denmark, India, Poland
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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University of RochesterNational Institute on Aging (NIA)Recruiting
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Dermatology Specialties Limited PartnershipCompletedTuberous Sclerosis | Facial AngiofibromaUnited States, Taiwan, Serbia, Spain, Australia, Czechia, Hungary, New Zealand, Slovakia
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Arrowhead PharmaceuticalsCompletedDyslipidemias | Hypertriglyceridemia | Familial HypercholesterolemiaAustralia, New Zealand
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AlexionCompletedWilson DiseaseUnited States, New Zealand, United Kingdom
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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National Eye Institute (NEI)CompletedNiemann Pick DiseasesUnited States, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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PharmaxisCompletedCystic FibrosisAustralia, New Zealand
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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National Institute of Allergy and Infectious Diseases...CompletedBacterial Infections | Group B StreptococcusUnited States
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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University of California, San FranciscoNational Institute of Neurological Disorders and Stroke (NINDS)CompletedEpilepsy | Infantile Spasms | Lennox-Gastaut Syndrome | Polymicrogyria | Localization-related Epilepsy | Periventricular HeterotopiasUnited States, Argentina, Australia
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University of Witten/HerdeckeCompletedSensitivity Training Groups | Complication, Cardio-respiratoryGermany
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The University of QueenslandTelethon Kids InstituteCompletedBronchiectasis | Cystic FibrosisAustralia, New Zealand
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NYU Langone HealthCompletedEpilepsy | Tuberous Sclerosis Complex | Focal Cortical DysplasiaUnited States
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Chile, France, Germany, Italy, Japan, Netherlands, Portugal, Spain, Tunisia, Turkey, United Kingdom
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Lassen Therapeutics 1 PTY LTDRecruitingThyroid Eye Disease | Pulmonary FibrosisAustralia, New Zealand, Hong Kong
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National Niemann-Pick Disease FoundationIcahn School of Medicine at Mount Sinai; Engage Health Inc.CompletedNiemann-Pick DiseasesUnited States
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Genzyme, a Sanofi CompanyTerminatedNiemann-Pick Disease | Acid Sphingomyelinase DeficiencyUnited States
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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Gilead SciencesCompletedLong QT SyndromeUnited States, Romania, New Zealand, Germany
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Arrowhead PharmaceuticalsTerminatedCystic Fibrosis, PulmonaryAustralia, New Zealand
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Mandos LLCTerminatedNiemann-Pick Type C DiseaseUnited States
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Akesobio Australia Pty LtdCompletedAtopic DermatitisNew Zealand, Australia
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Icahn School of Medicine at Mount SinaiPfizerRecruitingFocus Group | Screening ToolUnited States
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Dana-Farber Cancer InstituteNovartis PharmaceuticalsCompletedTuberous Sclerosis Complex | TSC1 | TSC2 | MTORUnited States
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Columbia UniversityTerminatedLymphoma | Leukemia | Histiocytosis | Bone Marrow Failure Syndromes | ImmunodeficienciesUnited States
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Cyclo Therapeutics, Inc.CompletedNiemann-Pick Disease, Type C1United States
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Yale UniversityNational Cancer Institute (NCI)TerminatedKidney Cancer | Head and Neck Cancer | Lung Cancer | Brain and Central Nervous System Tumors | Intraocular Melanoma | Melanoma (Skin) | Pheochromocytoma | Islet Cell Tumor | Gastrointestinal Carcinoid Tumor | Neoplastic Syndrome | Neuroendocrine Carcinoma of the Skin | Childhood Langerhans Cell HistiocytosisUnited States
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PfizerTerminatedHemophilia AUnited States, New Zealand
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SanofiCompletedSphingomyelin LipidosisItaly, Czechia, Belgium, France, Portugal, Turkey, United States, Argentina, Brazil, Chile, Germany, Romania, Spain
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New York Medical CollegeCompletedLymphoma | Leukemia | Sickle Cell Disease | Histiocytosis | Immunodeficiencies | Inborn Errors of Metabolism | Bone Marrow Failure | Beta ThalassemiaUnited States
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TVA Medical Inc.Completed
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CSL LimitedCompleted
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The Hospital for Sick ChildrenActive, not recruitingRare Histiocytic Disorders (RHDs) | Juvenile Xanthogranuloma (JXG) | Reticulohistiocytoma (Epithelioid Histiocytoma) | Xanthoma Disseminatum (XD) | Multicentric Reticulohistiocytosis (MRH) | Systemic Juvenile Xanthogranuloma | Erdheim-Chester Disease (ECD) | Multi-system Rosai-Dorfman Disease (RDD)Canada, United States, Poland, Argentina, Austria, Czechia, Germany, Italy, Russian Federation, Spain
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Ellipse Technologies, Inc.CompletedThoracic Insufficiency SyndromeHong Kong, New Zealand, Finland, Turkey, Egypt, Italy, United Kingdom
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Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia
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Marinus PharmaceuticalsCompletedTuberous SclerosisUnited States
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Prehospital Center, Region ZealandNot yet recruitingDrowning | Drowning; Anoxia | Drowning, Near | Drowning; Asphyxia | Drowning and Nonfatal Submersion | Drowning or Immersion of Unknown Intent | Drowning and Submersion, Undetermined Intent | Drowning and Submersion While in Bath-Tub | Drowning and Submersion While in Natural Water | Drowning and Submersion... and other conditionsDenmark
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedChronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Leukocyte Adhesion Deficiency | Chronic Active Epstein-Barr Virus Infection | HIGM-1 | IPEXUnited States, Canada
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States