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Clinical Trials on Disturbi Eredodegenerativi, Sistema Nervoso
Total 82302 results
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Crolll GmbhUniversity of Magdeburg; Estimate, GmbHCompletedNon-alcoholic Steatohepatitis | Increased Iron Storage / Disturbed DistributionGermany
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National Human Genome Research Institute (NHGRI)CompletedFamilial Dementia With Neuroserpin Inclusion Bodies | Nervous System Heredodegenerative DisorderUnited States
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Kissei Pharmaceutical Co., Ltd.Completed
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Columbia UniversityUniversity of North Carolina, Chapel HillTerminated
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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NYU Langone HealthNot yet recruitingFamilial DysautonomiaUnited States
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NYU Langone HealthNot yet recruiting
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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NYU Langone HealthWithdrawnFamilial DysautonomiaUnited States
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University College, LondonRecruitingHereditary Sensory Neuropathy Type IUnited Kingdom
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NYU Langone HealthCompletedAtunomic NeuropathyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Second Affiliated Hospital, School of Medicine,...RecruitingHereditary AtaxiaChina
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UCB PharmaCompletedUnverricht-Lundborg DiseaseUnited States, Canada, Finland, France, Israel, Russian Federation, Serbia, Tunisia
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National Institute of Neurological Disorders and...Completed
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Second Affiliated Hospital, School of Medicine,...Recruiting
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Ionis Pharmaceuticals, Inc.CompletedLafora DiseaseUnited States, Italy, Spain
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Azienda Socio Sanitaria Territoriale di MantovaUnknownUnverricht-Lundborg Disease
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UCB Pharma SACompletedUnverricht-Lundborg DiseaseFrance, Italy, Sweden, Finland, Netherlands, Tunisia, Réunion
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Shenzhen Beike Bio-Technology Co., Ltd.The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical... and other collaboratorsUnknown
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Lupin Ltd.Recruiting
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Lupin Ltd.Active, not recruitingMyotonic DystrophyFrance, Germany, United Kingdom
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University of NancyCentral Hospital, Nancy, FranceCompleted
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University of VersaillesAssistance Publique - Hôpitaux de Paris; Association Française contre les Myopathies...Completed
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University...Recruiting
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Newcastle UniversityRecruiting
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Chinese University of Hong KongRecruiting
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Ataxia Study GroupRecruitingSpinocerebellar AtaxiaAustria, Belgium, France, Germany, Hungary, Italy, Netherlands, Poland, Spain, United Kingdom
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Steminent Biotherapeutics Inc.CompletedCerebellar AtaxiaTaiwan
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Kissei Pharmaceutical Co., Ltd.CompletedSpinocerebellar DegenerationJapan
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University Hospital TuebingenCompleted
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University of South FloridaBaxter Healthcare CorporationUnknownSpinocerebellar AtaxiasUnited States
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Kissei Pharmaceutical Co., Ltd.CompletedSpinocerebellar DegenerationJapan
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Kissei Pharmaceutical Co., Ltd.CompletedSpinocerebellar DegenerationJapan
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Chang Gung UniversityCompletedSpinocerebellar AtaxiaTaiwan
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University of South FloridaBaxter Healthcare CorporationCompletedSpinocerebellar AtaxiaUnited States
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University of Mississippi Medical CenterUniversity of TexasCompletedSpinocerebellar AtaxiaUnited States
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University of TurkuUnknownUnverricht-Lundborg SyndromeFinland
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Biohaven Pharmaceuticals, Inc.AvailableSpinocerebellar Ataxias | SCA
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Columbia UniversityCompleted
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Barbara BorroniCompleted
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Kissei Pharmaceutical Co., Ltd.CompletedSpinocerebellar DegenerationJapan
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Beth Israel Deaconess Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)CompletedSpinocerebellar AtaxiaUnited States
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Kissei Pharmaceutical Co., Ltd.CompletedSpinocerebellar DegenerationJapan
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IRCCS Policlinico S. MatteoCompletedTransthyretin AmyloidosisItaly
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Chang Gung UniversityCompleted
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ARTHEx Biotech S.L.Not yet recruitingMyotonic Dystrophy 1