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Clinical Trials on Emery-Dreifuss Muscular Dystrophy
Total 743 results
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedMyotonic Dystrophy Type 1United Kingdom
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University of RochesterCompletedMyotonic DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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Stanford UniversityUnknownMyotonic Dystrophy Type 1United States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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Grete Andersen, MDCompletedHyperkalemic Periodic Paralysis | Myotonia Congenita | Paramyotonia Congenita | Dystrophia Myotonica Type 1 | Potassium-Aggravated MyotoniaDenmark
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Massachusetts General HospitalRecruiting
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Newcastle UniversityLudwig-Maximilians - University of Munich; LGMD2i Research Fund; CureLGMD2iRecruitingLimb Girdle Muscular Dystrophy | Congenital Muscular Dystrophy | LGMDR9 | LGMD2I | Walker-Warburg Syndrome | Muscle-Eye-Brain Disease | FKRP Gene MutationUnited Kingdom
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Institut de Myologie, FranceEnrolling by invitationMyotonic Dystrophy Type 1France
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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Prof. Dr. Benedikt SchoserCompleted
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National Institute of Nursing Research (NINR)CompletedCerebral Palsy | Neuromuscular DiseaseUnited States
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Centre d'Investigation Clinique et Technologique...Recruiting
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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University of LiverpoolBournemouth University; Robert Jones and Agnes Hunt Orthopaedic and District... and other collaboratorsRecruitingNeuromuscular Diseases | Shoulder Injuries | Shoulder Pain | Upper Extremity Problem | Facio-Scapulo-Humeral DystrophyUnited Kingdom
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Myogem Health Company, S.L.CompletedMyotonic Dystrophy 1Spain
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Assistance Publique - Hôpitaux de ParisTerminatedNeuromuscular Diseases | Amyotrophic Lateral Sclerosis | Duchenne Muscular DystrophyFrance
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Assistance Publique - Hôpitaux de ParisNot yet recruitingMyotonic Dystrophy 1 | Steinert's Disease | MetforminFrance
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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Lokman Hekim ÜniversitesiHacettepe UniversityCompletedQuality of Life | Lower Urinary Tract Symptoms | Muscle Weakness | Duchenne Muscular Dystrophy | Pelvic Floor Muscle Weakness | Posture Disorders in Children | Lumbar LordosisTurkey
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Eye Hospital Pristina KosovoEnrolling by invitationMacular Corneal DystrophyKosovo
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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University of Campania "Luigi Vanvitelli"RecruitingSudden Cardiac Death | Myotonic Dystrophy 1Italy
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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Turkish Society of Pediatric Gastroenterology,...CompletedDuchenne Muscular Dystrophy | Pompe Disease (Late-onset)Turkey
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University College, LondonNational Institute for Health Research, United Kingdom; Myotonic Dystrophy... and other collaboratorsRecruitingMyotonic Dystrophy 1 | Dysphagia, OropharyngealUnited Kingdom
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National Institute of Respiratory Diseases, MexicoUnknownMyotonic Dystrophy 1 | Steinert DiseaseMexico
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCardiomyopathy, Hypertrophic | Muscular Dystrophy, OculopharyngealUnited States
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Barcelona Macula FoundationRecruitingRetinitis Pigmentosa | Choroideremia | Stargardt Disease 1 | Best Disease | Pattern Dystrophy of MaculaSpain
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Wake Forest University Health SciencesTerminatedFuchs Dystrophy | Cystoid Macular EdemaUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingRetinal Detachment | Epiretinal Membrane | Macular Holes | Macular DystrophiesItaly
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GlaxoSmithKlineCompleted
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University Children's Hospital, ZurichUniversity of ZurichWithdrawnMuscular Dystrophies
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Alessandra PedrocchiCompletedMuscular DystrophiesItaly
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FDA Office of Orphan Products DevelopmentCompletedMuscular DystrophiesUnited States
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Edgewise Therapeutics, Inc.CompletedMuscular DystrophiesUnited States
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Wake Forest University Health SciencesCompleted
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South Valley UniversityUnknownMuscular DystrophyEgypt
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National Heart, Lung, and Blood Institute (NHLBI)Terminated
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Universitat Pompeu FabraHospital Clinic of BarcelonaRecruiting
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IRCCS Eugenio MedeaCompletedMuscular DystrophiesItaly
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AbiliTech Medical Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownMuscular Dystrophies
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Neurogen Brain and Spine InstituteWithdrawn
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Katherine MathewsNational Institute of Neurological Disorders and Stroke (NINDS)Recruiting
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Centre Hospitalier Universitaire de NiceActive, not recruitingMuscular Dystrophy | FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de Saint EtienneMinistry of Health, France; Association Française contre les Myopathies (AFM)...CompletedMuscular Dystrophy | FacioscapulohumeralFrance
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Food and Drug Administration (FDA)National Eye Institute (NEI)RecruitingAge-Related Macular Degeneration | Retinal Degeneration | Retinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Rod Dystrophy | Cone Rod Dystrophy | Hydroxychloroquine Retinopathy | Late-Onset Retinal Degeneration | Rod Cone DystrophyUnited States