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Clinical Trials on Familial Chylomicronemia Syndrome
Total 35258 results
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Mayo ClinicCompleted
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Centre Hospitalier Universitaire de la RéunionRecruitingLipodystrophy | Dunnigan SyndromeRéunion
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Institut National de la Santé Et de la Recherche...RecruitingPrader-Willi Syndrome | Angelman Syndrome | Beckwith-Wiedemann Syndrome | Pseudohypoparathyroidism | Silver Russell Syndrome | Transient Neonatal Diabetes Mellitus | Temple Syndrome | Kagami-Ogata Syndrome | Familial Precocious PubertyFrance
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Laboratorios Sophia S.A de C.V.Completed
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M.D. Anderson Cancer CenterRecruitingFamilial Platelet Disorder | HematopoieticUnited States
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Shenzhen People's HospitalRecruitingEvaluate the Efficacy and Safety of IBI306 in Subjects With Homozygous Familial HypercholesterolemiaLipid Metabolism Disorders | Familial Hypercholesterolemia - Homozygous | Proprotein Convertase Subtilisin/Kexin 9China
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Groupe Francophone des MyelodysplasiesBristol-Myers Squibb; AbbVieRecruitingUntreated Myelodysplastic SyndromeFrance
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Case Comprehensive Cancer CenterRecruitingMyelodysplastic Syndrome (MDS)United States
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Novartis PharmaceuticalsTerminatedMyelodysplastic Syndrome (MDS)France, Spain, Belgium, Italy, Greece, Hungary, Germany
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Weill Medical College of Cornell UniversityNovartis PharmaceuticalsCompletedMyelodysplastic Syndrome (MDS)United States
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Incyte CorporationTerminatedMDS (Myelodysplastic Syndrome)United States
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Chinese Society of HematologyHarbin Institute of Hematology & OncologyUnknownMyelodysplastic Syndrome (MDS)
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Asociación Andaluza de Hematología y HemoterapiaCompleted
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Genzyme, a Sanofi CompanyTerminatedMyelodysplastic Syndrome (MDS)Germany, United Kingdom, France, Netherlands
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Heinrich-Heine University, DuesseldorfTerminatedMyelodysplastic Syndrome MDSGermany
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TelikTerminatedMyelodysplastic Syndrome (MDS)United States
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TelikCompletedMyelodysplastic Syndrome (MDS)United States
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Seagen Inc.CompletedMyelodysplastic Syndrome (MDS)United States
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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zhang shoulongChanghai Hospital; Jinan Military General HospitalRecruitingImmune Effector Cell Associated Neurotoxicity SyndromeChina
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndrome (MDS)United States, Australia, Austria, Belgium, Brazil, Canada, China, Czechia, France, Germany, Israel, Italy, Japan, Korea, Republic of, Netherlands, Poland, Puerto Rico, Russian Federation, Spain, Taiwan, Turkey, United Kingdom, Hungary
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Amphivena Therapeutics, Inc.CompletedMyelodysplastic Syndrome (MDS)United States
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CelgeneCompletedMyelodysplastic Syndrome (MDS)China
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Novartis PharmaceuticalsTerminatedMyelodysplastic Syndrome (MDS)Germany
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TelikCompletedMyelodysplastic Syndrome (MDS)United States
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Bellus Health IncFDA Office of Orphan Products DevelopmentCompletedGastrointestinal Diseases | Kidney Diseases | Rheumatoid Arthritis | Nephrotic Syndrome | Secondary (AA) Amyloidosis | Familial Mediterranean SyndromeUnited States, Israel, Finland, France, Italy, Lithuania, Netherlands, Poland, Russian Federation, Spain, Turkey, United Kingdom
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Otsuka Pharmaceutical Co., Ltd.RecruitingMyelodysplastic Syndrome (MDS)Japan
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Fondazione Italiana Sindromi Mielodisplastiche-ETSRecruiting
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Novartis PharmaceuticalsActive, not recruitingMyelodysplastic Syndrome (MDS)United States
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Fujifilm Pharmaceuticals U.S.A., Inc.WithdrawnMyelodysplastic Syndrome (MDS)
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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TelikTerminatedMyelodysplastic Syndrome (MDS)United States
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Oncology Specialties, AlabamaTerminatedMyelodysplastic Syndrome (MDS)United States
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Mirum Pharmaceuticals, Inc.Active, not recruitingCholestatic Liver Disease | Alagille Syndrome | Progressive Familial Intrahepatic CholestasisUnited States, United Kingdom, France, Belgium, Poland, Brazil, Mexico
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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Thomas Jefferson UniversityAbbVieRecruitingMyelodysplastic Syndrome | Recurrent Myelodysplastic Syndrome | Refractory Myelodysplastic SyndromeUnited States
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University of Wisconsin, MadisonTerminatedCompartment Syndrome of LegUnited States
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Scripps HealthJ. Craig Venter InstituteCompletedLi-Fraumeni Syndrome | Hereditary Cancer Syndromes | TP53 Gene Germline Mutation CarrierUnited States
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University Medical Center GroningenAstraZenecaCompletedHeart Failure | Cardiomyopathy, Familial | Phospholamban R14del CardiomyopathyNetherlands
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Erasmus Medical CenterEnrolling by invitationComplex Regional Pain Syndromes | CRPS (Complex Regional Pain Syndromes)Netherlands
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Institut fuer anwendungsorientierte Forschung und...University Medical Center GoettingenCompletedMyelodysplastic Syndromes (MDS) | Chromosmal Aberrations | Karyotype Evolution | Rare Abnormalities | Cytogenetic MonitoringGermany
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Larissa University HospitalRecruitingDumping Syndrome | Gastric SurgeryGreece
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TakedaCompletedDravet Syndrome (DS)China, Canada, France, Hungary, Poland, United States, Spain, Greece, Australia, Brazil, Serbia, Germany, Italy, Japan, Latvia, Netherlands, Ukraine, Russian Federation
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Institute of Cardiometabolism and Nutrition, FranceAmgenUnknownFamilial Hypercholesterolemia - HeterozygousFrance
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Children's Hospital of PhiladelphiaUniversity of PennsylvaniaRecruiting
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingLeukemia | Myelodysplastic Syndrome | Recurrent Myelodysplastic SyndromeUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingHigh Risk Myelodysplastic SyndromeUnited States
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Jasper Therapeutics, Inc.Recruiting