- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Familial LCAT Deficiency
Total 10159 results
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Cornell UniversityCenters for Disease Control and Prevention; Arogyavaram Medical CentreActive, not recruitingAnemia | Vitamin B 12 Deficiency | Folate DeficiencyIndia
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Mayo ClinicUniversity of California, San Francisco; University of MinnesotaCompletedFamilial Pancreatic CancerUnited States
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University of TorontoThe Hospital for Sick Children; Heinz EndowmentsCompletedIron Deficiency | Folic Acid DeficiencyCanada
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Institute of Cardiometabolism and Nutrition, FranceAmgenUnknownFamilial Hypercholesterolemia - HeterozygousFrance
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West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
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National Human Genome Research Institute (NHGRI)CompletedGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets Type2United States
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University Hospital TuebingenCompletedImmune Deficiency DiseaseGermany
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Cytos Biotechnology AGCompletedPerennial Allergy to House Dust Mite and/or CatEstonia, Latvia, Lithuania
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University of Lagos, NigeriaAminu Kano Teaching HospitalCompletedIron Deficiency Anemia of PregnancyNigeria
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University of AarhusCompletedVitamin B12 DeficiencyDenmark
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Mario Negri Institute for Pharmacological ResearchFondazione TelethonCompleted
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REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
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Karo Bio ABTerminatedHeterozygous Familial Hypercholesterolaemia
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Arrowhead Regional Medical CenterRecruitingIron Deficiency Anemia of PregnancyUnited States
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Cornell UniversityCenters for Disease Control and Prevention; St. John's Research Institute; Arogyavaram...Active, not recruiting
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United States Army Research Institute of Environmental...RecruitingStress, Physiological | Energy Supply; Deficiency | Energy Supply; Deficiency, SevereUnited States
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Universität des SaarlandesInstitute of Alternative and Sustainable Nutrition (IFANE)CompletedCobalamin DeficiencyGermany
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Ohio State UniversityCompletedSaccadic Eye Movement Deficiency | Oculomotor Dysfunction | Oculomotor DeficiencyUnited States
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CENTOGENE GmbH RostockWithdrawnLipoprotein Lipase Deficiency | Inborn Error of Lipid Metabolism | Corneal ArcusGermany, India, Sri Lanka
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Ultragenyx Pharmaceutical IncCompletedCarnitine Palmitoyltransferase (CPT I or CPT II) Deficiency | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Long-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine-acylcarnitine Translocase (CACT) DeficiencyUnited States, United Kingdom
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He Eye HospitalUnknown
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University of Colorado, DenverCompletedIron Deficiency Anemia | Iron DeficiencyUnited States
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University Health Network, TorontoSunnybrook Health Sciences Centre; Queen's University; Heart and Stroke Foundation...Not yet recruitingCardiac Surgery | Chronic Iron Deficiency AnaemiaCanada
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Westfälische Wilhelms-Universität MünsterICON plcUnknownPseudoxanthoma Elasticum | Generalized Arterial Calcification in Infancy | Autosomal Recessive Hypophosphatemic RicketsGermany
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TakedaCompletedVitamin D Deficiency | Calcium DeficiencyGermany
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Fundació Institut de Recerca de l'Hospital de la...Hospital Clinic of BarcelonaCompletedFamilial Hypocalciuric HypercalcemiaSpain
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Assistance Publique - Hôpitaux de ParisRecruitingArtemis (DCLRE1C ) Deficient Severe Combined ImmunodeficiencyFrance
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West China HospitalWest China Second University HospitalCompletedIron Deficiency Anemia of PregnancyChina
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Bispebjerg HospitalCompletedObesity | Deficiency, Vitamin D
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King's CollegeCompletedIron-deficiency | Iron Deficiency Anemia | Iron Deficiency (Without Anemia)United States
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Northwestern UniversityCompletedIron-deficiency AnemiaUnited States
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Peking Union Medical College HospitalUnknown
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Ifakara Health InstituteSwiss Tropical & Public Health InstituteUnknownIron-Deficiency AnemiaTanzania
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University of MichiganAvailable
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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Swiss Federal Institute of TechnologyUnited States Agency for International Development (USAID); Quadram Institute... and other collaboratorsCompletedIron-deficiency | Iron Deficiency Anemia | Iron Deficiency (Without Anemia)Peru
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityNot yet recruitingVitamin d DeficiencyChina
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Indonesia UniversityUnited States Agency for International Development (USAID); Ministry of Research...Completed
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Harvard UniversityCompleted
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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HaEmek Medical Center, IsraelCompleted
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ZonMw: The Netherlands Organisation for Health...Cardiff University; University Medical Center Groningen; Erasmus Medical Center; Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA) and other collaboratorsUnknownColorectal Neoplasms, Hereditary Nonpolyposis
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Visirna Therapeutics HK LimitedNot yet recruitingFamilial Chylomicronemia Syndrome
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Ionis Pharmaceuticals, Inc.AvailableFamilial Chylomicronemia Syndrome
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Jiangsu HengRui Medicine Co., Ltd.CompletedMixed Hyperlipidemia | Non-familial HypercholesterolemiaChina
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Abhimanyu GargCompletedFamilial Partial LipodystrophyUnited States