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Clinical Trials on Gaucher Disease, Type 3 in United Kingdom
Total 26841 results
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Genzyme, a Sanofi CompanyActive, not recruitingGaucher Disease Type 1 | Gaucher Disease Type 3Germany, United States, Japan, United Kingdom
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SanofiRecruitingGaucher's Disease Type IIIUnited States, Germany, Hungary, France, China, Japan, Canada, Argentina, Italy, Turkey
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SanofiActive, not recruitingGaucher's Disease Type III | Gaucher's Disease Type ICanada, Argentina, France, Italy, Japan, Russian Federation, Spain, Sweden, Turkey, United Kingdom
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Baylor Research InstituteTexas Scottish Rite Hospital for ChildrenWithdrawnGaucher Disease Type 1 | Gaucher Disease Type 3United States
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Cambridge University Hospitals NHS Foundation TrustMedical Research Council; National Institute for Health Research, United KingdomRecruitingGaucher Disease, Type III | Gaucher Disease, Type IUnited Kingdom
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, United States
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University of MinnesotaRecruitingGaucher Disease, Type 3United States
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Freeline TherapeuticsRecruitingGaucher Disease, Type 1Spain, Israel, United States, United Kingdom, Brazil, Germany, Paraguay
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, Israel, South Africa, United States
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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Allievex CorporationCompletedMucopolysaccharidosis Type IIIB | Mucopolysaccharidosis Type 3 B | MPS III B | MPS 3 BUnited States, Spain, Turkey, Taiwan, Australia, Colombia, Germany, United Kingdom
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Prevail TherapeuticsEli Lilly and CompanyActive, not recruitingGaucher Disease, Type 2United States, United Kingdom
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University of East AngliaQuadram Institute BioscienceCompletedMetabolism and Clearance of Cyanidin 3 GlucosideUnited Kingdom
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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NHS Greater Glasgow and ClydeUniversity of Strathclyde; Microsoft CorporationCompletedTelemedicine | Reconstructive Surgery | 3 DimensionalUnited Kingdom
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Gloucestershire Hospitals NHS Foundation TrustSuspendedLichen Sclerosus | Squamous Cell Carcinoma | Normal Vulval Skin | High Grade Dysplasia - Usual Type ('VIN 2-3') | High Grade Dysplasia - Differentiated Type ('VIN 2-3') | Epithelial Hyperplasia Without Atypia | Atypia Not Otherwise Specified/ Low Grade Dysplasia ('VIN 1') | Pagets Disease of the...United Kingdom
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Fondazione Angelo Bianchi BonomiSintesi Research SrlActive, not recruitingType 3 Von Willebrand's DiseaseFinland, France, Germany, Hungary, Iran, Islamic Republic of, Italy, Netherlands, Spain, Sweden, United Kingdom
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States, United Kingdom
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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ShireCompletedGaucher DiseaseUnited States, Spain, United Kingdom, Israel
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ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
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University Hospitals, LeicesterCompletedAssess Effect of Omega-3 Fish Oil in Patients With Severe Acute PancreatitisUnited Kingdom
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Baxalta now part of ShireCompletedVon Willebrand DiseaseUnited States, Germany, United Kingdom, Italy, Austria, Canada
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ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
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University of AberdeenNHS Grampian; Chief Scientist Office of the Scottish GovernmentCompletedStage 2 or 3 Full Thickness Macular HoleUnited Kingdom, Ireland
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Astellas Pharma Global Development, Inc.No longer availableAcute Myeloid Leukemia (AML) | FMS-like Tyrosine Kinase-3 (FLT3) MutationsAustralia, Italy, United Kingdom
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PfizerWithdrawnType 1 Gaucher DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India
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Hiantis SrlSciensano; Genefirst LTDCompletedNeoplasms | Neoplasms by Histologic Type | Carcinoma in Situ | Neoplasm Cervix | Cervical Intraepithelial Neoplasia Grade 2/3 | Carcinoma Cervix UterineItaly, Ireland, United Kingdom
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyEnrolling by invitationKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2) | Primary Hyperoxaluria Type 3 (PH3)United States, France, Germany, Japan, Lebanon, Spain, United Kingdom, Australia, Canada, Italy, Netherlands, Norway, Turkey
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Exsar CorporationSuspendedType I Gaucher DiseaseUnited States
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University Research Foundation for Lysosomal Storage...University of PittsburghCompletedGaucher DiseaseUnited States
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SanofiCompletedGaucher's DiseaseUnited States
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher Disease Type 1United States
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain, Germany
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AVROBIOTerminatedType 1 Gaucher DiseaseUnited States, Canada
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, Israel, Mexico, Russian Federation, Argentina, Italy
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AVROBIOTerminatedGaucher DiseaseUnited States, Canada
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National Institute of Neurological Disorders and...Completed
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SanofiCompletedGaucher's DiseaseUnited States
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National Institute of Mental Health (NIMH)Completed
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Dicerna Pharmaceuticals, Inc.CompletedPrimary Hyperoxaluria Type 3United States, Germany, Netherlands, United Kingdom