- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Disorder
Total 150426 results
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World Federation of HemophiliaRecruitingHemophilia A | Hemophilia B | Von Willebrand DiseasesCanada
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BUnited States
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Rady Pediatric Genomics & Systems Medicine InstituteRecruiting
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityRecruiting
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Kevin BruceNot yet recruiting
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Vanderbilt University Medical CenterRecruitingGenetic DiseaseUnited States
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Rady Pediatric Genomics & Systems Medicine InstituteActive, not recruiting
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Illumina, Inc.Medical College of WisconsinActive, not recruitingGenetic DiseaseUnited States
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Igentify LtdSheba Medical CenterUnknown
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Maastricht University Medical CenterRecruiting
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University of California, San DiegoCalifornia Institute for Regenerative Medicine (CIRM); n-Lorem FoundationActive, not recruitingGenetic DiseaseUnited States
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Igentify LtdTel-Aviv Sourasky Medical CenterUnknownGenetic Disease
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Karolinska InstitutetKarolinska University HospitalEnrolling by invitationRare Diseases | Genetic Disease | Chromosome AbnormalitySweden
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseFrance
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsBrazil
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitationIntellectual Disability | Down Syndrome | Attention Deficit Hyperactivity Disorder | Fragile X SyndromeUnited States
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The University of Hong KongEnrolling by invitationCannabis Use | Neurocognitive Dysfunction | Genetic PredispositionHong Kong
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The University of Hong KongCompletedPsychotic Disorders | Schizophrenia | Substance Use Disorders | Genetic Predisposition | Ketamine AbuseHong Kong
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsSpain, Canada, United Kingdom
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Duke UniversitySuspendedLysosomal Storage Diseases | Genetic Disease | Inborn Errors of Metabolism | Glycogen Storage Disease | Storage DiseaseUnited States
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Eloxx Pharmaceuticals, Inc.SGS Life Sciences, a division of SGS Belgium NVCompleted
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Fundación Pública Andaluza para la Investigación...Delos ClinicalCompleted
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Eloxx Pharmaceuticals, Inc.SGS Life Sciences, a division of SGS Belgium NVCompleted
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Baxalta now part of ShireTakedaCompleted
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PfizerCompletedHemophilia BGermany, Austria
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Liggins InstituteRecruiting
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Children's Mercy Hospital Kansas CityCompletedGenetic Disease | Diseases/DiagnosesUnited States
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Suellen Marinho AndradeNot yet recruiting
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University of Central FloridaNational Institute on Deafness and Other Communication Disorders (NIDCD); University...CompletedDown Syndrome | Speech Sound Disorder | Speech Disorders in Children | Speech Intelligibility | Speech and Language DisorderUnited States
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AB2 Bio Ltd.CompletedNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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AB2 Bio Ltd.Active, not recruitingNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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University Hospital, BordeauxNot yet recruitingNervous System Diseases | Genetic Disease
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Lithuanian University of Health SciencesRecruitingInflammation | Cognitive Dysfunction | Genetic Predisposition to Disease | Endotoxemia | Major Depressive Disorder | Blood Brain Barrier DefectLithuania
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Hacettepe UniversitySuleyman Demirel UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Posture Disorders in Children | Ambulation Disorder, NeurologicTurkey
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Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical ResearchRecruitingFamilial Hypercholesterolemia | Genetic Disease | Cholesterol, ElevatedUnited States
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Massachusetts General Hospitaln-Lorem FoundationNot yet recruiting
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National Human Genome Research Institute (NHGRI)RecruitingGenetic ConditionsUnited States
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University of PennsylvaniaFox Chase Cancer Center; Columbia University; Thomas Jefferson UniversityEnrolling by invitationCardiovascular Diseases | Cancer | Genetic DiseaseUnited States
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Hospices Civils de LyonNot yet recruitingAtaxia | Genetic Disease | Degenerative DiseaseFrance
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Robert Bosch Medical CenterCompletedQuality of Life | Physical Activity | Genetic Testing
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia A | Hemophilia B | HemophiliaTurkey
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Assiut UniversityNot yet recruitingHemophilia A | Hemophilia B
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Poland, Canada, Armenia, Turkey
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Regeneron PharmaceuticalsRecruitingHemophilia BUnited States, Germany, United Kingdom, Canada
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Swedish Orphan BiovitrumIQVIA Pvt. LtdTerminatedHemophilia A | Hemophilia BBulgaria, Croatia, Czechia, France, Hungary, Ireland, Italy, Romania, Slovenia, Spain, United Kingdom