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Clinical Trials on Genetic Disorder
Total 151813 results
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Glanzmann's DiseaseSpain, Bulgaria, Pakistan, Belgium, Germany, France, United Kingdom, Italy, Hungary, Netherlands, United States, Algeria, Austria, Sweden, Switzerland
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The Affiliated Hospital of Xuzhou Medical UniversityRecruitingType 2 Diabetes Mellitus | Genetic Mutations | Gene Polymorphisms | Susceptibility, GeneticChina
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Scripps HealthWest Virginia UniversityCompletedCardiovascular Diseases | Heart Failure | Hypertension | Atrial Fibrillation | Metabolic Syndrome | Genetic DiseaseUnited States
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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Universidad del AzuayCompletedHemophilia A | Hemophilia B | Von Willebrand DiseaseEcuador
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ADMA Biologics, Inc.CompletedPrimary Immune Deficiency Disorders (PIDD)United States
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Eloxx Pharmaceuticals, Inc.TerminatedGenetic Diseases | Nonsense Mutations
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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Weill Medical College of Cornell UniversityUniversity of Alabama at BirminghamCompletedTourette Disorder | Chronic Tic DisorderUnited States
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University of South FloridaJohns Hopkins All Children's HospitalCompletedObsessive-compulsive Disorder | Prader Willi SyndromeUnited States
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Dana-Farber Cancer InstituteRecruitingLung Cancer | Genetic Disease | Genetic Predisposition | Hereditary DiseasesUnited States
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BSweden, Finland, Denmark
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Karolinska University HospitalKarolinska Institutet; The Swedish Society of MedicineUnknownHemophilia A | Hemophilia B | Von Willebrand's DiseaseSweden
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Virginia Commonwealth UniversityCSL BehringCompletedHemophilia A | Hemophilia B | Vitamin D DeficiencyUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AItaly, Sweden, Netherlands, Austria, Spain, United States, Switzerland, Germany, France, Hungary, Greece, Slovenia, Czechia, Slovakia, Poland
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Antonio PersicoUniversity of Bari; Associazione Italiana Sindrome di Phelan-McDermid (AISPHEM)Enrolling by invitationAutism Spectrum Disorder | Phelan-McDermid SyndromeItaly
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Novo Nordisk A/SCompletedComparison of the Action of Drugs in the Body and Safety of N8 and Advate® in Haemophilia A SubjectsCongenital Bleeding Disorder | Haemophilia ASpain, Germany, Switzerland, Italy, Israel
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Germany, Switzerland, United Kingdom, Italy, Japan, Turkey
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia ASpain, Germany, Malaysia, Latvia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited Kingdom, Malaysia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela
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University Hospital, MontpellierRecruitingHemophilia A | Hemophilia B | ArthropathyFrance
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Novo Nordisk A/SActive, not recruitingHaemophilia A Without Inhibitors | Haemophilia B Without InhibitorsSpain, United States, Korea, Republic of, United Kingdom, Australia, Lithuania, France, Turkey, India, Estonia, Russian Federation, Ukraine, Mexico, Japan, South Africa, Serbia, Canada, Croatia, Algeria, Bosnia and Herzegovina, ... and more
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Laboratoire français de Fractionnement et de BiotechnologiesLFB USA, Inc.CompletedA Phase III Study on the Safety, Pharmacokinetics and Efficacy of Coagulation Factor VIIa (PERSEPT2)Hemophilia A With Inhibitors | Hemophilia B With InhibitorsBulgaria, Ukraine, Czechia, United States, Georgia, South Africa
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X SyndromeUnited States
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia BSweden, United States, France, Italy, Russian Federation, United Kingdom, Germany, China, Poland, Japan, Australia, Brazil, Canada, India, South Africa, Hong Kong, Belgium
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Bioverativ Therapeutics Inc.CompletedSevere Hemophilia BUnited States, Italy, Belgium, Australia, Brazil, Hong Kong, India, Ireland, Japan, South Africa, United Kingdom, Netherlands, Sweden, Canada, Poland, China, France, Germany
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)CompletedFragile X SyndromeUnited States
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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Hospices Civils de LyonNot yet recruiting
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Bowdoin CollegeMassachusetts General HospitalCompletedTourette Syndrome | Persistent Tic DisorderUnited States
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Otsuka Pharmaceutical Development & Commercialization...TerminatedTourette's Disorder (TD)United States, Canada, Hungary
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Hospices Civils de LyonUnknownCancer | Paraneoplastic Syndromes | Neurologic Disorder | Immune System and Related Disorders | Tumor GeneticsFrance
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National Human Genome Research Institute (NHGRI)RecruitingGenetic DiseaseUnited States
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University of MinnesotaTerminated
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University Hospital, MontpellierRecruitingGenetic Disease | Myopathy | Phenotypic AbnormalityFrance
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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Children's Hospital Medical Center, CincinnatiRecruitingFragile X SyndromeUnited States
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Novo Nordisk A/SActive, not recruitingHaemophilia A With Inhibitors | Haemophilia B With InhibitorsSpain, Korea, Republic of, India, Australia, United Kingdom, Russian Federation, Poland, Ukraine, Thailand, Mexico, United States, Turkey, Japan, South Africa, Serbia, France, Croatia, Denmark, Algeria, Bulgaria, Malaysia, Portugal, Slovaki... and more
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AryoGen Pharmed Co.CompletedHemophilia A With Inhibitor | Hemophilia B With InhibitorIran, Islamic Republic of
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.UnknownHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedHemophilia A | Hemophilia BUnited States, Canada, France, Italy
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rEVO BiologicsLaboratoire français de Fractionnement et de BiotechnologiesCompletedHemophilia A With Inhibitors | Hemophilia B With InhibitorsUnited States, Bulgaria, Poland, Russian Federation, Belarus, Georgia, Israel, Romania, Ukraine, United Kingdom
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BayerCompletedHemophilia A, Hemophilia BItaly, China, New Zealand, Russian Federation, Taiwan, Singapore, Bulgaria, United States, Denmark, Germany, Hungary, South Africa, United Kingdom, Romania, Colombia, Mexico, Turkey, France, India, Japan, Australia, Netherlands, Poland and more
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New York Presbyterian HospitalCompletedHemophilia A | Hemophilia BUnited States
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Esoterix Genetic Laboratories, LLCUnknownFragile X SyndromeUnited States
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia B | Allergic ReactionsFrance, Italy, United States, Austria, Belgium, Spain, United Kingdom, Canada, Germany
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States