- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Disorder
Total 151860 results
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Baxalta now part of ShireActive, not recruiting
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Novo Nordisk A/SEnrolling by invitation
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Ultragenyx Pharmaceutical IncCompletedHemophilia BUnited States, United Kingdom
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Baxalta now part of ShireCompletedHemophilia A | Hemophilia BUnited States, Spain, Italy, Germany, France, Austria
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Centre Hospitalier Universitaire DijonUnknown
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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Ultragenyx Pharmaceutical IncTerminatedHemophilia BUnited States, United Kingdom, Bulgaria
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Bio Products LaboratoryCompletedHaemophilia BPoland, Ukraine
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Bio Products LaboratoryCompletedHaemophilia BUnited Kingdom
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Children's Hospital of PhiladelphiaNational Institutes of Health (NIH); National Human Genome Research Institute...Recruiting
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The Leeds Teaching Hospitals NHS TrustGenomic Medicine Services AllianceCompletedGenetic Disease | Bereavement | Fetal AnomalyUnited Kingdom
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Yale UniversityCompletedSkin Diseases | Immune System Diseases | Hypersensitivity | Hypersensitivity, Immediate | Skin Diseases, Genetic | Dermatitis | Eczema | Skin Diseases, Eczematous | Dermatitis, Atopic | Genetic Disease, InbornUnited States
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National Institute of Allergy and Infectious Diseases...CompletedGenetic Diseases, X-Linked | Lymphoproliferative Disease | X-Linked Lymphoproliferative DiseaseUnited States
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Regina Elena Cancer InstituteRecruiting
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The Hospital for Sick ChildrenCompletedHemophilia A | Hemophilia BCanada, Brazil
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderJapan
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American Thrombosis and Hemostasis NetworkSanofi; Pfizer; Genentech, Inc.; CSL Behring; Hemophilia of Georgia, Inc.; Hemab TherapeuticsRecruitingHemophilia | Thrombosis | Thrombophilia | Sickle Cell Disease | Thalassemia | Bleeding Disorder | Von Willebrand Diseases | Factor IX Deficiency | Connective Tissue Disorder | Factor VIII Deficiency | Hematologic Disorder | Rare Bleeding Disorder | Platelet DisorderUnited States
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Firalis SARecruiting
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National Cancer Institute (NCI)CompletedDyskeratosis Congenita | Telomere Biology DisordersUnited States
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Clinical Hospital Center RijekaKarolinska Institutet; University Medical Centre Ljubljana; Croatian Science...Enrolling by invitationParkinson Disease | Genetic Disease | Microbiota | Neuro-Degenerative Disease | Neuroinflammatory ResponseCroatia
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Yuzuncu Yıl UniversityHasan Kalyoncu University; University of Gaziantep; Acıbadem Adana HospitalRecruiting
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KK Women's and Children's HospitalCompletedChronic Pain | Anaesthesia | Genetics PredispositionSingapore
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Equilibra Bioscience LLCRecruitingHemophilia A | Hemophilia B | Healthy ParticipantsUnited States
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Swedish Orphan BiovitrumCerner EnvizaCompleted
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Shanghai Belief-Delivery BioMed Co., LtdActive, not recruiting
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Baxalta now part of ShireTerminatedHemophilia BTurkey, Spain
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University of MiamiShireTerminated
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Cliniques universitaires Saint-Luc- Université...Completed
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Bio Products LaboratoryCompletedHaemophilia BUnited Kingdom
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AvigenThe University of Texas Health Science Center, Houston; Children's Hospital... and other collaboratorsTerminatedHemophilia BUnited States
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderIsrael
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TiumBio Co., Ltd.RecruitingHemophilia A | Hemophilia B | Blood Coagulation DisordersKorea, Republic of
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CSL BehringRecruiting
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CSL BehringRecruiting
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Institute of Hematology & Blood Diseases HospitalEast China University of Science and TechnologyActive, not recruiting
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Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
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Baxalta now part of ShireCompletedHemophilia BColombia, Bulgaria, Chile, Poland, Romania, Argentina, Brazil, Czechia, Russian Federation, Ukraine
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Spark TherapeuticsChildren's Hospital of Philadelphia; Royal Prince Alfred Hospital, Sydney,... and other collaboratorsCompleted
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Bio Products LaboratoryCompletedHaemophilia BUnited Kingdom, Poland
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Bio Products LaboratoryCompletedHaemophilia BPoland, Romania, Russian Federation
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PfizerCompleted
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Jerry Vockley, MD, PhDEnrolling by invitationGenetic Disease | Infant, Newborn, DiseaseUnited States
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Taipei Veterans General Hospital, TaiwanNational Yang Ming UniversityUnknownObesity | MenopauseTaiwan
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Anahuac UniversityCompletedGenetic Predisposition | Carrier, GestationalMexico
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General Genetics CorporationSyntactxUnknownGenetics of Drug MetabolismUnited States, Puerto Rico
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BGermany
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Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
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Baxalta now part of ShireCompletedRecombinant Factor VIIa BI (rFVIIa BI) Treatment of Acute Bleeding Episodes Per an On-demand RegimenHemophilia A | Hemophilia BJapan, Russian Federation, Spain, United States, Poland, Romania, Serbia, Taiwan, Ukraine
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BayerCompletedHemophilia A; Hemophilia BIsrael
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Novo Nordisk A/SCompletedHaemophilia A | Haemophilia BUnited States