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Clinical Trials on Genitourinary Congenital Anomalies in New Zealand
Total 867 results
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Terumo BCTbioUnited States Department of Defense; U.S. Army Medical Research and Development... and other collaboratorsTerminatedTransfusion Dependent ThalassemiaUnited States, Israel, Italy, Turkey
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The Rogosin InstituteWeill Medical College of Cornell University; New York Presbyterian HospitalWithdrawnAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Emmaus Medical, Inc.CompletedSickle Cell Anemia | Sickle ß0-ThalassemiaUnited States
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RWTH Aachen UniversityUnknownAngina Pectoris | Left Ventricular Wall Motion AbnormalitiesGermany
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QOL Medical, LLCRecruitingCongenital Sucrase-Isomaltase Deficiency | CSID | Sucrase Isomaltase DeficiencyUnited States
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Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
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IcagenJohnson & Johnson Pharmaceutical Research & Development, L.L.C.TerminatedSickle Cell Disease | Sickle Cell AnemiaUnited States
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States
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Yale UniversityTerminatedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Terminated
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...CompletedBody Weight Changes | Sarcopenia | Prader Labhart Willi SyndromeTaiwan
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Memphis; RTI...CompletedSickle Cell DiseaseUnited States
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Boston Children's HospitalChildren's Hospital Colorado; Cedars-Sinai Medical Center; Hospital for Special... and other collaboratorsRecruitingAdolescent Idiopathic Scoliosis | Idiopathic Scoliosis | Spondylolisthesis | Spine Deformity | Neuromuscular Scoliosis | Congenital ScoliosisUnited States
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Susan P. PerrineIcahn School of Medicine at Mount Sinai; University of Illinois at Chicago; Boston... and other collaboratorsCompletedSickle Cell Anemia | Skin UlcersUnited States
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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University of Central FloridaNational Institute on Deafness and Other Communication Disorders (NIDCD); University...CompletedDown Syndrome | Speech Sound Disorder | Speech Disorders in Children | Speech Intelligibility | Speech and Language DisorderUnited States
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Palvella Therapeutics, Inc.RecruitingMicrocystic Lymphatic MalformationUnited States
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NYU Langone HealthCompletedAnxiety Disorders | Familial Dysautonomia | Dysthymia | Paroxysmal Hypertension | Autosomal Recessive DiseaseUnited States
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Gary M Brittenham, MDCompletedVitamin D Deficiency | Asthma | Sickle Cell Disease | Acute Chest Syndrome | Respiratory InfectionsUnited States
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Natera, Inc.Children's Hospital of Philadelphia; Montefiore Medical Center; University of... and other collaboratorsCompletedPrader-Willi Syndrome | DiGeorge Syndrome | 22q11 Deletion Syndrome | Angelman Syndrome | Trisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy X | Sex Chromosome Abnormalities | 1p36 Deletion Syndrome | Cri-du-Chat SyndromeUnited States, Australia, Ireland, Spain, Sweden, United Kingdom
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International Spine Study Group FoundationMedtronic; Globus Medical Inc; SI-BONE, Inc.RecruitingScoliosis | Kyphosis | Adult Spinal Deformity | Sagittal ImbalanceUnited States, Canada
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The Rogosin InstituteWeill Medical College of Cornell UniversityCompletedAutosomal Dominant Polycystic KidneyUnited States
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Montefiore Medical CenterDuke UniversityCompleted
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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Mark GladwinCompletedSickle Cell DiseaseUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)TerminatedSickle Cell DiseaseUnited States
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Agios Pharmaceuticals, Inc.CompletedHealthy Volunteers | Anemia, Sickle CellUnited States, Spain, Denmark
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CephalonCompletedPain | Cancer | Sickle Cell Anemia | Severe BurnsUnited States, Canada, Puerto Rico
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States
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Foundation for Prader-Willi ResearchRTI InternationalRecruitingPrader-Willi SyndromeUnited States
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National Human Genome Research Institute (NHGRI)RecruitingGenetic Disease | GenomicsUnited States, Sierra Leone
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Editas Medicine, Inc.RecruitingSickle Cell Disease | HemoglobinopathiesUnited States, Canada
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PfizerPfizerActive, not recruitingSickle Cell DiseaseUnited States, Lebanon, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AIndia
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Bausch Health Americas, Inc.CompletedSickle Cell DiseaseUnited States, Canada, Kenya
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Mirum Pharmaceuticals, Inc.Active, not recruitingCholestatic Liver Disease | Alagille Syndrome | Progressive Familial Intrahepatic CholestasisUnited States, United Kingdom, France, Belgium, Poland, Brazil, Mexico
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Weill Medical College of Cornell UniversityThe Rogosin InstituteEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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NYU Langone HealthCompletedSystemic Lupus Erythematosus | Congenital Heart Block | Sjogren's Syndrome | Neonatal LupusUnited States
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Dana-Farber Cancer InstituteNovartis PharmaceuticalsCompletedTuberous Sclerosis Complex | TSC1 | TSC2 | MTORUnited States
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Oregon Health and Science UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingPancreatitis | Pancreatitis, Acute | Pancreas Divisum | Pancreatitis Idiopathic | Pancreas InflamedUnited States, Canada, Netherlands
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NICHD Global Network for Women's and Children's...Thomas Jefferson University; Thrasher Research Fund; RTI InternationalCompletedNeurodevelopmental AbnormalityUnited States, Zambia, Congo, The Democratic Republic of the, India, Pakistan, Guatemala
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland
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University Hospital, EssenRecruitingHereditary Hemorrhagic TelangiectasiaGermany
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LivaNovaTerminatedHeart Diseases | Cardiovascular Diseases | Congenital Abnormalities | Pathological Conditions, Anatomical | Aortic Stenosis | Heart Valve Diseases | Aortic Regurgitation | Aortic Valve Insufficiency | Cardiovascular AbnormalitiesUnited States
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Recruiting
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VentureMed Group Inc.CompletedArteriovenous Fistula StenosisUnited States
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Reprixys Pharmaceutical CorporationNational Heart, Lung, and Blood Institute (NHLBI); Food and Drug Administration...CompletedSickle Cell DiseaseUnited States, Brazil, Jamaica
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PfizerPfizerRecruitingSickle Cell DiseaseUnited States, Nigeria, Kenya, Lebanon
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University of New MexicoUniversity of California, San FranciscoRecruitingCerebral Cavernous MalformationUnited States