- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Glycogen Storage Disease
Total 379541 results
-
Ari ZimranPfizerActive, not recruitingGaucher Disease, Type 3Israel, Turkey, India
-
CEN BiotechTakeda; BioClinica, Inc.Completed
-
ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
-
ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
-
ShireApproved for marketingGaucher Disease, Type 1United States
-
University Research Foundation for Lysosomal Storage...University of PittsburghCompletedGaucher DiseaseUnited States
-
Shaare Zedek Medical CenterCompletedGaucher Disease Type 1Israel
-
Nantes University HospitalCompletedPatients With Gaucher's DiseaseFrance
-
National Institute of Mental Health (NIMH)Completed
-
University of MinnesotaRecruitingGaucher Disease, Type 3United States
-
TakedaActive, not recruiting
-
Shaare Zedek Medical CenterShireCompletedGaucher Disease, Type 1
-
Shaare Zedek Medical CenterPfizerCompletedGaucher Disease, Type 1
-
National Taiwan University HospitalSanofiCompleted
-
ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
-
ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
-
PfizerWithdrawnType 1 Gaucher DiseaseUnited States
-
National Taiwan University HospitalActelionUnknown
-
ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
-
National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
-
Exsar CorporationSuspendedType I Gaucher DiseaseUnited States
-
SanofiCompletedGaucher's DiseaseUnited States
-
ShireCompletedGaucher DiseaseUnited States, Spain, United Kingdom, Israel
-
ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
-
ShireCompletedGaucher Disease, Type 3Egypt, India, Tunisia
-
ISU Abxis Co., Ltd.CompletedGaucher Disease, Type 1
-
Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
-
Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
-
Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India
-
ISU Abxis Co., Ltd.Completed
-
Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
-
Crolll GmbhUniversity of Magdeburg; Estimate, GmbHCompletedNon-alcoholic Steatohepatitis | Increased Iron Storage / Disturbed DistributionGermany
-
Massachusetts General HospitalGenzyme, a Sanofi Company; Scott and White Hospital & ClinicTerminatedKidney Diseases | Genetic Diseases, X-Linked | End Stage Renal Disease | ESRD | Fabry Disease | Rare DiseasesUnited States
-
AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
-
Freeline TherapeuticsRecruitingGaucher Disease, Type 1Spain, Israel, United States, United Kingdom, Brazil, Germany, Paraguay
-
He HuangLingyi Biotech Co., Ltd.Recruiting
-
CANbridge (Suzhou) Bio-pharma Co., Ltd.RecruitingGaucher Disease, Type 1 | Gaucher Disease, Type 3China
-
Cambridge University Hospitals NHS Foundation TrustMedical Research Council; National Institute for Health Research, United KingdomRecruitingGaucher Disease, Type III | Gaucher Disease, Type IUnited Kingdom
-
SanofiCompleted
-
Shaare Zedek Medical CenterCompleted
-
Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
-
Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, Israel, South Africa, United States
-
SanofiCompleted
-
AVROBIOWithdrawn
-
Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, United States
-
CENTOGENE GmbH RostockCompletedLysosomal Storage Diseases | Sphingolipidoses | Gaucher DiseaseAlbania, Greece, India, Israel, Morocco, Pakistan, Spain
-
National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States
-
Shoshana VilkGenzyme, a Sanofi CompanyCompletedGaucher Disease | Patient Reported OutcomeIsrael
-
Lysosomal and Rare Disorders Research and Treatment...RecruitingBone Diseases | Gaucher DiseaseUnited States