- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Hereditary Angioedema in United Kingdom
Total 1441 results
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Cornea Research Foundation of AmericaCompletedBullous Keratopathy | Fuchs' Endothelial Corneal Dystrophy | Iridocorneal Endothelial Syndrome | Posterior Polymorphous DystrophyUnited States
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Ultragenyx Pharmaceutical IncCompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States, Israel
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The University of Texas Medical Branch, GalvestonTerminatedHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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Georgetown UniversityVirginia Commonwealth University; Cornell UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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Baxalta now part of ShireCompletedHereditary Thrombotic Thrombocytopenic Purpura (TTP)United States, Germany, United Kingdom, Switzerland, Austria, Japan, Poland
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Washington University School of MedicineCompletedVasculopathy, Retinal, With Cerebral Leukodystrophy | Cerebroretinal Vasculopathy, HereditaryUnited States
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Gyroscope Therapeutics LimitedNovartis PharmaceuticalsActive, not recruitingEye Diseases | Macular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal Disease | Macular AtrophyUnited States, United Kingdom
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Vanderbilt UniversityCompletedHypertension | Diabetes Type 2United States
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National Institute of Allergy and Infectious Diseases...CompletedHypotension | Angioedema | Anaphylaxis | BronchospasmUnited States
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Memorial Sloan Kettering Cancer CenterHarvard University; Broad InstituteActive, not recruitingLynch Syndrome | Hereditary Colonic Polyposis SyndromesUnited States
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Emory UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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University of PittsburghCompletedLynch Syndrome | Hereditary Diffuse Gastric Cancer | FAP | Peutz-Jeghers Syndrome | Juvenile Polyposis SyndromeUnited States
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The University of Texas Medical Branch, GalvestonActive, not recruitingHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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The Cleveland ClinicCompletedHereditary Hemorrhagic Telangiectasia | Idiopathic Vascular EctasiaUnited States
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National Human Genome Research Institute (NHGRI)Completed
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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Jaeb Center for Health ResearchUsher 1F Collaborative; Marjorie C. Adams FoundationActive, not recruitingRetinal Degeneration | Retinitis Pigmentosa | Eye Diseases, HereditarySwitzerland, United States, Germany, Netherlands, Canada, France, Israel
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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State University of New York at BuffaloHadley Jo FoundationCompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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State University of New York at BuffaloThe Callum McKeefery and Nikki Albano McKeefery Pediatric Division of Genetics...CompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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Ambry GeneticsBeth Israel Deaconess Medical Center; HonorHealth Research Institute; University...CompletedPancreatic Ductal AdenocarcinomaUnited States
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Calliditas Therapeutics ABRecruitingAlport SyndromeUnited Kingdom, Spain, Czechia
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Lassen Therapeutics Inc.RecruitingEye Diseases | Endocrine System Diseases | Thyroid Eye Disease | Graves Ophthalmopathy | Orbital Diseases | Thyroid Associated Ophthalmopathy | Graves Orbitopathy | ProptosisUnited States, United Kingdom, Spain
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Opus Genetics, IncRecruiting
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University of PittsburghCompleted
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Tufts UniversityAmerican Pistachio GrowersRecruitingEye Diseases | Macular Degeneration | Retinal Degeneration | Retinal DiseasesUnited States
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Geisinger ClinicNational Cancer Institute (NCI)CompletedLynch SyndromeUnited States
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Georgetown UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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Novartis PharmaceuticalsCompletedHereditary Periodic FeversBelgium, Italy, Japan, Russian Federation, Turkey, Spain, Germany, United Kingdom, France, United States, Ireland, Israel, Canada, Hungary, Netherlands, Switzerland
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Massachusetts General HospitalNational Cancer Institute (NCI); Boston Medical CenterCompletedGenetic TestingUnited States
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National Eye Institute (NEI)CompletedHealthy Volunteer | Retinal Disease | Inherited Retinal DegenerationUnited States
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Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
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Fox Chase Cancer CenterRecruiting
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Boston Children's HospitalBoston Children's Hospital - Children's Rare Disease Cohorts InitiativeRecruitingMovement Disorders | Neurodegenerative Diseases | Motor Neuron Disease | Spasticity, Muscle | Pediatric Disorder | Hereditary Spastic ParaplegiaUnited States
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Boston UniversityNational Institute on Minority Health and Health Disparities (NIMHD); University... and other collaboratorsRecruitingLynch Syndrome | Hereditary Breast and Ovarian CancerUnited States
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Baylor College of MedicineNational Eye Institute (NEI); National Institutes of Health (NIH)RecruitingColoboma | Microphthalmia | AnophthalmiaUnited States
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National Eye Institute (NEI)RecruitingColobomaUnited States
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National Cancer Institute (NCI)Active, not recruitingCancer | Hereditary Neoplasms | Genetic Predisposition to Cancer | EnvironmentUnited States
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Children's Hospital Medical Center, CincinnatiGenzyme, a Sanofi Company; Virginia Commonwealth UniversityCompletedHereditary Pulmonary Alveolar ProteinosisUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Completed
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GlaxoSmithKlineTerminatedTelangiectasia, Hereditary HemorrhagicUnited States, Canada
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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National Institute of Neurological Disorders and...CompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Hereditary Spastic ParaplegiaUnited States
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ProQR TherapeuticsTerminatedEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium
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Novartis PharmaceuticalsCompletedBreast Cancer | Advanced Solid Tumors | Cowden SyndromeNetherlands, Spain, Germany, United Kingdom, United States
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National Human Genome Research Institute (NHGRI)CompletedBreast CancerUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); National Institutes of Health (NIH)RecruitingColorectal Cancer | Lynch Syndrome | T CellsUnited States
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Kaiser PermanenteM.D. Anderson Cancer Center; Dana-Farber Cancer Institute; Vanderbilt University and other collaboratorsCompletedLynch Syndrome | Colon CancerUnited States
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UNC Lineberger Comprehensive Cancer CenterUniversity of North Carolina, Chapel Hill; National Center for Advancing Translational... and other collaboratorsRecruitingLynch SyndromeUnited States