- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Hereditary Ataxia in United States
Total 1627 results
-
UNC Lineberger Comprehensive Cancer CenterCompletedEndometrial Hyperplasia | Endometrial Hyperplasia Without AtypiaUnited States
-
Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia
-
KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Israel, Netherlands, Spain, United Kingdom, Australia, Germany, South Africa, Slovakia, Austria, New Zealand, Romania, Canada, Japan
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedHereditary HemochromatosisUnited States
-
Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Albert Einstein College of MedicineRecruiting
-
4D Molecular TherapeuticsActive, not recruitingChoroideremiaUnited States
-
jCyte, IncCalifornia Institute for Regenerative Medicine (CIRM)CompletedRetinitis PigmentosaUnited States
-
US Department of Veterans AffairsCompletedRetinal Degeneration | Age Related MaculopathyUnited States
-
BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | PediatricSpain, Austria, Canada, France, Germany, Israel, Italy, Poland, Romania, United Kingdom
-
Wellstat TherapeuticsCompletedHereditary Orotic AciduriaUnited States
-
University of UtahCompletedDominantly Inherited Stargardt's Disease (STGD3)United States
-
Stanford UniversityCompletedEpistaxis | Hereditary Hemorrhagic Telangiectasia | HHT | Nose Bleeds | Nasal BleedingUnited States
-
AllerganCompletedRetinitis PigmentosaFrance, United States, Germany, Portugal
-
KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
-
Jonsson Comprehensive Cancer CenterBeiGene; Driven To CureWithdrawnMetastatic Renal Cell Carcinoma | Stage IV Renal Cell Cancer AJCC v8 | Papillary Renal Cell Carcinoma | Collecting Duct Carcinoma | Unresectable Renal Cell Carcinoma | Hereditary Leiomyomatosis and Renal Cell Carcinoma | Clear Cell Papillary Renal Neoplasm | Hereditary Papillary Renal Cell Carcinoma and other conditionsUnited States
-
ShireCompletedHereditary AngioedemaUnited States
-
Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Bulgaria, Canada, Hungary, Israel, Italy, Macedonia, The Former Yugoslav Republic of, Poland, Romania, Serbia, South Africa
-
National Cancer Institute (NCI)RecruitingLynch SyndromeUnited States, Puerto Rico
-
KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
-
ShireCompletedHereditary AngioedemaUnited States
-
Data Collection Analysis Business ManagementPAS Research ServicesUnknownHereditary CancerUnited States
-
Columbia UniversityNot yet recruiting
-
National Eye Institute (NEI)Completed
-
University of Kansas Medical CenterRecruitingBreast Cancer | Hereditary Breast and Ovarian CancerUnited States
-
Cedars-Sinai Medical CenterSientra, Inc.CompletedBreast Cancer | Hereditary Breast and Ovarian Cancer Syndrome | Breast Implant; ComplicationsUnited States
-
GenSight BiologicsRecruitingNon-syndromic Retinitis PigmentosaUnited States, France, United Kingdom
-
MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompletedAchromatopsiaUnited Kingdom, United States
-
MeiraGTx UK II LtdJanssen Research & Development, LLCCompleted
-
Brigham and Women's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingGenetic Predisposition to Disease | Hereditary DiseasesUnited States
-
The University of Texas at DallasEnrolling by invitationPrimary Progressive Aphasia | Apraxia of SpeechUnited States
-
National Eye Institute (NEI)The Emmes Company, LLCCompletedRetinitis PigmentosaUnited States
-
University of South FloridaBoston Children's HospitalCompletedPTEN Gene MutationUnited States
-
Johns Hopkins UniversityNational Institute of Nursing Research (NINR); National Eye Institute (NEI)Completed
-
SparingVisionActive, not recruitingRetinitis PigmentosaUnited States, France
-
PTC TherapeuticsCompletedAniridiaUnited States, Canada
-
M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedHigh-Frequency Microsatellite Instability | Mismatch Repair Gene Mutation | Mutation-Negative Lynch Syndrome | Mutation-Positive Lynch SyndromeUnited States
-
St George's, University of LondonTerminatedEndometrial Cancer | Hereditary Non-polyposis Colon Cancer (hmsh2, hmlh1, hpms1, hpms2)United Kingdom
-
MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompleted
-
Johns Hopkins UniversityNational Cancer Institute (NCI)RecruitingPancreatic Cancer, ATM, BRCA, Hereditary CancerUnited States
-
National Cancer Institute (NCI)CompletedGastric Cancer | Gastric NeoplasmsUnited States
-
University of Illinois at ChicagoWithdrawnDysplastic Nevus SyndromeUnited States
-
National Cancer Institute (NCI)CompletedHamartoma Syndrome, Multiple | Cowden's DiseaseUnited States
-
ShireCompletedHereditary AngioedemaUnited States, Australia, Israel, Canada, Hungary, Romania, Russian Federation, South Africa, Ukraine
-
University of California, Los AngelesNational Institute on Aging (NIA); University of Southern CaliforniaUnknownAlzheimer Disease | Corticobasal Degeneration | Primary Progressive Aphasia | Alzheimer Disease, Early Onset | Alzheimer Disease, Late Onset | Dementia, Alzheimer Type | Logopenic Progressive Aphasia | Visuospatial/Perceptual Abilities | Posterior Cortical Atrophy | Executive Dysfunction | Ideomotor ApraxiaUnited States
-
Novartis PharmaceuticalsCompletedEye Diseases | Age-Related Macular Degeneration | Macular Degeneration | Retinal Degeneration | Retinal Diseases | Wet Macular DegenerationUnited States, Puerto Rico
-
ProQR TherapeuticsActive, not recruitingEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium, Brazil, Canada, France, Germany, Italy, Netherlands, United Kingdom
-
Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
-
National Eye Institute (NEI)RecruitingRetinal Degeneration | Retinitis Pigmentosa | Stargardt's DiseaseUnited States