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Clinical Trials on Hereditary Fructose Intolerance in United States
Total 2070 results
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Vestibular SchwannomasUnited States
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National Institute of Neurological Disorders and...CompletedNeoplasms | Vestibular Disease | Nervous System DiseaseUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedClear Cell Sarcoma of the Kidney | Recurrent Wilms Tumor and Other Childhood Kidney Tumors | Stage III Wilms Tumor | Rhabdoid Tumor of the Kidney | Stage IV Wilms Tumor | Stage V Wilms Tumor | Stage I Wilms Tumor | Stage II Wilms TumorUnited States
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National Cancer Institute (NCI)CompletedFamilial Adenomatous PolyposisUnited States, Puerto Rico
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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Passage Bio, Inc.SuspendedLeukodystrophy, Globoid CellUnited States, Brazil, Netherlands, United Kingdom, Canada, Israel
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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James GossageHHT Foundation InternationalCompletedEpistaxis | Telangiectasia, Hereditary HemorrhagicUnited States
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Immunovant Sciences GmbHRecruitingThyroid Eye DiseaseUnited States, Belgium, Latvia, Hungary, Spain, Slovakia, Puerto Rico, New Zealand, Turkey
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IGermany, United Kingdom, France
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Cambridge University Hospitals NHS Foundation TrustUnknown
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University College London HospitalsJohns Hopkins University; Children's Hospital of Philadelphia; University of... and other collaboratorsCompletedCharcot-Marie-Tooth DiseaseUnited Kingdom
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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XOMA (US) LLCTerminatedBehcet's Disease UveitisUnited States
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis Type 1United States, Spain, Poland, Russian Federation
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House Ear InstituteUnknownMeningioma | Neurofibromatosis 2 | Schwannoma, VestibularUnited States
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National Cancer Institute (NCI)Not yet recruitingFamilial Adenomatous Polyposis | Colorectal Carcinoma | Colorectal Adenomatous Polyp | Multiple Adenomatous PolypsUnited States
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Dana-Farber Cancer InstituteCompletedSarcoma | Neuroblastoma | Wilms Tumor | Pediatric Solid TumorUnited States
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Neuroversion, Inc.Active, not recruitingChronic Fatigue Syndrome | Myalgic Encephalomyelitis | Encephalomyelitis, Myalgic | Chronic Fatigue Disorder | Chronic Fatigue and Immune Dysfunction Syndrome | Postviral Fatigue Syndrome | Systemic Exertion Intolerance Disease | Infectious Mononucleosis-Like Syndrome, Chronic | Chronic Fatigue-Fibromyalgia...United States
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Vitaccess LtdPharnext SA; Charcot-Marie-Tooth Association; ACMT-Rete per la malattia di Charcot-Marie-Tooth... and other collaboratorsRecruitingCharcot-Marie-Tooth DiseaseUnited Kingdom
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Cure HHTUniversity of Colorado, Denver; Massachusetts General Hospital; Mayo Clinic; Children... and other collaboratorsRecruitingArteriovenous Malformations | Epistaxis | Hereditary Hemorrhagic Telangiectasia | GastroIntestinal Bleeding | Telangiectasia | Vascular Malformation | Cerebral Arteriovenous MalformationsUnited States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of MedicineNot yet recruitingHepatocellular Carcinoma | Liposarcoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Malignant Rhabdoid Tumor | Yolk Sac Tumor | Embryonal Sarcoma of LiverUnited States
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University of Texas Southwestern Medical CenterNational Cancer Institute (NCI); Howard Hughes Medical InstituteRecruitingKidney Cancer | Renal Cell Carcinoma | Urothelial Carcinoma | Hereditary Leiomyomatosis and Renal Cell Cancer | Metastatic Urothelial Carcinoma | Chromophobe Renal Cell Carcinoma | Papillary Renal Cell Carcinoma | HLRCC | Clear Cell Carcinoma | Metastatic Kidney Cancer | Fumarate Hydratase Deficiency | Succinate...United States
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Massachusetts Eye and Ear InfirmaryEnrolling by invitationDizziness | Neurofibromatosis 2 | Vestibular Schwannoma | Vestibular Disorder | Inner Ear DiseaseUnited States
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National Cancer Institute (NCI)WithdrawnSarcoma | Osteosarcoma | Brain Tumor | Neuroblastoma | Wilms TumorUnited States
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NYU Langone HealthGlaxoSmithKlineCompletedNeurofibromatosis 2 | Vestibular SchwannomaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedSarcoma | Lung Cancer | Brain and Central Nervous System Tumors | Neuroblastoma | Intraocular Melanoma | Melanoma (Skin) | RetinoblastomaUnited States
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Meningiomas | Vestibular SchwannomasUnited States
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Acrotech Biopharma Inc.National Cancer Institute (NCI)CompletedSarcoma | Lymphoma | Leukemia | Neuroblastoma | Brain Tumors | Wilms TumorUnited States
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Jonsson Comprehensive Cancer CenterNovartis PharmaceuticalsTerminatedNeuroma, Acoustic | Neurofibromatosis Type 2United States
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Cardiff UniversityNovartisUnknownTuberous SclerosisUnited Kingdom
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Immunovant Sciences GmbHRecruitingThyroid Eye DiseaseUnited States, Italy, Poland, United Kingdom, Canada, Israel, Germany, Japan, Georgia
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedMeningioma | Neuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Von Hippel-Lindau Syndrome | Metastatic Well Differentiated Neuroendocrine Neoplasm | Somatostatin Positive Neoplastic Cells PresentUnited States
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Massachusetts Eye and Ear InfirmaryNo longer availableNeurofibromatosis Type 2 | Severe Profound Sensorineural Hearing LossUnited States
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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University of LeicesterChildren's Cancer and Leukaemia Group; Gesellschaft fur Padiatrische Onkologie... and other collaboratorsUnknownKidney CancerUnited Kingdom, Germany, France, Netherlands
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London North West Healthcare NHS TrustUnknownFamilial Adenomatous PolyposisUnited Kingdom
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Roswell Park Cancer InstituteCompletedLymphoma | Brain and Central Nervous System Tumors | Neuroblastoma | RetinoblastomaUnited States
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Alnylam PharmaceuticalsCompletedAcute Hepatic PorphyriaUnited States, Belgium, Bulgaria, France, Italy, Mexico, Spain, Taiwan, United Kingdom, Netherlands, Korea, Republic of, Switzerland, Czechia, Poland, Finland, Australia, Germany, Israel, Norway, South Africa
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Food and Drug Administration (FDA)National Eye Institute (NEI)RecruitingAge-Related Macular Degeneration | Retinal Degeneration | Retinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Rod Dystrophy | Cone Rod Dystrophy | Hydroxychloroquine Retinopathy | Late-Onset Retinal Degeneration | Rod Cone DystrophyUnited States
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University of IowaChildren's Hospital of Philadelphia; University College London Hospitals; National... and other collaboratorsRecruitingCharcot Marie Tooth DiseaseUnited States, United Kingdom, Australia, Italy
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Cutaneous Neurofibroma | Optic Nerve GliomaUnited States
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UNC Lineberger Comprehensive Cancer CenterCompletedOptic Glioma | Plexiform Neurofibroma | Neurofibromatosis-1United States
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Sling Therapeutics, Inc.Active, not recruitingEye Diseases | Endocrine System Diseases | Thyroid Diseases | Thyroid Eye Disease | Graves Ophthalmopathy | Exophthalmos | Orbital Diseases | Thyroid Associated Ophthalmopathy | Graves Orbitopathy | Proptosis | IGF1R | HashimotoUnited States, Spain, Italy, United Kingdom, Canada
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FDA Office of Orphan Products DevelopmentCompletedNeurofibromatosis 2United States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingHereditary Breast and Ovarian Cancer Syndrome | Premenopausal | Deleterious BARD1 Gene Mutation | Deleterious BRCA1 Gene Mutation | Deleterious BRCA2 Gene Mutation | Deleterious BRIP1 Gene Mutation | Deleterious EPCAM Gene Mutation | Deleterious MLH1 Gene Mutation | Deleterious MSH2 Gene Mutation | Deleterious... and other conditionsUnited States
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Children's Oncology GroupRecruitingBilateral Retinoblastoma | Childhood Intraocular Retinoblastoma | Unilateral Retinoblastoma | Group D Retinoblastoma | Stage I RetinoblastomaUnited States, Australia
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University Hospitals Bristol and Weston NHS Foundation...University College, London; The Tuberous Sclerosis AssociationActive, not recruitingTuberous Sclerosis ComplexUnited Kingdom
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University College London HospitalsKingston University; Charcot Marie Tooth United KingdomCompletedCharcot-Marie-Tooth Disease, Type IAUnited Kingdom
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Hoffmann-La RocheRecruitingThyroid Eye Disease | TEDJapan, Australia, Singapore, United States, Argentina, Germany, Italy, Hong Kong