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Clinical Trials on Hereditary Retinal Dystrophies in United States
Total 7311 results
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE MyopathyUnited States, Israel
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Krystal Biotech, Inc.Stanford UniversityWithdrawnDystrophic Epidermolysis Bullosa | DEB - Dystrophic Epidermolysis BullosaUnited States
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Phoenix Tissue Repair, Inc.Phoenix Tissue Repair, a BridgeBio companyCompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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University of PennsylvaniaNational Eye Institute (NEI)Active, not recruitingRetinal Diseases | Amaurosis of LeberUnited States
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Columbia UniversityTerminatedEpidermolysis BullosaUnited States
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Belite Bio, IncActive, not recruitingStargardt Disease 1United States, Australia, Belgium, China, France, Germany, Hong Kong, Netherlands, Switzerland, Taiwan, United Kingdom
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Alkeus Pharmaceuticals, Inc.Enrolling by invitationStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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Phoenicis TherapeuticsNot yet recruitingDystrophic Epidermolysis BullosaUnited States
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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ProQR TherapeuticsActive, not recruitingEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium, Brazil, Canada, France, Germany, Italy, Netherlands, United Kingdom
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Astellas Institute for Regenerative MedicineCompleted
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IVERIC bio, Inc.Active, not recruitingStargardt Disease 1Italy, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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Abeona Therapeutics, IncCompletedEpidermolysis Bullosa | Recessive Dystrophic Epidermolysis BullosaUnited States
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University of Colorado, DenverRecruitingHearing Loss | Smith-Lemli-Opitz Syndrome | Cone-Rod DystrophyUnited States
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EmmecellActive, not recruitingEndothelial Dysfunction | Corneal Edema | Fuchs Dystrophy | Corneal Endothelial Dystrophy | Bullous Keratopathy | Pseudophakic Bullous Keratopathy | Corneal Endothelial Dysfunction | Fuchs Endothelial Corneal Dystrophy | Moderate Corneal Endothelial DecompensationUnited States
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Astellas Institute for Regenerative MedicineCompleted
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St. Jude Children's Research HospitalActive, not recruitingRetinoblastomaUnited States
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Genzyme, a Sanofi CompanyCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Gene Therapy | Age-Related Maculopathies | Age-Related Maculopathy | Retinal Neovascularization | Maculopathies, Age-Related | Maculopathy, Age-Related | Therapy, GeneUnited States
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Children's Hospital Medical Center, CincinnatiTerminatedRetinoblastomaUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...TerminatedRetinoblastomaUnited States
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Wills EyeThomas Jefferson UniversityCompletedRetinoblastomaUnited States
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M.D. Anderson Cancer CenterTerminatedRetinoblastomaUnited States
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Memorial Sloan Kettering Cancer CenterCompleted
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Memorial Sloan Kettering Cancer CenterUniversity of Pennsylvania; Milton S. Hershey Medical Center; New York Presbyterian...Completed
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Jonsson Comprehensive Cancer CenterBeiGene; Driven To CureWithdrawnMetastatic Renal Cell Carcinoma | Stage IV Renal Cell Cancer AJCC v8 | Papillary Renal Cell Carcinoma | Collecting Duct Carcinoma | Unresectable Renal Cell Carcinoma | Hereditary Leiomyomatosis and Renal Cell Carcinoma | Clear Cell Papillary Renal Neoplasm | Hereditary Papillary Renal Cell Carcinoma and other conditionsUnited States
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Abeona Therapeutics, IncRecruitingEpidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | RDEBUnited States
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Washington University School of MedicineActive, not recruiting
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Gemini Therapeutics, Inc.TerminatedMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal DiseaseUnited States
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Targeted Therapy Technologies, LLCActive, not recruiting
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St. Jude Children's Research HospitalUniversity of Wisconsin, MadisonCompletedRetinoblastomaUnited States
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St. Jude Children's Research HospitalNational Cancer Institute (NCI)Completed
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Weill Medical College of Cornell UniversityMemorial Sloan Kettering Cancer CenterCompletedRetinoblastomaUnited States
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Castle Creek Biosciences, LLC.Active, not recruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Memorial Sloan Kettering Cancer CenterRecruitingRetinoblastoma | Pediatric RetinoblastomaUnited States
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University of MiamiNational Eye Institute (NEI)CompletedGlaucoma | Macular Degeneration | Retinal Degeneration | Optic Neuropathy | Glaucoma Suspect | Visual Pathway DisorderUnited States
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Stanford UniversityWithdrawnRetinoblastoma | Eye CancerUnited States
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Stanford UniversityTerminated
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St. Jude Children's Research HospitalCompletedRetinoblastomaUnited States
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PfizerCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Age-Related Maculopathies | Age-Related MaculopathyUnited States
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Kubota Vision Inc.CompletedStargardt Disease | Macular AtrophyUnited States
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St. Jude Children's Research HospitalNational Cancer Institute (NCI)Completed
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University of Texas Southwestern Medical CenterRecruiting
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TyrogenexInternational Drug Development Institute; SynteractHCRTerminatedEye Diseases | Macular Degeneration | Retinal Degeneration | Retinal Diseases | Age-Related Macular Degeneration (AMD) | Exudative Age-related Macular Degeneration | AMD | Macular Degeneration, Age-related, 10United States
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Children's Hospital Medical Center, CincinnatiWithdrawn
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National Eye Institute (NEI)CompletedHereditary Eye DiseaseUnited States
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National Eye Institute (NEI)Completed
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M.D. Anderson Cancer CenterRecruiting