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Clinical Trials on Hereditary Sensory and Autonomic Neuropathies
Total 6443 results
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The University of Texas Health Science Center at...National Institute of General Medical Sciences (NIGMS)RecruitingKidney Neoplasms | Bone Cancer | Thyroid Neoplasms | Pheochromocytoma | Paraganglioma | Other Cancer | Inherited Cancer Syndrome | Associated ConditionsUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedSarcoma | Kidney Cancer | Neuroblastoma | Retinoblastoma | Adrenocortical Carcinoma | Gastrointestinal Carcinoid TumorUnited States
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University of AarhusCompletedVascular Diseases | Kidney Diseases | Sleep Apnea | Diabetic Nephropathy Type 2 | Arterial Stiffness | Coronary Atheroscleroses | Heart InsufficiencyDenmark
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Novartis PharmaceuticalsCompletedLymphangioleiomyomatosis (LAM) | Tuberous Sclerosis Complex (TSC)United States, United Kingdom, Germany, Italy, Russian Federation, Netherlands, Japan, Canada, Poland, France, Spain
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Massachusetts Eye and Ear InfirmaryEnrolling by invitationDizziness | Neurofibromatosis 2 | Vestibular Schwannoma | Vestibular Disorder | Inner Ear DiseaseUnited States
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NYU Langone HealthGlaxoSmithKlineCompletedNeurofibromatosis 2 | Vestibular SchwannomaUnited States
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Recursion Pharmaceuticals Inc.RecruitingNeurofibromatosis Type 2United States
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Jonsson Comprehensive Cancer CenterNovartis PharmaceuticalsTerminatedNeuroma, Acoustic | Neurofibromatosis Type 2United States
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Massachusetts General HospitalUnited States Department of Defense; AstraZenecaCompletedMeningioma | Neurofibromatosis 2United States
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Massachusetts Eye and Ear InfirmaryJohns Hopkins University; Mayo Clinic; Stanford University; Ohio State University; Nationwide Children's HospitalTerminatedMeningioma | Neurofibromatosis Type 2 | Vestibular Schwannoma | Acoustic NeuromaUnited States
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Vestibular SchwannomasUnited States
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Li PengBetta Pharmaceuticals Co., Ltd.CompletedNeurofibromatosis Type 2 | Vestibular SchwannomaChina
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National Institute of Neurological Disorders and...CompletedNeoplasms | Vestibular Disease | Nervous System DiseaseUnited States
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Fakultas Kedokteran Universitas IndonesiaUnknownVogt-Koyanagi-Harada Disease | Behçet Disease | Posterior Uveitis | Intermediate Uveitis | Autoimmune Uveitis | Idiopathic Uveitis | Noninfectious Panuveitis | Anterior Uveitis IdiopathicIndonesia
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 2 | Vestibular SchwannomaUnited States
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Beijing Tiantan HospitalShandong Simcere-Medgenn Bio-pharmaceutical Co., LtdCompletedNeurofibromatosis Type 2 | Vestibular SchwannomaChina
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Shenzhen Second People's HospitalGuangzhou Women and Children's Medical Center; Shenzhen UniversityRecruitingAdrenoleukodystrophy | Metachromatic LeukodystrophyChina
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University of Alabama at BirminghamMemorial Sloan Kettering Cancer CenterActive, not recruitingNeurofibromatosis 2 | Progressive Vestibular Schwannoma (VS)United States
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University of Alabama at BirminghamGenentech, Inc.CompletedNeurofibromatosis Type 2 | Progressive Vestibular SchwannomasUnited States
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Meningiomas | Vestibular SchwannomasUnited States
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University Hospital TuebingenNational Center for Tumor Diseases, HeidelbergCompletedNeurofibromatosis Type 2 | Vestibular Schwannoma | Acoustic NeuromaGermany
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Charite University, Berlin, GermanyUnknownPancreatic Neoplasms | Crohn Disease | Ulcerative Colitis | Familial Adenomatous Polyposis | Diverticulitis | Hepatobiliary Neoplasm | Bowel Obstruction | Cancer of the Gastrointestinal Tract | Stoma Ileostomy | Bowel Ischemia | Abnormality of the Gastrointestinal Tract | Symptomatic Disorders of the Gastrointestinal...Germany
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Azienda Ospedaliero-Universitaria Consorziale Policlinico...Institute of Biomembranes, Bioenergetics and Molecular Biotechnologies; Istituti... and other collaboratorsCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD) | IgA Nephropathy (IgAN) | Diabetic Kidney Disease (DKD) | Advanced-Chronic Kidney Disease (CKD)Italy
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University of California, San FranciscoUnited States Department of DefenseRecruitingMultiple Sclerosis, Chronic Progressive | Multiple Sclerosis, Relapsing-Remitting | Multiple Sclerosis (MS) | Multiple Sclerosis Relapse | Multiple Sclerosis, Primary Progressive | Multiple Sclerosis Brain Lesion | Multiple Sclerosis BenignUnited States
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Jazz PharmaceuticalsRecruitingSeizure in Participants With Tuberous Sclerosis Complex | Seizure in Participants With Dravet Syndrome | Seizure in Participants With Lennox-Gastaut SyndromeUnited States
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Jennerex BiotherapeuticsSolving Kids' CancerCompletedLymphoma | Neuroblastoma | Rhabdomyosarcoma | Wilm's Tumor | Ewing's SarcomaUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingNeurodegenerative Diseases | Ataxia | Cerebellar Ataxia | Leukodystrophy | Adrenomyeloneuropathy | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation | Leukoencephalopathy With Brain Stem and Spinal Cord Involvement and High Lactate Syndrome (Disorder)United States
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Istanbul UniversityUnknownCOVID | FMF | Behcet DiseaseTurkey
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Children's National Research InstituteRecruitingSoft Tissue Sarcoma | Ewing Sarcoma | Bone Metastases | Solid Tumors | Rhabdomyosarcoma | Wilms Tumor | Germ Cell Tumor | Hepatic Tumor | Malignant Epithelial NeoplasmUnited States
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National Cancer Institute (NCI)WithdrawnSarcoma | Lymphoma | Brain Neoplasms | Osteosarcoma | Wilm's TumorUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedSarcoma | Kidney Cancer | Ovarian Cancer | Brain and Central Nervous System Tumors | Chordoma | Neuroblastoma | Retinoblastoma | Liver Cancer | Childhood Germ Cell TumorUnited States
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New York Medical CollegeRecruitingEwing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Germ Cell TumorUnited States
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University of Colorado, DenverNational Institute of Nursing Research (NINR); University of California, San...CompletedParkinson Disease | Alzheimer Disease | Lewy Body Disease | Parkinsonism | Supranuclear Palsy, Progressive | Parkinsonism Vascular | Multiple System Atrophy | Corticobasal Degeneration | Frontotemporal Dementia | Primary Progressive Aphasia | Vascular DementiaUnited States
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Memorial Sloan Kettering Cancer CenterRecruitingSolid Tumor | Rhabdoid Tumor | Wilms Tumor | Nephroblastoma | Malignant Peripheral Nerve Sheath Tumors | MPNST | XPO1 Gene MutationUnited States
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Brown UniversityTaiho Oncology, Inc.RecruitingSoft Tissue Sarcoma | Advanced Breast Cancer | SCLC | Bladder Cancer | Endometrial Cancer | Treatment-Refractory Solid Tumors | Retinoblastoma DeficiencyUnited States
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University of PennsylvaniaMichael J. Fox Foundation for Parkinson's ResearchCompletedParkinson's Disease | Myasthenia Gravis | Spinal Cord Injuries | Multiple System Atrophy | Progressive Supranuclear Palsy | Essential Tremor | Alzheimer's Disease | Diffuse Lewy Body Disease | Drug Induced Parkinson's DiseaseUnited States
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dr. Laura C. G. de Graaff-HerderRecruitingDisorders of Sex Development | Congenital Adrenal Hyperplasia | Tuberous Sclerosis | Kallmann Syndrome | Prader-Willi Syndrome | Neurofibromatosis | Rett Syndrome | 22q11 Deletion Syndrome | Turner Syndrome | Noonan Syndrome | Allan-Herndon-Dudley Syndrome | Saethre-Chotzen Syndrome | Congenital Hypopituitarism | Cornelia... and other conditionsNetherlands
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Travere Therapeutics, Inc.RecruitingFocal Segmental Glomerulosclerosis | Immunoglobulin A Nephropathy | Minimal Change Disease | Alport Syndrome | IgA VasculitisUnited States, Italy, Netherlands, Poland, Spain, United Kingdom, Germany, Sweden
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National Cancer Institute (NCI)CompletedOsteosarcoma | Acute Lymphoblastic Leukemia | Ewing Sarcoma | Neurofibromatosis Type 1 | NeuroblastomaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Testicular Germ Cell Tumor | Ovarian Cancer | Brain and Central Nervous System Tumors | Unspecified Adult Solid Tumor, Protocol Specific | Retinoblastoma | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Visionary Intelligence Ltd.Peking University First Hospital; Beijing Municipal Science & Technology CommissionCompletedDiabetic Retinopathy | Retinal Vein Occlusion | Retinitis Pigmentosa | Optic Atrophy | Retinal Detachment | Epiretinal Membrane | Macular Holes | Central Serous Chorioretinopathy | Retinal Artery Occlusion | Suspect Glaucoma | Pathologic Myopia | Nonexudative Age-related Macular Degeneration | Exudative Age Related...China
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedMeningioma | Neuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Von Hippel-Lindau Syndrome | Metastatic Well Differentiated Neuroendocrine Neoplasm | Somatostatin Positive Neoplastic Cells PresentUnited States
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Istanbul University - Cerrahpasa (IUC)CompletedQuality of Life | Multiple Sclerosis | Neuropathic Pain | Incontinence, Urinary | Disabilities Multiple | Incontinence BowelTurkey
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Assistance Publique - Hôpitaux de ParisRecruitingAdrenoleukodystrophy | Adrenomyeloneuropathy | Metachromatic Leukodystrophy | Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaFrance
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Masonic Cancer Center, University of MinnesotaTerminatedSickle Cell Disease | Thalassemia | Cerebral Adrenoleukodystrophy | Inherited Metabolic Disorders | High Risk Hematologic DisordersUnited States
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Université de MontréalWithdrawnGlaucoma | Cataract | Astigmatism | Myopia | Retinopathy of Prematurity | Retinoblastoma | Hyperopia | Amblyopia | Xerophthalmia | TrachomaHaiti
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Massachusetts Eye and Ear InfirmaryNo longer availableNeurofibromatosis Type 2 | Severe Profound Sensorineural Hearing LossUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Adult Kidney Wilms Tumor | Beckwith-Wiedemann Syndrome | Childhood Kidney Wilms Tumor | Diffuse Hyperplastic Perilobar Nephroblastomatosis | Rhabdoid Tumor of the Kidney | Stage V Kidney...United States, Canada, Australia, New Zealand, Puerto Rico, Israel