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Clinical Trials on Hurler Syndrome (MPS I)
Total 796 results
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Hospital de Clinicas de Porto AlegreThe Isaac FoundationActive, not recruitingMucopolysaccharidoses | Mucopolysaccharidosis VI | Morquio A Syndrome | Mucopolysaccharidosis IV A | MPS IV A | MPS VI | MPS - Mucopolysaccharidosis | Morquio Syndrome A | Morquio SyndromeBrazil
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Sangamo TherapeuticsTerminated
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Radboud University Medical CenterRecruitingMyelodysplastic Syndromes (MDS)Denmark, Switzerland, Serbia, Austria, Croatia, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Romania, Spain, Sweden, United Kingdom
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TakedaWithdrawn
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Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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Patricia I. Dickson, M.D.The Ryan FoundationTerminatedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Spinal Cord Compression | Hurler-Scheie SyndromeFinland, United States
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Stanford UniversityCelgene CorporationTerminatedLeukemia | Myelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML)United States
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Sunnybrook Health Sciences CentrePrincess Margaret Hospital, Canada; Juravinski Cancer CenterUnknownQuality of Life | Myelodysplastic Syndromes (MDS) | Red Blood Cell (RBC) TransfusionsCanada
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Dilşad SindelCompletedFemale Patients With Myofascial Pain Syndrome (MPS) Related to Upper Trapezius Active Trigger Points (TP)
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Novartis PharmaceuticalsRecruitingMyelodysplastic Syndrome (MDS)United States
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Otsuka Pharmaceutical Co., Ltd.RecruitingMyelodysplastic Syndrome (MDS)Japan
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Fondazione Italiana Sindromi Mielodisplastiche-ETSRecruiting
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Fujifilm Pharmaceuticals U.S.A., Inc.WithdrawnMyelodysplastic Syndrome (MDS)
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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TelikTerminatedMyelodysplastic Syndrome (MDS)United States
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Oncology Specialties, AlabamaTerminatedMyelodysplastic Syndrome (MDS)United States
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Case Comprehensive Cancer CenterRecruitingMyelodysplastic Syndrome (MDS)United States
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndrome (MDS)France, Spain, Belgium, Italy, Greece, Hungary, Germany
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Weill Medical College of Cornell UniversityNovartis PharmaceuticalsCompletedMyelodysplastic Syndrome (MDS)United States
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Incyte CorporationTerminatedMDS (Myelodysplastic Syndrome)United States
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Chinese Society of HematologyHarbin Institute of Hematology & OncologyUnknownMyelodysplastic Syndrome (MDS)
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Asociación Andaluza de Hematología y HemoterapiaCompleted
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Genzyme, a Sanofi CompanyTerminatedMyelodysplastic Syndrome (MDS)Germany, United Kingdom, France, Netherlands
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Heinrich-Heine University, DuesseldorfTerminatedMyelodysplastic Syndrome MDSGermany
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TelikTerminatedMyelodysplastic Syndrome (MDS)United States
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TelikCompletedMyelodysplastic Syndrome (MDS)United States
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Seagen Inc.CompletedMyelodysplastic Syndrome (MDS)United States
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Peter MacCallum Cancer Centre, AustraliaGlaxoSmithKline; Celgene CorporationCompletedMyelodysplastic Syndromes (MDS) | Acute Myeloid Leukaemia (AML)Australia
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndrome (MDS)United States, Australia, Austria, Belgium, Brazil, Canada, China, Czechia, France, Germany, Hungary, Israel, Italy, Japan, Korea, Republic of, Netherlands, Poland, Puerto Rico, Russian Federation, Spain, Taiwan, Turkey, United Kingdom
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Amphivena Therapeutics, Inc.CompletedMyelodysplastic Syndrome (MDS)United States
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CelgeneCompletedMyelodysplastic Syndrome (MDS)China
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Novartis PharmaceuticalsTerminatedMyelodysplastic Syndrome (MDS)Germany
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TelikCompletedMyelodysplastic Syndrome (MDS)United States
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Novartis PharmaceuticalsActive, not recruitingAcute Myeloid Leukemia (AML) | High-risk Myelodysplastic Syndrome (MDS)Spain, Singapore, Australia, Germany, Italy, Finland, United States
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University of UlmTerminatedAcute Myeloid Leukemia (AML) | High-risk Myelodysplastic Syndrome (MDS)Germany
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SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
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Helsinn Healthcare SACompletedMyelodysplastic Syndrome | MDSUnited States
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Sunnybrook Health Sciences CentreNot yet recruitingMyelodysplastic Syndromes | MDSCanada
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Astex Pharmaceuticals, Inc.CompletedMyelodysplastic Syndrome | MDSUnited States, Canada
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H. Lee Moffitt Cancer Center and Research InstituteCelgene CorporationCompletedMyelodysplastic Syndrome | MDSUnited States
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Groupe Francophone des MyelodysplasiesCelgeneRecruitingMyelodysplastic Syndromes | MDSFrance
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Ascentage Pharma Group Inc.Suzhou Yasheng Pharmaceutical Co., Ltd.RecruitingMyelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML)China
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Aprea TherapeuticsTerminatedMyelodysplastic Syndromes | MDSUnited States
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M.D. Anderson Cancer CenterNovartisCompletedMyelodysplastic Syndromes | MDSUnited States
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompleted
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalCompletedMPS IVA | Maroteaux Lamy Syndrome | MPS VI | Morquio Syndrome AUnited States
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Kiadis PharmaNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsWithdrawnMyelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML)United States
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Astex Pharmaceuticals, Inc.CompletedAML | MDS | CMMLUnited States, Canada