- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Hypoadrenocorticism, Familial
Total 1149 results
-
Institute of Cardiometabolism and Nutrition, FranceAmgenUnknownFamilial Hypercholesterolemia - HeterozygousFrance
-
Visirna Therapeutics HK LimitedNot yet recruitingFamilial Chylomicronemia Syndrome
-
Ionis Pharmaceuticals, Inc.AvailableFamilial Chylomicronemia Syndrome
-
Jiangsu HengRui Medicine Co., Ltd.CompletedMixed Hyperlipidemia | Non-familial HypercholesterolemiaChina
-
Abhimanyu GargCompletedFamilial Partial LipodystrophyUnited States
-
Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
-
UniQure Biopharma B.V.CompletedLipoprotein Lipase Deficiency | Familial Hyperlipoproteinemia Type 1 | Familial HyperchylomicronemiaGermany
-
Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
-
Organon and CoCompletedPrimary Hypercholesterolemia and Homozygous Familial Hypercholesterolemia (HoFH)
-
REGENXBIO Inc.CompletedHomozygous Familial Hypercholesterolemia (HoFH)United States
-
NYU Langone HealthNot yet recruitingFamilial DysautonomiaUnited States
-
NYU Langone HealthNot yet recruiting
-
University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
-
Regeneron PharmaceuticalsActive, not recruitingFamilial Partial Lipodystrophy | Metabolic AbnormalitiesUnited States, France, Spain, Turkey, United Kingdom
-
NYU Langone HealthCompletedFamilial DysautonomiaUnited States
-
Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Partial LipodystrophyUnited States
-
IRCCS Policlinico S. MatteoCompletedTransthyretin AmyloidosisItaly
-
Fundació Institut de Recerca de l'Hospital de la...Hospital Clinic of BarcelonaCompletedFamilial Hypocalciuric HypercalcemiaSpain
-
University of MichiganAvailable
-
NYU Langone HealthCompletedFamilial DysautonomiaUnited States
-
NYU Langone HealthCompletedFamilial DysautonomiaUnited States
-
Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
-
Katarzyna HolcmanRecruitingTransthyretin AmyloidosisPoland
-
University Hospital, BordeauxUniversity of BordeauxCompletedAmyloid Neuropathies, FamilialFrance
-
Centre Hospitalier Universitaire de NīmesCompletedTransthyretin AmyloidosisFrance
-
NYU Langone HealthWithdrawnFamilial DysautonomiaUnited States
-
Medical University InnsbruckUnknownFamilial Hypobetalipoproteinaemia - Heterozygous Form | Low-LDL-syndromeAustria
-
University of GeorgiaCompletedSAAF-T | FUEL for Families
-
Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
-
Cambridge University Hospitals NHS Foundation TrustRecruitingDiabetes | Diet Modification | LipodystrophyUnited Kingdom
-
National Jewish HealthUniversity of Colorado, Denver; Vanderbilt University; Landspitali University...RecruitingIdiopathic Pulmonary Fibrosis | Idiopathic Interstitial Pneumonia | Familial Pulmonary Fibrosis | Familial Interstitial PneumoniaUnited States, Iceland
-
Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
-
University of MichiganNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingPregnancy Related | Obesity; FamilialUnited States
-
New French Society of AtherosclerosisAkcea TherapeuticsCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
-
Boston Medical CenterEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedLow Income Families Basic Social NeedsUnited States
-
Hospices Civils de LyonCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
-
Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
-
University of Sao PauloMerck Sharp & Dohme LLCUnknownHeterozigous Familial HypercholesterolemiaBrazil
-
University of UtahNational Institute on Aging (NIA)CompletedDementia, FamilialUnited States
-
John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
-
University of NottinghamUniversity of OxfordCompletedFamilial Breast CancerUnited Kingdom
-
Meir Medical CenterRambam Health Care Campus; Hadassah Medical Organization; Assaf-Harofeh Medical... and other collaboratorsUnknownPatella, Familial Recurrent Dislocation OfIsrael
-
Yonsei UniversityCompletedFamilial Hypertrophic CardiomyopathyKorea, Republic of
-
AstraZenecaRecruiting
-
Washington University School of MedicineEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Lou Gehrig Disease | Familial Amyotrophic Lateral Sclerosis | Motor Neuron Disease, FamilialUnited States
-
Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
-
Montreal Heart InstituteCanadian Institutes of Health Research (CIHR)Enrolling by invitationCardiomyopathies | Hypertrophic Cardiomyopathy | Hypertrophic Obstructive Cardiomyopathy | Familial Hypertrophic CardiomyopathyCanada
-
PfizerCompletedTransthyretin Amyloidosis | Transthyretin Gene MutationsUnited States, France, Spain, Taiwan, Israel, Korea, Republic of, Denmark, Canada, Netherlands, Japan, Sweden, Brazil, Mexico, Argentina, Portugal, Belgium, Bulgaria, Cyprus, Germany, Italy, Malaysia, Romania, Saudi Arabia, Turkey, United...
-
PfizerCompletedPolyneuropathy | Hereditary Transthyretin Amyloidosis (ATTRv)Spain
-
Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1United States, Canada, Germany, Israel, Italy, South Africa, Spain, United Kingdom, Brazil, France, Netherlands