- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Hypotonie musculaire
Total 7302 results
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Newcastle UniversityRecruitingFacioscapulohumeral Muscular DystrophyUnited Kingdom
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Hillel Yaffe Medical CenterRecruiting
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Robert Jones and Agnes Hunt Orthopaedic and District...CompletedFacioscapulohumeral Muscular Dystrophy
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Bioblast Pharma Ltd.CompletedMuscular Dystrophy, Oculopharyngeal (OPMD)Canada
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Rigshospitalet, DenmarkUnknownOculopharyngeal Muscular DystrophyDenmark
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Centre Hospitalier Universitaire de NiceCompletedFacioscapulohumeral Muscular DystrophyFrance
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Virginia Commonwealth UniversityWashington University School of Medicine; University of Iowa; University of Minnesota and other collaboratorsRecruitingMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, United Kingdom
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Sarepta Therapeutics, Inc.Active, not recruiting
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityCompletedMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, Denmark
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Neurogen Brain and Spine InstituteWithdrawn
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Nationwide Children's HospitalMyonexus TherapeuticsRecruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...Johns Hopkins UniversityTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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Rigshospitalet, DenmarkUnknownFacioscapulohumeral Muscular Dystrophy 1aDenmark
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Cure CMDCongenital Muscle Disease International RegistrWithdrawnLAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)United States
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Spain, United Kingdom, Netherlands
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy Type 2France, Italy, Spain
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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Grete Andersen, MDCompletedFSHD - Facioscapulohumeral Muscular DystrophyDenmark
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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Rigshospitalet, DenmarkFunding: Toyota Foundation; Funding: Hede Nielsen Foundation; Funding: Grosserer... and other collaboratorsActive, not recruiting
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GenethonActive, not recruitingLGMD2IDenmark, France, United Kingdom
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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Neurogen Brain and Spine InstituteWithdrawn
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Rigshospitalet, DenmarkRecruitingLimb Girdle Muscular DystrophyDenmark
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Lancashire Teaching Hospitals NHS Foundation TrustDuchenne UKRecruiting
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, Turkey, United Kingdom, Italy
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Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Hoffmann-La RocheSarepta Therapeutics, Inc.Recruiting
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West China HospitalRecruiting
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Hacettepe UniversityNot yet recruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PepGen IncRecruitingDuchenne Muscular DystrophyCanada
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RecruitingDuchenne Muscular DystrophyUnited States
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Beni-Suef UniversityNot yet recruitingDuchenne Muscular Dystrophy
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingStudy of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsMuscular Dystrophy, DuchenneItaly
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Muş Alparlan UniversityHacettepe UniversityRecruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.; SYSNAV; ImagingNMDRecruitingBecker Muscular DystrophyUnited States, Spain, Netherlands, United Kingdom
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Taiho Pharmaceutical Co., Ltd.RecruitingDuchenne Muscular DystrophyJapan
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GenethonRecruiting
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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Halic UniversityIstanbul University; Biruni UniversityCompletedDuchenne Muscular DystrophyTurkey
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Sarepta Therapeutics, Inc.Hansa Biopharma ABActive, not recruitingDuchenne Muscular DystrophySpain