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Clinical Trials on Idiopaattinen tulehduksellinen myopatia
Total 1165 results
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Clinic for Special ChildrenRecruitingMyopathy | Myopathy; Hereditary | Myopathies, Nemaline | TNNT1-associated Myopathy | Infantile-onset Nemaline Rod Myopathy | Myopathy, Rod | Amish Nemaline Myopathy | Nemaline Myopathy 5 | NEM5 | Genetic Muscle Disease | Recessive Hereditary Disorder (Autosomal) | ANMUnited States
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Vastra Gotaland RegionEnrolling by invitationMusculoskeletal Diseases | Neuromuscular Diseases | Centronuclear Myopathy | Nemaline Myopathy | Congenital Myopathy | Myosin Storage MyopathySweden
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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Radboud University Medical CenterUMC UtrechtNot yet recruitingCentronuclear Myopathy | Nemaline Myopathy | Central Core Disease | Multi-Minicore DiseaseNetherlands
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Astellas Gene TherapiesCompletedX-linked Myotubular MyopathyUnited States, France, United Kingdom, Canada, Germany
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University of FloridaAudentes TherapeuticsCompletedX-linked Myotubular MyopathyUnited States
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Assiut UniversityNot yet recruitingMyositis | Congenital Myopathy | Acquired Myopathy
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrCompleted
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Rigshospitalet, DenmarkActive, not recruitingCongenital Myopathy | Inherited Muscle Diseases | RYR1-myopathyDenmark
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Ra PharmaceuticalsTerminatedImmune Mediated Necrotizing MyopathyUnited States, Netherlands, France, United Kingdom
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Ultragenyx Pharmaceutical IncNewcastle UniversityCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)United States, Bulgaria, Canada, France, United Kingdom
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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NobelpharmaCompletedGNE Myopathy | Nonaka Disease | Distal Myopathy With Rimmed Vacuoles (DMRV) | Hereditary Inclusion Body Myopathy (hIBM)Japan
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He Eye HospitalNot yet recruiting
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University of BradfordCoopervision, Inc.; University of HuddersfieldNot yet recruiting
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Visioneering Technologies, IncRecruitingMyopiaUnited States, Canada, Hong Kong, Singapore
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University Eye Hospital, FreiburgRecruiting
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Shanghai 10th People's HospitalCompletedMyopia | Myopia, ProgressiveChina
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Tianjin Eye HospitalActive, not recruiting
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Tianjin Eye HospitalCompleted
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Sultan Qaboos UniversityChristian Medical College, Vellore, IndiaUnknown
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Peking University People's HospitalUnknownProgressive MyopiaChina
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Shanghai Eye Disease Prevention and Treatment CenterNot yet recruiting
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Beijing Airdoc Technology Co., Ltd.Recruiting
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Shanghai Eye Disease Prevention and Treatment CenterRecruiting
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Beijing Airdoc Technology Co., Ltd.The First People's Hospital of XuzhouRecruiting
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Universidad Complutense de MadridCooperativa de Ensino Superior, Politécnico e Universitário; Novovision; Instituto... and other collaboratorsActive, not recruiting
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Nova Southeastern UniversityWithdrawnMyopia, Progressive
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Shanghai Eye Disease Prevention and Treatment CenterShanghai General Hospital, Shanghai Jiao Tong University School of MedicineEnrolling by invitationHigh Myopia | Pathologic MyopiaChina
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National Taiwan University HospitalUnknown
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Lawson Health Research InstituteCompleted
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Shanghai Eye Disease Prevention and Treatment CenterRecruiting
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Shanghai Eye Disease Prevention and Treatment CenterShanghai General Hospital, Shanghai Jiao Tong University School of MedicineNot yet recruiting
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iVeena Delivery Systems, Inc.Not yet recruitingMyopia, Progressive
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Shanghai Eye Disease Prevention and Treatment CenterPeking University People's Hospital; Shanghai General Hospital, Shanghai Jiao... and other collaboratorsNot yet recruiting
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Scripps HealthCompleted
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Cloudbreak Therapeutics, LLCNovotech (Australia) Pty LimitedCompletedMyopia, ProgressiveAustralia
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Texas Tech University Health Sciences CenterRecruiting
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Rockefeller UniversityTerminatedMyopathy (Statin Associated)United States
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Menicon Co., Ltd.Universidad Europea de Madrid; Aston University; Clinica novovisionCompletedChildren, Only | Myopia, Progressive | Contact Lens Complication | Perception, Self | Axial Myopia
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Reneo Pharma LtdCompletedPrimary Mitochondrial MyopathyUnited States, Spain, Australia, France, United Kingdom, New Zealand, Denmark, Norway, Czechia, Belgium, Canada, Germany, Hungary, Italy, Netherlands
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Stealth BioTherapeutics Inc.TerminatedPrimary Mitochondrial MyopathyUnited States, Germany, Canada, Italy, United Kingdom, Denmark, Hungary
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Reneo Pharma LtdTerminatedPrimary Mitochondrial MyopathyUnited Kingdom
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Armgo Pharma, Inc.National Institute of Nursing Research (NINR); National Institute of Neurological... and other collaboratorsCompletedRYR-1 MyopathyUnited States