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Clinical Trials on Inborn Errors of Metabolism in Spain
Total 443 results
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Hospital Universitario de CanariasUnknownKidney Failure, Chronic | Disorder of Vitamin DSpain
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Fundació Institut de Recerca de l'Hospital de la...Active, not recruitingParkinson Disease | Huntington DiseaseSpain
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Centre d'Etude des Cellules SouchesGenethonRecruitingWolfram SyndromeFrance, Spain
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Corporacion Parc TauliInstituto de Salud Carlos IIIRecruitingSleep Disorder | Hyperphagia | Behavior DisordersSpain
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Otsuka Pharmaceutical Europe LtdCompletedHyponatremia | Syndrome of Inappropriate ADH (SIADH) SecretionSpain
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Hospital Universitari Vall d'Hebron Research InstituteHospital Universitario La PazNot yet recruitingHereditary Angioedema With C1 Esterase Inhibitor DeficiencySpain
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AstraZenecaCompletedDiabetesFrance, Spain, United Kingdom, Germany, Greece, Italy, Netherlands, Ireland
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Otsuka Pharmaceutical Europe LtdCompletedHyponatremia | Syndrome of Inappropriate ADH (SIADH) SecretionGermany, Spain
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsSpain, Canada, United Kingdom
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Leiden University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Horizon...RecruitingSevere Combined Immunodeficiency Due to RAG1 DeficiencySpain, Netherlands, Italy, Poland, Australia, Turkey, United Kingdom
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ApoPharmaCompletedFriedreich's AtaxiaCanada, Australia, Belgium, France, Italy, Spain
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RWTH Aachen UniversityAssistance Publique - Hôpitaux de ParisWithdrawnFriedreich AtaxiaSpain, Italy, Austria, Germany, United Kingdom, France
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Ionis Pharmaceuticals, Inc.CompletedLafora DiseaseUnited States, Italy, Spain
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University Rovira i VirgiliMinisterio de Ciencia e Innovación, SpainRecruitingMild Cognitive Impairment | Dementia With Lewy Bodies | Dementia Alzheimers | Parkinson Disease Dementia | Dementia FrontotemporalSpain
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Instituto Universitario de Oftalmobiología Aplicada...Hospital del Río Hortega; Hospital Clínico Universitario de ValladolidCompletedMultiple Sclerosis | Eye Abnormalities | Parkinson Disease | Ataxia, Cerebellar | Injury BrainSpain
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Laboratorios OrdesaPeruvian Clinical Research; Quantum ExperimentalCompletedMalnutrition | Cystic Fibrosis | Failure to ThriveSpain, Peru
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Hospital del Mar Research Institute (IMIM)Enrolling by invitationNeurodegenerative Diseases | Cognitive Impairment | Dementia | Alzheimer Disease | Lewy Body Disease | Frontotemporal Dementia | Vascular DementiaSpain
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Hospital Universitari de BellvitgeCompletedObesity | Weight Loss | Obstructive Sleep Apnea of Adult | LifestyleSpain
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BioMarin PharmaceuticalCompletedAchondroplasiaSpain, Denmark, Italy, Austria, Germany, Sweden
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University of BirminghamActive, not recruitingWolfram SyndromeFrance, United Kingdom, Poland, Spain
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argenxRecruitingCongenital Myasthenic SyndromeSpain, Italy, France, United Kingdom, United States, Canada
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University of Texas at AustinHospital Clinic of Barcelona; Fundació Institut de Recerca de l'Hospital de...RecruitingNeurocognitive Disorders | Neurodegenerative Diseases | Dementia | Alzheimer Disease | Language Disorders | Communication Disorders | Primary Progressive Aphasia | Aphasia | Speech Disorders | Frontotemporal Lobar Degeneration | Dysarthria | Apraxia, Motor | Dementia, Frontotemporal | Bilingual AphasiaSpain, United States
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Ascendis Pharma Growth Disorders A/SActive, not recruitingAchondroplasiaUnited States, Denmark, Ireland, New Zealand, Australia, Canada, Spain
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Scholar Rock, Inc.CompletedNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2United States, Spain, Italy, Netherlands
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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Otsuka Pharmaceutical Development & Commercialization...CompletedSyndrome of Inappropriate Antidiuretic Hormone Secretion (SIADH)Germany, United Kingdom, Spain, Sweden, Hungary, Czech Republic, Denmark
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CSL BehringCompletedHemophilia AAustria, Belgium, France, Germany, Italy, Spain, Switzerland
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University of ValenciaHospital Universitario La Fe; Hospital General Universitario de Valencia; Hospital...CompletedAsthma | Type 1 Diabetes | Allergic Rhinitis | Cystic Fibrosis | Pulmonary Disease | Atopic Dermatitis | Food Allergy | Allergic Asthma | Rhinoconjunctivitis | Primary Ciliary Dyskinesia | Short StatureSpain
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Novo Nordisk A/SCompletedTurner Syndrome | Genetic DisorderSpain
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University Medical Center GroningenNot yet recruitingADPKDNetherlands, United Kingdom, Belgium, Germany, France, Spain
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IntraBio IncRecruitingAtaxia Telangiectasia | Louis Bar SyndromeSpain, United States, Germany, United Kingdom
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PfizerTerminatedAchondroplasiaUnited States, Australia, Belgium, Denmark, Italy, Portugal, Spain
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AviadoBio LtdRecruitingFrontotemporal Dementia | FTD | FTD-GRN | Dementia, FrontotemporalNetherlands, Spain, Poland, United States
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Lexicon PharmaceuticalsSanofiCompletedType 1 Diabetes Mellitus (T1DM) | High Level of Sugar (Glucose) in the BloodUnited States, Australia, Spain, Belgium, Argentina, Bulgaria, Canada, Colombia, Czechia, France, Germany, Hungary, Israel, Italy, New Zealand, Poland, Slovakia, South Africa, United Kingdom
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Dermatology Specialties Limited PartnershipCompletedTuberous Sclerosis | Facial AngiofibromaUnited States, Taiwan, Serbia, Spain, Australia, Czechia, Hungary, New Zealand, Slovakia
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Otsuka Pharmaceutical Europe LtdUnknownAutosomal Dominant Polycystic Kidney DiseaseSpain, United Kingdom, Germany, France, Belgium, Switzerland, Austria
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European Friedreich's Ataxia Consortium for Translational...RecruitingFriedreich's AtaxiaAustria, Germany, Italy, Spain, Belgium, Czechia, France, Greece, Ireland, United Kingdom
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University Hospital, GenevaCompletedAfibrinogenemia, CongenitalFrance, Turkey, Switzerland, Netherlands, Spain, India, Poland, Canada, United States, Algeria, Egypt, Germany, Italy, Japan, Kuwait, Lebanon, Morocco, Pakistan, Serbia, Slovakia, Tunisia
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AmgenCompletedOsteogenesis ImperfectaSpain, United States, Turkey, Austria, Germany, Greece, Hungary, Italy
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PfizerTerminatedAchondroplasiaBelgium, United States, Japan, Australia, Portugal, Denmark, Italy, Spain
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, United Kingdom, Japan, Spain, Turkey
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QED Therapeutics, Inc.RecruitingAchondroplasiaUnited States, Spain, United Kingdom, France, Canada, Australia
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David Franco CastellanosJesús Ángel Seco Calvo; Javier Tejada GarciaNot yet recruitingDementia | Neurologic Disorder | Dementia, Vascular | Cognitive Decline | Dementia, Mixed | Dementia With Lewy Bodies | Neurologic Dysfunction | Dementia of Alzheimer Type | Neurologic Deficits | Dementia FrontalSpain
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Merck KGaA, Darmstadt, GermanyMerck Serono S.A., GenevaCompletedTurner Syndrome | Idiopathic Growth Hormone DeficiencySpain, France, Canada, United Kingdom, Czech Republic, Argentina, Germany, Italy, Sweden
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QED Therapeutics, Inc.Enrolling by invitationAchondroplasiaUnited States, Spain, United Kingdom, France, Australia, Canada
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Noema Pharma AGRecruitingTuberous Sclerosis ComplexUnited States, Turkey, Poland, Spain, United Kingdom, India, Italy, Israel
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain